Patisiran treatment for ATTR cardiac amyloidosis: 18-month results of the phase 3 APOLLO-B study von Fontana, M., L Berk, J., Hanna, M., D Gillmore, J., Pedro-Schwartzmann, V., Lairez, O., Hyun-Jai, C., Van Der Meer, P., White, M.T., Elena, Y., Sweetser, M.T., Jay, P.Y., Vest, J., S Maurer, M.

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BG-12 (dimethyl fumarate) and pregnancy: Preclinical studies and pregnancy outcomes reported during the clinical development program von Gold, R, Phillips, J.T, Havrdova, E, Bar-Or, A, Kappos, L, Clarke, J, Yuan, H, Novas, M, Sweetser, M.T, Kurukulasuriya, N.C, Viglietta, V, Fox, R.J

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Safety and tolerability of BG-12 (dimethyl fumarate) in relapsing–/INS;remitting multiple sclerosis: Interim results from the endorse extension study von Selmaj, K, Phillips, J.T, Fox, R.J, Raghupathi, K, Yuan, H, Novas, M, Sweetser, M.T, Kurukulasuriya, N.C, Viglietta, V, Dawson, K.T, Gold, R

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Risk Factors for Mortality in Patients with Hereditary Transthyretin-Mediated Amyloidosis: An Analysis of APOLLO and Global Open Label Extension Studies von Polydefkis, M., Gillmore, J., Dispenzieri, A., Chen, J., Sweetser, M.T., Vest, J., Melanson, M., Conceicao, I., Kristen, A.

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Long-term integrated safety of patisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy von Gillmore, J, Berk, J, Dispenzieri, A, Polydefkis, M, Gonzalez-Duarte, A, Sekijima, Y, Sweetser, M.T, Arum, S, Wang, J.J, White, M.T, Maurer, M

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Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis von Maurer, Mathew S., Kale, Parag, Fontana, Marianna, Berk, John L., Grogan, Martha, Gustafsson, Finn, Hung, Rebecca R., Gottlieb, Robert L., Damy, Thibaud, González-Duarte, Alejandra, Sarswat, Nitasha, Sekijima, Yoshiki, Tahara, Nobuhiro, Taylor, Mark S., Kubanek, Milos, Donal, Erwan, Palecek, Tomas, Tsujita, Kenichi, Tang, W.H. Wilson, Yu, Wen-Chung, Obici, Laura, Simões, Marcus, Fernandes, Fábio, Poulsen, Steen Hvitfeldt, Diemberger, Igor, Perfetto, Federico, Solomon, Scott D., Di Carli, Marcelo, Badri, Prajakta, White, Matthew T., Chen, Jihong, Yureneva, Elena, Sweetser, Marianne T., Jay, Patrick Y., Garg, Pushkal P., Vest, John, Gillmore, Julian D.

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Résultats primaires de l’étude APOLLO-B d’extension en ouvert du patisiran chez les patients atteints d’amylose cardiaque à transthyrétine von Maurer, M.S., Berk, J.L., Gillmore, J.D., Lairez, O., White, M.T., Sweetser, M., Lainé, A.F., Fontana, M.

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A Recurrent De Novo PACS2 Heterozygous Missense Variant Causes Neonatal-Onset Developmental Epileptic Encephalopathy, Facial Dysmorphism, and Cerebellar Dysgenesis von Olson, H.E., Jean-Marcais, N., Yang, E., Heron, D., Tatton-Brown, K., Zwaag, P.A. van der, Bijlsma, E.K., Krock, B.L., Backer, E., Kamsteeg, E.J., Sinnema, M., Reijnders, M.R.F., Bearden, D., Begtrup, A., Telegrafi, A., Lunsing, R.J., Burglen, L., Lesca, G., Cho, M.T., Smith, L.A., Sheidley, B.R., Achkar, C.M. el, Pearl, P.L., Poduri, A., Skraban, C.M., Tarpinian, J., Nesbitt, A.I., Putte, D.E.F. van de, Ruivenkamp, C.A.L., Rump, P., Chatron, N., Sabatier, I., Bellescize, J. de, Guibaud, L., Sweetser, D.A., Waxler, J.L., Wierenga, K.J., Donadieu, J., Narayanan, V., Ramsey, K.M., Nava, C., Riviere, J.B., Vitobello, A., Mau-Them, F.T., Philippe, C., Bruel, A.L., Duffourd, Y., Thomas, L., Lelieveld, S.H., Schuurs-Hoeijmakers, J., Brunner, H.G., Keren, B., Thevenon, J., Faivre, L., Thomas, G., Thauvin-Robinet, C.

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Looking Towards 2030: Strengthening the Environmental Health in Childhood-Adolescent Cancer Survivor Programs von Cabrera-Rivera, Laura T, Sweetser, Brittney, Fuster-Soler, José L, Ramis, Rebeca, López-Hernández, Fernando A, Pérez-Martínez, Antonio, Ortega-García, Juan A

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Human AML cells in NOD/SCID mice: engraftment potential and gene expression von LUMKUL, R, GORIN, N-C, CIVIN, Cl, MALEHORN, M. T, HOEHN, G. T, ZHENG, R, BALDWIN, B, SMALL, D, GORE, S, SMITH, D, MELTZER, P. S

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Differential Diagnosis and Management of Diarrhea in Patients with Neuroendocrine Tumors von Pusceddu, Sara, Rossi, Roberta Elisa, Torchio, Martina, Prinzi, Natalie, Niger, Monica, Coppa, Jorgelina, Giacomelli, Luca, Sacco, Rodolfo, Facciorusso, Antonio, Corti, Francesca, Raimondi, Alessandra, Prisciandaro, Michele, Colombo, Elena, Beninato, Teresa, Del Vecchio, Marta, Milione, Massimo, Di Bartolomeo, Maria, de Braud, Filippo

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Endourological management of upper tract transitional cell carcinoma von Gettman, M.T., Segura, J.W.

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Identification of Auxins in a Commercial Seaweed Concentrate von Crouch, I.J., Smith, M.T., van Staden, J., Lewis, M.J., Hoad, G.V.

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Electrochemistry of colloidal palladium : an experimental study of sol formation and electrocatalysis von VAN DER PUTTEN, A. M. T, DE BAKKER, J.-W. G, FOKKINK, L. G. J

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Electron transfer reactions from proflavin or acridine yellow radical anions to ion acceptors and the possibility of water reduction von Nenadović, M.T., Mićić, O.I., Kosanić, M.M.

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Pathogenic Impact of Fatty Acid-Binding Proteins in Parkinson's Disease-Potential Biomarkers and Therapeutic Targets von Kawahata, Ichiro, Fukunaga, Kohji

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Accelerated Migration of Respiratory Dendritic Cells to the Regional Lymph Nodes Is Limited to the Early Phase of Pulmonary Infection von Legge, Kevin L, Braciale, Thomas J

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Gravity Recovery and Interior Laboratory (GRAIL): Mapping the Lunar Interior from Crust to Core von Zuber, Maria T., Smith, David E., Lehman, David H., Hoffman, Tom L., Asmar, Sami W., Watkins, Michael M.

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Modular Utilization of Distal cis-Regulatory Elements Controls Ifng Gene Expression in T Cells Activated by Distinct Stimuli von Balasubramani, Anand, Shibata, Yoichiro, Crawford, Gregory E., Baldwin, Albert S., Hatton, Robin D., Weaver, Casey T.

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An Essential Role of the Transcription Factor GATA-3 for the Function of Regulatory T Cells von Wang, Yunqi, Su, Maureen A., Wan, Yisong Y.

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