P037: Design of a multi-center randomized phase 3 clinical trial (HURCULES) evaluating OTL-203 in MPS-IH vs allogeneic hematopoietic stem cell transplantation von Harmatz, Paul, Wynn, Robert, Gupta, Ashish, Kharbanda, Sandhya, Lindemans, Caroline, Ahrens-Nicklas, Rebecca, van Hasselt, Peter, Lund, Troy, Olson, Timothy, Tucci, Francesca, Martin, Leonie, Boeglin, Nathalie, Brooks, Jean, Syonmez, Su, Campbell, Laura, Jones, Simon, Orchard, Paul, Bernardo, Maria Ester

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Design of a multi-center randomized active controlled phase 3 clinical trial (HURCULES) evaluating the safety and efficacy of OTL-203 in patients with MPS IH versus standard of car... von Orchard, Paul J., Wynn, Robert F., Kharbanda, Sandhya, Ahrens-Nicklas, Rebecca, van Hasselt, Peter M., Lund, Troy C., Olson, Timothy S., Tucci, Francesca, Martin, Leonie, Boeglin, Nathalie, Brooks, Jean, Syonmez, Su, Campbell, Laura, Harmatz, Paul, Jones, Simon A., Gupta, Ashish O., Bernardo, Maria Ester

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Design of a Multi-Center Randomized Active Controlled Phase 3 Clinical Trial (HURCULES) Evaluating the Safety and Efficacy of OTL-203 in Patients with MPS-IH Versus Standard of Car... von Gupta, Ashish O., Wynn, Robert F, Kharbanda, Sandhya, Lindemans, Caroline A., Ahrens-Nicklas, Rebecca, van Hasselt, Peter M., Lund, Troy C., Olson, Timothy S., Tucci, Francesca, Martin, Leonie, Boeglin, Nathalie, Brooks, Jean, Syonmez, Su, Campbell, Laura, Harmatz, Paul, Jones, Simon A., Orchard, Paul J., Bernardo, Maria Ester

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