PABPN1 gene therapy for oculopharyngeal muscular dystrophy von Malerba, A., Klein, P., Bachtarzi, H., Jarmin, S. A., Cordova, G., Ferry, A., Strings, V., Espinoza, M. Polay, Mamchaoui, K., Blumen, S. C., St Guily, J. Lacau, Mouly, V., Graham, M., Butler-Browne, G., Suhy, D. A., Trollet, C., Dickson, G.

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Gene replacement therapy as a novel approach for the treatment of oculopharyngeal muscular dystrophy von Malerba, A, Klein, P, Bachtarzi, H, Jarmin, S, Ferry, A, Graham, M, Strings, V, Butler-Browne, G, Suhy, D, Dickson, G, Trollet, C

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TH.O.15 - Gene therapy for oculopharyngeal muscular dystrophy von Malerba, A., Klein, P., Bachtarzi, H., Jarmin, S., Cordova, G., Ferry, A., Strings, V., Espinoza, M. Polay, Mamchaoui, K., Blumen, S., Guily, J. Lacau St, Mouly, V., Graham, M., Butler-Browne, G., Suhy, D., Trollet, C., Dickson, G.

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Gene therapy for oculopharyngeal muscular dystrophy von Malerba, A., Klein, P., Bachtarzi, H., Jarmin, S., Cordova, G., Ferry, A., Strings, V., Espinoza, M. Polay, Mamchaoui, K., Blumen, S., Guily, J. Lacau St, Mouly, V., Graham, M., Butler-Browne, G., Suhy, D., Trollet, C., Dickson, G.

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P.179 - Gene replacement therapy as a novel approach for the treatment of oculopharyngeal muscular dystrophy von Malerba, A., Klein, P., Bachtarzi, H., Jarmin, S., Ferry, A., Graham, M., Strings, V., Butler-Browne, G., Suhy, D., Dickson, G., Trollet, C.

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FSHD / OPMD / EDMD / DMI: P.367BB-301: a single ``silence and replace'' AAV-based vector for the treatment of oculopharyngeal muscular dystrophy von Strings-Ufombah, V., Malerba, A., Harbaran, S., Roth, F., Cappellari, O., Nguyen, N., Kao, S., Takahashi, K., Kloth, C., Roelvink, P., Dickson, G., Trollet, C., Suhy, D.

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FSHD / OPMD / EDMD / DMI von Strings-Ufombah, V., Malerba, A., Harbaran, S., Roth, F., Cappellari, O., Nguyen, N., Kao, S., Takahashi, K., Kloth, C., Roelvink, P., Dickson, G., Trollet, C., Suhy, D.

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PABPN1 gene therapy for oculopharyngeal muscular dystrophy von Malerba, A, Klein, P, Bachtarzi, H, Jarmin, SA, Cordova, G, Ferry, A, Strings, V, Espinoza, MP, Mamchaoui, K, Blumen, SC, St Guily, JL, Mouly, V, Graham, M, Butler-Browne, G, Suhy, DA, Trollet, C, Dickson, G

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Established PABPN1 intranuclear inclusions in OPMD muscle can be efficiently reversed by AAV-mediated knock-down and replacement of mutant expanded PABPN1 von Malerba, A, Klein, P, Lu-Nguyen, N, Cappellari, O, Strings-Ufombah, V, Harbaran, S, Roelvink, P, Suhy, D, Trollet, C, Dickson, G

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Prospects for fundamental physics with LISA von Hertog, Thomas, Witek, Helvi, Abdelsalhin, T, Achucarro, A, Afshordi, N, Baibhav, V, Bellini, E, Bena, I, Benkel, R, Bernard, L, Bertacca, D, Beyer, F, Bicak, J, Biondini, S, Boller, K, Bulten, H, Cabral, F, Celoria, M, Chatziioannou, K, Comelli, D, Compere, G, Cruces, D, Cusin, G, Datta, S, De Rham, C, Filippo, F. Di, Dimastrogiovanni, E, Doneva, D, Durrer, R, East, W, Ellis, J. R, Ezquiaga, J. M, Fairhurst, S, Ferrari, V, Frauendiener, J, Fujita, R, Germani, C, Gourgoulhon, E, Halburd, R, Han, W. -B, Hees, A, Heng, I. S, Hennig, J, Hull, M, Kalaghatgi, C, Kastha, S, Keresztes, Z, Kimpson, T, Klein, A, Kokkotas, K, Koyama, K, Krishnendu, N. V, Kroon, J. A. V, Landragin, A, Poncin-Lafitte, C. Le, Lemos, J, Li, B, Liguori, M, Liu, G, Lobo, F. S. N, Martens, W, Martinovic, K, Matarrese, S, Mazumdar, A, Mittnacht, L, Martin-Moruno, P, Novak, J, Orlando, G, Peloso, M, Podolsky, J, Prabhat, S, Pratten, G, Prouza, M, Randall, L, Raymond, V, Riotto, A, Robson, T, Rosofsky, S, Sago, N, Sakellariadou, M, Sberna, L, Scheel, M, Silva, A. d, Simpson, C, Stefanek, B. A, Stein, L, Stergioulas, N, Sutton, P, Tagoshi, H, Tahamtan, T, Takeda, H, Trodden, M, Traykova, D, Unal, C, Brand, J. Van den, Verde, L, Vretinaris, S, Voelkel, S, Wiltshire, D, Yi, L

