Biology of adeno-associated viral vectors in the central nervous system von Murlidharan, Giridhar, Samulski, Richard J, Asokan, Aravind

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Engraftment of a Galactose Receptor Footprint onto Adeno-associated Viral Capsids Improves Transduction Efficiency von Shen, Shen, Horowitz, Eric D., Troupes, Andrew N., Brown, Sarah M., Pulicherla, Nagesh, Samulski, Richard.J., Agbandje-McKenna, Mavis, Asokan, Aravind

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Packaging Capacity of Adeno-Associated Virus Serotypes: Impact of Larger Genomes on Infectivity and Postentry Steps von GRIEGER, Joshua C, SAMULSKI, Richard J

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Engineering and Selection of Shuffled AAV Genomes: A New Strategy for Producing Targeted Biological Nanoparticles von Li, Wuping, Asokan, Aravind, Wu, Zhijian, Van Dyke, Terry, DiPrimio, Nina, Johnson, Jarrod S, Govindaswamy, Lakshmanan, Agbandje-McKenna, Mavis, Leichtle, Stefan, Eugene Redmond Jr, D, McCown, Thomas J, Petermann, Kimberly B, Sharpless, Norman E, Samulski, Richard J

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Separate Basic Region Motifs within the Adeno-Associated Virus Capsid Proteins Are Essential for Infectivity and Assembly von GRIEGER, Joshua C, SNOWDY, Stephen, SAMULSKI, Richard J

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Adeno-Associated Virus Type 2 Contains an Integrin α5β1 Binding Domain Essential for Viral Cell Entry von ASOKAN, Aravind, HAMRA, Julie B, GOVINDASAMY, Lakshmanan, AGBANDJE-MCKENNA, Mavis, SAMULSKI, Richard J

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Optimization of Self-complementary AAV Vectors for Liver-directed Expression Results in Sustained Correction of Hemophilia B at Low Vector Dose von Wu, Zhijian, Sun, Junjiang, Zhang, Taiping, Yin, Chaoying, Yin, Fang, Van Dyke, Terry, Samulski, Richard J, Monahan, Paul E

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Self-complementary adeno-associated virus serotype 2 vector: global distribution and broad dispersion of AAV-mediated transgene expression in mouse brain von Fu, Haiyan, Muenzer, Joseph, Samulski, Richard J, Breese, George, Sifford, Jerillyn, Zeng, Xinhua, McCarty, Douglas M

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Supramolecular Nanomimetics: Replication of Micelles, Viruses, and Other Naturally Occurring Nanoscale Objects von Maynor, Benjamin W., LaRue, Isaac, Hu, Zhaokang, Rolland, Jason P., Pandya, Ashish, Fu, Qiang, Liu, Jie, Spontak, Richard J., Sheiko, Sergei S., Samulski, Richard J., Samulski, Edward T., DeSimone, Joseph M.

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Comparison of Fetal Mesencephalic Grafts, AAV-delivered GDNF, and Both Combined in an MPTP-induced Nonhuman Primate Parkinson’s Model von Redmond, D Eugene, McEntire, Caleb R S, Kingsbery, Joseph P, Leranth, Csaba, Elsworth, John D, Bjugstad, Kimberly B, Roth, Robert H, Samulski, Richard J, Sladek, John R

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Autoimmune anemia in macaques following erythropoietin gene therapy von Chenuaud, Pierre, Larcher, Thibaut, Rabinowitz, Joseph E., Provost, Nathalie, Cherel, Yan, Casadevall, Nicole, Samulski, Richard J., Moullier, Philippe

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Gene Delivery of Activated Factor VII Using Alternative Adeno-Associated Virus Serotype Improves Hemostasis in Hemophiliac Mice with FVIII Inhibitors and Adeno-Associated Virus Neu... von Sun, Junjiang, Hua, Baolai, Chen, Xiaojing, Samulski, Richard J, Li, Chengwen

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Inhibition of antigen presentation during AAV gene therapy using virus peptides von Shao, Wenwei, Chen, Xiaojing, Samulski, Richard J, Hirsch, Matthew L, Li, Chengwen

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Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain von Kaplitt, Michael G, Leone, Paola, Samulski, Richard J, Xiao, Xiao, Pfaff, Donald W, O'Malley, Karen L, During, Matthew J

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Adeno-Associated Virus Type 2 Contains an Integrin alpha 5 beta 1 Binding Domain Essential for Viral Cell Entry von Asokan, Aravind, Hamra, Julie B, Govindasamy, Lakshmanan, Agbandje-McKenna, Mavis, Samulski, Richard J

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Impact of neutralizing antibodies against AAV is a key consideration in gene transfer to nonhuman primates von Xiao, Weidong, Gao, Guangping, Ling, Chen, Herzog, Roland W., Xiao, Xiao, Samulski, Richard J.

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Genetic modification of scAAV‐equine‐BMP‐2 transduced bone‐marrow‐derived mesenchymal stem cells before and after cryopreservation: An “off‐the‐shelf” option for fracture repair... von Ball, Alyssa N., Phillips, Jennifer N., McIlwraith, C. Wayne, Kawcak, Christopher E., Samulski, Richard J., Goodrich, Laurie R.

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Overexpression of SOD in retina: Need for increase in H2O2-detoxifying enzyme in same cellular compartment von Usui, Shinichi, Oveson, Brian C., Iwase, Takeshi, Lu, Lili, Lee, Sun Young, Jo, Young-Joon, Wu, Zhihao, Choi, Eun-Young, Samulski, Richard J., Campochiaro, Peter A.

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Efficient Retrograde Neuronal Transduction Utilizing Self-complementary AAV1 von Hollis II, Edmund R, Kadoya, Ken, Hirsch, Matthew, Samulski, Richard J, Tuszynski, Mark H

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Self-complementary AAV Virus (scAAV) Safe and Long-term Gene Transfer in the Trabecular Meshwork of Living Rats and Monkeys von Buie, LaKisha K, Rasmussen, Carol A, Porterfield, Eric C, Ramgolam, Vinod S, Choi, Vivian W, Markovic-Plese, Silva, Samulski, Richard J, Kaufman, Paul L, Borras, Teresa

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