CRISPR-based gene editing enables FOXP3 gene repair in IPEX patient cells von Goodwin, M, Lee, E, Lakshmanan, U, Shipp, S, Froessl, L, Barzaghi, F, Passerini, L, Narula, M, Sheikali, A, Lee, C M, Bao, G, Bauer, C S, Miller, H K, Garcia-Lloret, M, Butte, M J, Bertaina, A, Shah, A, Pavel-Dinu, M, Hendel, A, Porteus, M, Roncarolo, M G, Bacchetta, R

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SELECTION OF GENOME EDITED HEMATOPOIETIC STEM CELLS PRIOR TO TRANSPLANTATION DECREASES THE ENGRAFTMENT POTENTIAL AND THERAPEUTIC EFFICACY von Poletto, E, Colella, P, Sheikali, A, Khan, S, Tomatsu, S, Baldo, G, Gomez-Ospina, N

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Engineering monocyte/macrophage−specific glucocerebrosidase expression in human hematopoietic stem cells using genome editing von Scharenberg, Samantha G., Poletto, Edina, Lucot, Katherine L., Colella, Pasqualina, Sheikali, Adam, Montine, Thomas J., Porteus, Matthew H., Gomez-Ospina, Natalia

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Author Correction: Engineering monocyte/macrophage−specific glucocerebrosidase expression in human hematopoietic stem cells using genome editing von Scharenberg, Samantha G., Poletto, Edina, Lucot, Katherine L., Colella, Pasqualina, Sheikali, Adam, Montine, Thomas J., Porteus, Matthew H., Gomez-Ospina, Natalia

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Prioritizing zoonotic diseases utilizing the One Health approach: Jordan's experience von Kheirallah, Khalid A., Al-Mistarehi, Abdel-Hameed, Alsawalha, Lora, Hijazeen, Zaidoun, Mahrous, Heba, Sheikali, Sami, Al-Ramini, Salam, Maayeh, Mohammad, Dodeen, Rachel, Farajeh, Mahmoud, Masadeh, Nezar, Alemam, Amer, Alsulaiman, Jomana, Samhouri, Dalia

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Busulfan conditioning allows high engraftment of human genome edited hematopoietic stem cells and improved central nervous system correction in a mucopolysaccharidosis type I mouse... von Poletto, Edina, Colella, Pasqualina, Sheikali, Adam, Baldo, Guilherme, Gomez-Ospina, Natalia

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Monocyte lineage-specific glucocerebrosidase expression in human hematopoietic stem cells: A universal genome editing strategy for Gaucher disease von Gomez-Ospina, Natalia, Scharenberg, Samantha G., Lucot, Katherine L., Sheikali, Adam, Porteus, Matthew H.

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Highway to the danger zone: exposure-dependent costs of immunity in a vertebrate ectotherm von Brace, Amber J., Sheikali, Sam, Martin, Lynn B.

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The Binns Program for Cord Blood Research: A novel model of cord blood banking for academic biomedical research von Mantri, Sruthi, Sheikali, Adam, Binns, Corey, Lyell, Deirdre J., DiGiusto, David L., Porteus, Matthew H., Agarwal-Hashmi, Rajni

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Improved Genome Editing through Inhibition of FANCM and Members of the BTR Dissolvase Complex von de Alencastro, Gustavo, Puzzo, Francesco, Pavel-Dinu, Mara, Zhang, Feijie, Pillay, Sirika, Majzoub, Karim, Tiffany, Matthew, Jang, Hagoon, Sheikali, Adam, Cromer, M. Kyle, Meetei, Ruhikanta, Carette, Jan E., Porteus, Matthew H., Pekrun, Katja, Kay, Mark A.

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Jordan’s Pandemic Influenza Preparedness (PIP): A Reflection on COVID-19 Response von Kheirallah, Khalid A., Al-Nusair, Mohammed, Aljabeiti, Shahed, Sheikali, Nadir, Alzoubi, Abdallah, Alsulaiman, Jomana W., Al-Mistarehi, Abdel-Hameed, Alzoubi, Hamed, Bani Mousa, Ayman Ahmad, Allouh, Mohammed Z.

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Genetically corrected RAG2-SCID human hematopoietic stem cells restore V(D)J-recombinase and rescue lymphoid deficiency von Pavel-Dinu, Mara, Gardner, Cameron L., Nakauchi, Yusuke, Kawai, Tomoki, Delmonte, Ottavia M., Palterer, Boaz, Bosticardo, Marita, Pala, Francesca, Viel, Sebastien, Malech, Harry L., Ghanim, Hana Y., Bode, Nicole M., Kurgan, Gavin L., Detweiler, Angela M., Vakulskas, Christopher A., Neff, Norma F., Sheikali, Adam, Menezes, Sherah T., Chrobok, Jade, Hernández González, Elaine M., Majeti, Ravindra, Notarangelo, Luigi D., Porteus, Matthew H.

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The Binns Program for Cord Blood Research: A Novel Program for Cord Blood Procurement in an Academic Setting for Biomedical Research von Sheikali, Adam, Mantri, Sruthi, Lyell, Deirdre, Porteus, Matt, Agarwal, Rajni

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Physician workforce in otolaryngology von JAFEK, B.W., SLENKOVICH, N., SHEIKALI, S.

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Data from: Highway to the danger zone: exposure-dependent costs of immunity in a vertebrate ectotherm von Brace, Amber J., Sheikali, Sam, Martin, Lynn B.

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13C allocation and individual descriptives von Brace, Amber J., Sheikali, Sam, Martin, Lynn B.

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