Mechanism of action and therapeutic route for a muscular dystrophy caused by a genetic defect in lipid metabolism von Tavasoli, Mahtab, Lahire, Sarah, Sokolenko, Stanislav, Novorolsky, Robyn, Reid, Sarah Anne, Lefsay, Abir, Otley, Meredith O. C., Uaesoontrachoon, Kitipong, Rowsell, Joyce, Srinivassane, Sadish, Praest, Molly, MacKinnon, Alexandra, Mammoliti, Melissa Stella, Maloney, Ashley Alyssa, Moraca, Marina, Pedro Fernandez-Murray, J., McKenna, Meagan, Sinal, Christopher J., Nagaraju, Kanneboyina, Robertson, George S., Hoffman, Eric P., McMaster, Christopher R.

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Ryanodine channel complex stabilizer compound S48168/ARM210 as a disease modifier in dystrophin‐deficient mdx mice: proof‐of‐concept study and independent validation of efficacy... von Capogrosso, Roberta Francesca, Mantuano, Paola, Uaesoontrachoon, Kitipong, Cozzoli, Anna, Giustino, Arcangela, Dow, Todd, Srinivassane, Sadish, Filipovic, Marina, Bell, Christina, Vandermeulen, Jack, Massari, Ada Maria, De Bellis, Michela, Conte, Elena, Pierno, Sabata, Camerino, Giulia Maria, Liantonio, Antonella, Nagaraju, Kanneboyina, De Luca, Annamaria

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A mouse model of inherited choline kinase β-deficiency presents with specific cardiac abnormalities and a predisposition to arrhythmia von Tavasoli, Mahtab, Feridooni, Tiam, Feridooni, Hirad, Sokolenko, Stanislav, Mishra, Abhishek, Lefsay, Abir, Srinivassane, Sadish, Reid, Sarah Anne, Rowsell, Joyce, Praest, Molly, MacKinnon, Alexandra, Mammoliti, Melissa, Maloney, Ashley Alyssa, Moraca, Marina, Uaesoontrachoon, Kitipong, Nagaraju, Kanneboyina, Hoffman, Eric P., Pasumarthi, Kishore B.S., McMaster, Christopher R.

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Vamorolone targets dual nuclear receptors to treat inflammation and dystrophic cardiomyopathy von Heier, Christopher R, Yu, Qing, Fiorillo, Alyson A, Tully, Christopher B, Tucker, Asya, Mazala, Davi A, Uaesoontrachoon, Kitipong, Srinivassane, Sadish, Damsker, Jesse M, Hoffman, Eric P, Nagaraju, Kanneboyina, Spurney, Christopher F

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Orthogonal analysis of dystrophin protein and mRNA as a surrogate outcome for drug development von Uaesoontrachoon, Kitipong, Srinivassane, Sadish, Warford, Jordan, Mekhssian, Kevork, Montpetit, Hélène, Beauvois, Romain, Keyhani, Anahita, Hathout, Yetrib, Yamashita, Taishi, Satou, Youhei, Osaki, Hironori, Praest, Molly, Moraca, Marina, Malbasic, Maja, Ross, William, MacKinnon, Alexandra, Rowsell, Joyce, Mullen, Amanda, Matyas, Mark, Mummidivarpu, Swati, Nagaraju, Kanneboyina, Hoffman, Eric P

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