Gene therapy for neurological disorders: progress and prospects von Deverman, Benjamin E., Ravina, Bernard M., Bankiewicz, Krystof S., Paul, Steven M., Sah, Dinah W. Y.

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Control of phosphorothioate stereochemistry substantially increases the efficacy of antisense oligonucleotides von Iwamoto, Naoki, Butler, David C D, Svrzikapa, Nenad, Mohapatra, Susovan, Zlatev, Ivan, Sah, Dinah W Y, Meena, Standley, Stephany M, Lu, Genliang, Apponi, Luciano H, Frank-Kamenetsky, Maria, Zhang, Jason Jingxin, Vargeese, Chandra, Verdine, Gregory L

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Gene therapy for neurological disorders: progress and prospects von Deverman, Benjamin E, Ravina, Bernard M, Bankiewicz, Krystof S, Paul, Steven M, Sah, Dinah W Y

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Safety and Efficacy of RNAi Therapy for Transthyretin Amyloidosis von Coelho, Teresa, Adams, David, Silva, Ana, Lozeron, Pierre, Hawkins, Philip N, Mant, Timothy, Perez, Javier, Chiesa, Joseph, Warrington, Steve, Tranter, Elizabeth, Munisamy, Malathy, Falzone, Rick, Harrop, Jamie, Cehelsky, Jeffrey, Bettencourt, Brian R, Geissler, Mary, Butler, James S, Sehgal, Alfica, Meyers, Rachel E, Chen, Qingmin, Borland, Todd, Hutabarat, Renta M, Clausen, Valerie A, Alvarez, Rene, Fitzgerald, Kevin, Gamba-Vitalo, Christina, Nochur, Saraswathy V, Vaishnaw, Akshay K, Sah, Dinah W.Y, Gollob, Jared A, Suhr, Ole B

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RNAi therapeutics: a potential new class of pharmaceutical drugs von Sah, Dinah W Y, Bumcrot, David, Manoharan, Muthiah, Koteliansky, Victor

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Tumor heterogeneity is an active process maintained by a mutant EGFR-induced cytokine circuit in glioblastoma von Inda, Maria-del-Mar, Bonavia, Rudy, Mukasa, Akitake, Narita, Yoshitaka, Sah, Dinah W Y, Vandenberg, Scott, Brennan, Cameron, Johns, Terrance G, Bachoo, Robert, Hadwiger, Philipp, Tan, Pamela, Depinho, Ronald A, Cavenee, Webster, Furnari, Frank

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Lipid-like materials for low-dose, in vivo gene silencing von Love, Kevin T, Mahon, Kerry P, Levins, Christopher G, Whitehead, Kathryn A, Querbes, William, Dorkin, J. Robert, Qin, June, Cantley, William, Qin, Liu Liang, Racie, Timothy, Frank-Kamenetsky, Maria, Yip, Ka Ning, Alvarez, Rene, Sah, Dinah W.Y, de Fougerolles, Antonin, Fitzgerald, Kevin, Koteliansky, Victor, Akinc, Akin, Langer, Robert, Anderson, Daniel G

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Blockade of Nogo-66, Myelin-Associated Glycoprotein, and Oligodendrocyte Myelin Glycoprotein by Soluble Nogo-66 Receptor Promotes Axonal Sprouting and Recovery after Spinal Injury von Li, Shuxin, Liu, Betty P, Budel, Stephane, Li, Mingwei, Ji, Benxiu, Walus, Lee, Li, Weiwei, Jirik, Adrienna, Rabacchi, Sylvia, Choi, Eugene, Worley, Dane, Sah, Dinah W. Y, Pepinsky, Blake, Lee, Daniel, Relton, Jane, Strittmatter, Stephen M

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Targeted Delivery of RNAi Therapeutics With Endogenous and Exogenous Ligand-Based Mechanisms von Akinc, Akin, Querbes, William, De, Soma, Qin, June, Frank-Kamenetsky, Maria, Jayaprakash, K. Narayanannair, Jayaraman, Muthusamy, Rajeev, Kallanthottathil G, Cantley, William L, Dorkin, J Robert, Butler, James S, Qin, LiuLiang, Racie, Timothy, Sprague, Andrew, Fava, Eugenio, Zeigerer, Anja, Hope, Michael J, Zerial, Marino, Sah, Dinah WY, Fitzgerald, Kevin, Tracy, Mark A, Manoharan, Muthiah, Koteliansky, Victor, Fougerolles, Antonin de, Maier, Martin A

