Effective gene therapy of Stargardt disease with PEG-ECO/pGRK1-ABCA4-S/MAR nanoparticles von Sun, Da, Sun, Wenyu, Gao, Song-Qi, Lehrer, Jonathan, Naderi, Amirreza, Wei, Cheng, Lee, Sangjoon, Schilb, Andrew L., Scheidt, Josef, Hall, Ryan C., Traboulsi, Elias I., Palczewski, Krzysztof, Lu, Zheng-Rong

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Optimization of Synthesis of the Amino Lipid ECO for Effective Delivery of Nucleic Acids von Schilb, Andrew L., Scheidt, Josef H., Vaidya, Amita M., Sun, Zhanhu, Sun, Da, Lee, Sangjoon, Lu, Zheng-Rong

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Formulation and efficacy of ECO/pRHO-ABCA4-SV40 nanoparticles for nonviral gene therapy of Stargardt disease in a mouse model von Sun, Da, Sun, Wenyu, Gao, Song-Qi, Wei, Cheng, Naderi, Amirreza, Schilb, Andrew L., Scheidt, Josef, Lee, Sangjoon, Kern, Timothy S., Palczewski, Krzysztof, Lu, Zheng-Rong

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Efficacy of Targeted ECO/miR-200c Nanoparticles for Modulating Tumor Microenvironment and Treating Triple Negative Breast Cancer as Non-invasively Monitored by MR Molecular Imaging von Schilb, Andrew L., Ayat, Nadia R., Vaidya, Amita M., Hertz, Laura M., Hall, Ryan C., Scheidt, Josef H., Sun, Da, Sun, Zhanhu, Gopalakrishnan, Ramamurthy, Lu, Zheng-Rong

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Synthesis and Evaluation of pH-Sensitive Multifunctional Lipids for Efficient Delivery of CRISPR/Cas9 in Gene Editing von Sun, Da, Sun, Zhanhu, Jiang, Hongfa, Vaidya, Amita M, Xin, Rui, Ayat, Nadia R, Schilb, Andrew L, Qiao, Peter L, Han, Zheng, Naderi, Amirreza, Lu, Zheng-Rong

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Formulation of Biocompatible Targeted ECO/siRNA Nanoparticles with Long-Term Stability for Clinical Translation of RNAi von Ayat, Nadia R., Sun, Zhanhu, Sun, Da, Yin, Michelle, Hall, Ryan C., Vaidya, Amita M., Liu, Xujie, Schilb, Andrew L., Scheidt, Josef H., Lu, Zheng-Rong

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