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Cross-Disorder Genome-Wide Analyses Suggest a Complex Genetic Relationship Between Tourette's Syndrome and OCD von Yu, Dongmei, Mathews, Carol A, Scharf, Jeremiah M, Neale, Benjamin M, Gamazon, Eric R, Derks, Eske M, Evans, Patrick, Edlund, Christopher K, Fagerness, Jesen A, Osiecki, Lisa, Haddad, Stephen, Illmann, Cornelia, McGrath, Lauren M, Mayerfeld, Catherine, Arepalli, Sampath, Barr, Cathy L, Bellodi, Laura, Berrió, Gabriel Bedoya, Bienvenu, O Joseph, Bloch, Michael H, Budman, Cathy L, Cappi, Carolina, Cavallini, Maria C, Chouinard, Sylvain, Cook, Edwin H, Cookson, M R, Coric, Vladimir, Cusi, Daniele, Delorme, Richard, Eapen, Valsama, Egberts, Karin, Falkai, Peter, Fernandez, Thomas, Fournier, Eduardo, Garrido, Helena, Geller, Daniel, Gilbert, Donald L, Greenberg, Benjamin D, Gross-Tsur, Varda, Grünblatt, Edna, Hardy, John, Hemmings, Sian M J, Hezel, Dianne M, Hoekstra, Pieter J, Jankovic, Joseph, King, Robert A, Kurlan, Roger, Leboyer, Marion, Leckman, James F, Lennertz, Leonhard, Liu, Chunyu, Lochner, Christine, Lowe, Thomas L, Macciardi, Fabio, Maier, Wolfgang, Manunta, Paolo, Marconi, Maurizio, Mesa Restrepo, Sandra C, Moessner, Rainald, Moorjani, Priya, Morgan, Jubel, Muller, Heike, Murphy, Dennis L, Nurmi, Erika, Ochoa, William Cornejo, Ophoff, Roel A, Pato, Carlos N, Pollak, Yehuda, Renner, Tobias, Richter, Margaret A, Riddle, Mark A, Robertson, Mary M, Romero, Roxana, Rosenberg, David, Salvi, Erika, Sampaio, Aline S, Samuels, Jack, Service, Susan K, Singer, Harvey S, Smit, Jan H, Strengman, Eric, Tischfield, Jay A, Turiel, Maurizio, Valencia Duarte, Ana V, Walitza, Susanne, Wang, Ying, Weiss, Robert, Wendland, Jens R, Westenberg, Herman G M, Shugart, Yin Yao, Miguel, Euripedes C, Ruiz-Linares, Andres, McMahon, William, Rouleau, Guy A, Purcell, Shaun, Heutink, Peter, Hanna, Gregory L, Conti, David V, Arnold, Paul D, Pauls, David L

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Relation of insulin resistance to markers of preclinical cardiovascular disease: the Strong Heart Study von de Simone, G., Devereux, R.B., Palmieri, V., Roman, M.J., Celentano, A., Welty, T.K., Fabsitz, R.R., Contaldo, F., Howard, B.V., the Strong Heart Study Investigators

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A theory of scalar mesons von t Hooft, G, Isidori, G, Maiani, L, Polosa, A.D, Riquer, V

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Electromagnetic response of interacting Weyl semimetals von Jacobs, V. P. J, Betzios, Panagiotis, Gursoy, Umut, Stoof, H. T. C

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Optimal quantum clocks von Buzek, V, Derka, R, Massar, S

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Astrobites as a Community-led Model for Education, Science Communication, and Accessibility in Astrophysics von Khullar, Gourav, Kohler, Susanna, Konchady, Tarini, Foley, Mike, Hornsby, Amber L, Reyes, Mithi A. de los, Chisari, Nora Elisa, Villar, V. Ashley, Shin, Kaitlyn, Doughty, Caitlin, Shipp, Nora, Ramasawmy, Joanna, Penoyre, Zephyr, Lichtenberg, Tim, Storey-Fisher, Kate, Hall, Oliver, Lewis, Briley, Pearlman, Aaron B, Cárdenas-Avendaño, Alejandro, Bridge, Joanna S, González-Egea, Elena, Panwar, Vatsal, Slepian, Zachary, Zimmerman, Mara

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Photometric redshifts for the Kilo-Degree Survey. Machine-learning analysis with artificial neural networks von Bilicki, M, Hoekstra, H, Brown, M. J. I, Amaro, V, Blake, C, Cavuoti, S, Jong, J. T. A. de, Georgiou, C, Hildebrandt, H, Wolf, C, Amon, A, Brescia, M, Brough, S, Costa-Duarte, M. V, Erben, T, Glazebrook, K, Grado, A, Heymans, C, Jarrett, T, Joudaki, S, Kuijken, K, Longo, G, Napolitano, N, Parkinson, D, Vellucci, C, Kleijn, G. A. Verdoes, Wang, L

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Photometric redshifts for the Kilo-Degree Survey. Machine-learning analysis with artificial neural networks von Bilicki, M, Hoekstra, H, Brown, M. J. I, Amaro, V, Blake, C, Cavuoti, S, Jong, J. T. A. de, Georgiou, C, Hildebrandt, H, Wolf, C, Amon, A, Brescia, M, Brough, S, Costa-Duarte, M. V, Erben, T, Glazebrook, K, Grado, A, Heymans, C, Jarrett, T, Joudaki, S, Kuijken, K, Longo, G, Napolitano, N, Parkinson, D, Vellucci, C, Kleijn, G. A. Verdoes, Wang, L

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Explicit Construction of Local Hidden Variables for Any Quantum Theory Up to Any Desired Accuracy von t Hooft, Gerard

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Backreaction of a massless minimally coupled scalar field from inflationary quantum fluctuations von Glavan, D, Prokopec, T, Prymidis, V

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