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A combinatorial library of lipid-like materials for delivery of RNAi therapeutics von Anderson, Daniel G, Akinc, Akin, Zumbuehl, Andreas, Goldberg, Michael, Leshchiner, Elizaveta S, Busini, Valentina, Hossain, Naushad, Bacallado, Sergio A, Nguyen, David N, Fuller, Jason, Alvarez, Rene, Borodovsky, Anna, Borland, Todd, Constien, Rainer, de Fougerolles, Antonin, Dorkin, J Robert, Narayanannair Jayaprakash, K, Jayaraman, Muthusamy, John, Matthias, Koteliansky, Victor, Manoharan, Muthiah, Nechev, Lubomir, Qin, June, Racie, Timothy, Raitcheva, Denitza, Rajeev, Kallanthottathil G, Sah, Dinah W Y, Soutschek, Jürgen, Toudjarska, Ivanka, Vornlocher, Hans-Peter, Zimmermann, Tracy S, Langer, Robert

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Widespread suppression of huntingtin with convection-enhanced delivery of siRNA von Stiles, David K., Zhang, Zhiming, Ge, Pei, Nelson, Brian, Grondin, Richard, Ai, Yi, Hardy, Peter, Nelson, Peter T., Guzaev, Andrei P., Butt, Mark T., Charisse, Klaus, Kosovrasti, Verbena, Tchangov, Lubomir, Meys, Michael, Maier, Martin, Nechev, Lubomir, Manoharan, Muthiah, Kaemmerer, William F., Gwost, Douglas, Stewart, Gregory R., Gash, Don M., Sah, Dinah W.Y.

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Lipophilic siRNAs mediate efficient gene silencing in oligodendrocytes with direct CNS delivery von Chen, Qingmin, Butler, David, Querbes, William, Pandey, Rajendra K., Ge, Pei, Maier, Martin A., Zhang, Ligang, Rajeev, Kallanthottathil G., Nechev, Lubomir, Kotelianski, Victor, Manoharan, Muthiah, Sah, Dinah W.Y.

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Artemin induced functional recovery and reinnervation after partial nerve injury von Wang, Ruizhong, Rossomando, Anthony, Sah, Dinah W.Y., Ossipov, Michael H., King, Tamara, Porreca, Frank

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Oligonucleotide therapeutic approaches for Huntington disease von Sah, Dinah W Y, Aronin, Neil

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siRNA knock-down of mutant torsinA restores processing through secretory pathway in DYT1 dystonia cells von Hewett, Jeffrey W., Nery, Flávia C., Niland, Brian, Ge, Pei, Tan, Pamela, Hadwiger, Philipp, Tannous, Bakhos A., Sah, Dinah W.Y., Breakefield, Xandra O.

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Therapeutic potential of RNA interference for neurological disorders von Sah, Dinah W.Y.

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Targeting the Nogo Receptor to Treat Central Nervous System Injuries von Lee, Daniel H. S, Strittmatter, Stephen M, Sah, Dinah W. Y

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Tissue-specific gene silencing monitored in circulating RNA von Sehgal, Alfica, Chen, Qingmin, Gibbings, Derrick, Sah, Dinah W Y, Bumcrot, David

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Persistent restoration of sensory function by immediate or delayed systemic artemin after dorsal root injury von Cariani, Peter, Vanderah, Todd W, Porreca, Frank, Wang, Ruizhong, Frank, Eric, Ossipov, Michael H, Harvey, Pamela, King, Tamara, Rossomando, Anthony J, Sah, Dinah W Y

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First-in-humans trial of an RNA interference therapeutic targeting VEGF and KSP in cancer patients with liver involvement von Tabernero, Josep, Shapiro, Geoffrey I, LoRusso, Patricia M, Cervantes, Andres, Schwartz, Gary K, Weiss, Glen J, Paz-Ares, Luis, Cho, Daniel C, Infante, Jeffrey R, Alsina, Maria, Gounder, Mrinal M, Falzone, Rick, Harrop, Jamie, White, Amy C Seila, Toudjarska, Iva, Bumcrot, David, Meyers, Rachel E, Hinkle, Gregory, Svrzikapa, Nenad, Hutabarat, Renta M, Clausen, Valerie A, Cehelsky, Jeffrey, Nochur, Saraswathy V, Gamba-Vitalo, Christina, Vaishnaw, Akshay K, Sah, Dinah W Y, Gollob, Jared A, Burris, 3rd, Howard A

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