Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study von Ferrua, F, Cicalese, MP, Galimberti, S, Giannelli, S, Dionisio, F, Barzaghi, F, Migliavacca, M, Bernardo, ME, Calbi, V, Assanelli, AA, Facchini, M, Fossati, C, Albertazzi, E, Scaramuzza, S, Brigida, I, Scala, S, Basso-Ricci, L, Pajno, R, Casiraghi, M, Canarutto, D, Salerio, FA, Albert, MH, Bartoli, A, Wolf, HM, Fiori, R, Silvani, P, Gattillo, S, Villa, A, Biasco, L, Dott, C, Culme-Seymour, EJ, van Rossem, K, Atkinson, G, Valsecchi, MG, Roncarolo, MG, Ciceri, F, Naldini, L, Aiuti, A

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