P3.07 Preclinical safety of AVI-4658, a phosphorodiamidate morpholino oligomer (PMO) being developed to skip exon 51 in Duchenne muscular dystrophy von Shrewsbury, S.B, Sazani, P

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P1.10 Comparative pharmacokinetics (PK) in primates and humans of AVI-4658, a phosphorodiamidate morpholino oligomer (PMO) for treating DMD patients von Shrewsbury, S.B, Sazani, P, Muntoni, F

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Single and Chronic Dose Pharmacokinetics of a Novel Submicron Suspension of Budesonide von Shrewsbury, S.B, Uster, P

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O.16 Current progress and preliminary results with the systemic administration trial of AVI-4658, a novel phosphorodiamidate morpholino oligomer (PMO) skipping dystrophin exon 51 i... von Shrewsbury, S.B, Cirak, S, Guglieri, M, Bushby, K, Muntoni, F

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P03 Exon skipping and dystrophin restoration in Duchenne muscular dystrophy patients after systemic phosphorodiamidate morpholino oligomer treatment von Cirak, S, Arechavala-Gomeza, V, Guglieri, M, Feng, L, Torelli, S, Anthony, K, Garralda, M.E, Wells, D, Dickson, G, Wood, M.J.A, Wilton, S.D, Straub, V, Shrewsbury, S.B, Sewry, C, Morgan, J.E, Bushby, K, Muntoni, F

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Novel Pressurised Metered Dose Inhaler Aerosol Delivery of Fluticasone Propionate via Tempo® in Humans von Shrewsbury, S.B., Mohsen, N.M., Newman, S.P., Pitcairn, G., Armer, T.A.

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1FC2.1 Exon skipping and dystrophin restoration in Duchenne Muscular Dystrophy patients after systemic phosphorodiamidate morpholino oligomer treatment von Cirak, S., Arechavala-Gomeza, V., Guglieri, M., Feng, L., Torelli, S., Anthony, K., Garralda, M.E., Wells, D.J., Dickson, G., Wood, M.J.A., Wilton, S., Straub, V., Shrewsbury, S.B., Sewry, C., Morgan, J.E., Bushby, K., Muntoni, F.

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Long-term follow up of a double-blind, randomized, placebo-controlled trial of Cyclosporine Inhalation Solution (CyIS) in lung transplant recipients von Iacono, A.T., Capra, W.B., Shrewsbury, S.B., Johnson, B.A., Grgurich, W.F., Corcoran, T.E., Youssef, J.G., Smith-Seiler, D.A., Smaldone, G.C., Zeevi, A., Yousem, S.A., Fung, J.J., Dauber, J.H., Burckart, G.J., Griffith, B., McCurry, K.R.

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