LATE BREAKING NEWS E-POSTER PRESENTATION von Willcocks, Dr. Rebecca J, Forbes, Dr. Sean C, Lott, Dr. Donovan J, Senesac, Dr. Claudia R, Barnard, Dr. Alison M, Lehman, Kelly J, Nease, Carrie E, Church, Kathleen, Sahenk, Dr. Zarife, Sweeney, Dr. H. Lee, Rodino-Klapac, Dr. Louise R, Walter, Dr. Glenn A, Mendell, Dr. Jerry R, Vandenborne, Dr. Krista

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LATE BREAKING NEWS E-POSTER PRESENTATION: LBP 13 rAAVrh.74.MHCK7.micro-dystrophin gene therapy in children with Duchenne muscular dystrophy: A quantitative MR biomarker study von Willcocks, Dr. Rebecca J, Forbes, Dr. Sean C, Lott, Dr. Donovan J, Senesac, Dr. Claudia R, Barnard, Dr. Alison M, Lehman, Kelly J, Nease, Carrie E, Church, Kathleen, Sahenk, Dr. Zarife, Sweeney, Dr. H. Lee, Rodino-Klapac, Dr. Louise R, Walter, Dr. Glenn A, Mendell, Dr. Jerry R, Vandenborne, Dr. Krista

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Deflazacort vs prednisone treatment for Duchenne muscular dystrophy: A meta‐analysis of disease progression rates in recent multicenter clinical trials von McDonald, CM, Sajeev, G, Yao, Z, McDonnell, E, Elfring, G, Souza, M, Peltz, SW, Darras, BT, Shieh, PB, Cox, DA, Landry, J, Signorovitch, J, Torricelli, RE, Finkel, RS, Flanigan, KM, Goemans, N, Heydemann, P, Kaminska, A, Kirschner, J, Muntoni, F, Osorio, AN, Sejersen, T, Sweeney, HL, Tulinius, M, Vilchez, JJ, Voit, T, Wong, B, Alfano, LN, Eagle, M, James, MK, Mayhew, A, Nelson, L, Rose, KJ, Abdel-Hamid, HZ, Apkon, SD, Barohn, RJ, Bertini, E, Bloetzer, C, de Vaud, LC, Butterfield, RJ, Chabrol, B, Chae, JH, Jongno-Gu, DR, Comi, GP, Desguerre, I, Escobar, RG, Finanger, E, Guglieri, M, Iannaccone, ST, Karachunski, P, Kudr, M, Mah, JK, Mathews, K, Nevo, Y, Parsons, J, Pereon, Y, Araujo, APDQC, Renfroe, JB, de Resende, MBD, Ryan, M, Selby, K, Tennekoon, G, Vita, G, Abdel-Hamid, H, Apkon, S, Barohn, R, Belousova, E, Brandsema, J, Bruno, C, Burnette, W, Butterfield, R, Byrne, B, Chandratre, S, Connolly, A, De Groot, I, Deconinck, N, Dooley, J, Dubrovsky, A, Durigneux, J, Finkel, R, Harper, A, Iannaccone, S, Janas, J, Komaki, H, Leung, E, Mah, J, Mercuri, E, McMillan, H, de Munain, AL, Niks, E, Ogata, K, Pascual, S, Pegoraro, E, Renfroe, B, Sanka, RB, Schallner, J, Smith, E, Sparks, S, Victor, R, Wilichoswki, E

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