Elexacaftor–Tezacaftor–Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele von Middleton, Peter G, Mall, Marcus A, Dřevínek, Pavel, Lands, Larry C, McKone, Edward F, Polineni, Deepika, Ramsey, Bonnie W, Taylor-Cousar, Jennifer L, Tullis, Elizabeth, Vermeulen, François, Marigowda, Gautham, McKee, Charlotte M, Moskowitz, Samuel M, Nair, Nitin, Savage, Jessica, Simard, Christopher, Tian, Simon, Waltz, David, Xuan, Fengjuan, Rowe, Steven M, Jain, Raksha

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Lumacaftor–Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del CFTR von Wainwright, Claire E, Elborn, J. Stuart, Ramsey, Bonnie W, Marigowda, Gautham, Huang, Xiaohong, Cipolli, Marco, Colombo, Carla, Davies, Jane C, De Boeck, Kris, Flume, Patrick A, Konstan, Michael W, McColley, Susanna A, McCoy, Karen, McKone, Edward F, Munck, Anne, Ratjen, Felix, Rowe, Steven M, Waltz, David, Boyle, Michael P

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Ivacaftor treatment of cystic fibrosis in children aged 12 to <24 months and with a CFTR gating mutation (ARRIVAL): a phase 3 single-arm study von Rosenfeld, Margaret, Wainwright, Claire E, Higgins, Mark, Wang, Linda T, McKee, Charlotte, Campbell, Daniel, Tian, Simon, Schneider, Jennifer, Cunningham, Steve, Davies, Jane C, Rosenfeld, Margaret, Wainwright, Claire E., Higgins, Mark, Wang, Linda T., McKee, Charlotte, Campbell, Daniel, Tian, Simon, Schneider, Jennifer, Cunningham, Steve, Davies, Jane C., Harris, William, Mogayzel, Peter, McCoy, Karen, Milla, Carlos, Rubenstein, Ronald, Walker, Seth, Black, Philip, Montgomery, Gregory, McColley, Susanna, Hiatt, Peter, Sawicki, Gregory, Rock, Michael, Aurora, Paul, Ratjen, Felix, Maitra, Anirban, Ives, Andrew, Gaillard, Erol, McNalley, Paul, Selvadurai, Hiranjan, Robinson, Philip

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Efficacy and safety of lumacaftor and ivacaftor in patients aged 6–11 years with cystic fibrosis homozygous for F508del-CFTR : a randomised, placebo-controlled phase 3 trial von Ratjen, Felix, Prof, Hug, Christopher, MD, Marigowda, Gautham, MD, Tian, Simon, MD, Huang, Xiaohong, PhD, Stanojevic, Sanja, PhD, Milla, Carlos E, MD, Robinson, Paul D, MBChB, Waltz, David, MD, Davies, Jane C, Prof

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Long-term safety and efficacy of tezacaftor–ivacaftor in individuals with cystic fibrosis aged 12 years or older who are homozygous or heterozygous for Phe508del CFTR (EXTEND): an... von Flume, Patrick A, Downey, Damian G, Brown, Cynthia, Fischer, Rainald, De Boeck, Kris, Chang, Philip, Rubin, Jaime L, Yang, Yoojung, Wang, Xin, Ahluwalia, Neil, Owen, Caroline A, Ahrens, Richard C., Aitken, Moira, McBennett, Kimberly Ann, Pilewski, Joseph M., Billings, Joanne, Linnemann, Rachel, Powers, Michael R., Frederick, Carla Anne, Black, Philip, Berdella, Maria, Brown, Cynthia D., Anstead, Michael, Sicilian, Leonard, Moffett, Kathryn, Nasr, Samya, Taylor-Cousar, Jennifer, Barto, Tara Lynn, Antos, Nicholas, Quick, Bryon, Thompson, Henry R., Sawicki, Gregory, Smith, Thomas C., Schultz, Karen D., Omlor, Gregory J., Mehdi, Nighat, Ortiz, Maria Gabriela Tupayachi, Gardner, Tonia E., Jain, Raksha, Berlinski, Ariel, Calimano, Francisco J., Lascano, Jorge E., McWilliams, Bennie, Morrissey, Brian, Chittivelu, Subramanyam, Klingsberg, Ross, Biller, Julie A., Bui, Stephanie, Sommerburg, Olaf, Bignamini, Elisabetta, Collura, Mirella, Bentur, Lea, Efrati, Ori, Gallego, Esther Quintana, Barry, Peter, Asensi, Jose Ramon Villa, Armstrong, David Stuart, de la Cruz, Oscar Asensio, Gilchrist, Francis, Lands, Larry C., Lavoie, Annick, Linnane, Barry, Elidemir, Okan, Ringshausen, Felix, Kappler, Matthias, Hebestreit, Helge, Mainz, Jochen, Staab, Doris, Gleiber, Wolfgang, Pressler, Tacjana, Ketchell, Robert Ian, Doe, Simon, Nash, Edward Fairbairn, Peckham, Daniel Gavin, Kansra, Sonal, Delaisi, Bertrand, Le Bihan, Jean, Fajac, Isabelle, Sermet-Gaudelus, Isabelle, De Boeck, Christiane, Reix, Philippe, van Braeckel, Eva, Prevotat, Anne, van der Meer, Renske, Weersink, E.J.M., Gartner, Silvia, Jover, Amparo Sole, Fernandez, Antonio Alvarez, Cox, Desmond William, McKone, Edward F., Bowler, Simon David, Wainwright, Claire Elizabeth, Wilson, John William, Volpi, Sonia, Colombo, Carla, Fabrizzi, Benedetta, Lucidi, Vincenzina, Cucchiara, Salvatore, Eber, Ernst, Krantz, Christina

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