TRIAMF: A New Method for Delivery of Cas9 Ribonucleoprotein Complex to Human Hematopoietic Stem Cells von Yen, Jonathan, Fiorino, Michael, Liu, Yi, Paula, Steve, Clarkson, Scott, Quinn, Lisa, Tschantz, William R., Klock, Heath, Guo, Ning, Russ, Carsten, Yu, Vionnie W. C., Mickanin, Craig, Stevenson, Susan C., Lee, Cameron, Yang, Yi

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Transducer of Regulated CREB-Binding Proteins (TORCs) Induce PGC-1α Transcription and Mitochondrial Biogenesis in Muscle Cells von Wu, Zhidan, Huang, Xueming, Feng, Yajun, Handschin, Christoph, Feng, Yan, Gullicksen, P. Scott, Bare, Olivia, Labow, Mark, Spiegelman, Bruce, Stevenson, Susan C.

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CRISPR-Cas9 Editing of the HBG1 and HBG2 Promoters to Treat Sickle Cell Disease von Sharma, Akshay, Boelens, Jaap-Jan, Cancio, Maria, Hankins, Jane S., Bhad, Prafulla, Azizy, Marjohn, Lewandowski, Andrew, Zhao, Xiaojun, Chitnis, Shripad, Peddinti, Radhika, Zheng, Yan, Kapoor, Neena, Ciceri, Fabio, Maclachlan, Timothy, Yang, Yi, Liu, Yi, Yuan, Jianping, Naumann, Ulrike, Yu, Vionnie W.C., Stevenson, Susan C., De Vita, Serena, LaBelle, James L.

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Collaborative science to advance gene therapies in resource-limited parts of the world von McCune, Joseph M., Stevenson, Susan C., Doehle, Brian P., Trenor, Cameron C., Turner, Emily H., Spector, Jonathan M.

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Muscle-specific expression of PPARγ coactivator-1α improves exercise performance and increases peak oxygen uptake von CALVO, Jennifer A, DANIELS, Thomas G, XIAOMEI WANG, PAUL, Angelika, JIANDIE LIN, SPIEGELMAN, Bruce M, STEVENSON, Susan C, RANGWALA, Shamina M

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A molecular glue degrader of the WIZ transcription factor for fetal hemoglobin induction von Ting, Pamela Y, Borikar, Sneha, Kerrigan, John Ryan, Thomsen, Noel M, Aghania, Eamon, Hinman, Amelia E, Reyes, Alejandro, Pizzato, Nicolas, Fodor, Barna D, Wu, Fabian, Belew, Muluken S, Mao, Xiaohong, Wang, Jian, Chitnis, Shripad, Niu, Wei, Hachey, Amanda, Cobb, Jennifer S, Savage, Nikolas A, Burke, Ashley, Paulk, Joshiawa, Dovala, Dustin, Lin, James, Clifton, Matthew C, Ornelas, Elizabeth, Ma, Xiaolei, Ware, Nathaniel F, Sanchez, Carina C, Taraszka, John, Terranova, Remi, Knehr, Judith, Altorfer, Marc, Barnes, S Whitney, Beckwith, Rohan E J, Solomon, Jonathan M, Dales, Natalie A, Patterson, Andrew W, Wagner, Jürgen, Bouwmeester, Tewis, Dranoff, Glenn, Stevenson, Susan C, Bradner, James E

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Receptor interactions involved in adenoviral-mediated gene delivery after systemic administration in non-human primates von SMITH, Theodore A. G, IDAMAKANTI, Neeraja, SHERER, Alfred D, MARKOVITS, Judit E, LYONS, Russette M, KALEKO, Michael, STEVENSON, Susan C, MARSHALL-NEFF, Jennifer, ROLLENCE, Michele L, WRIGHT, Patrick, KALOSS, Michele, KING, Laura, MECH, Christine, DINGES, Lisa, IVERSON, William O

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In Vivo Hepatic Adenoviral Gene Delivery Occurs Independently of the Coxsackievirus–Adenovirus Receptor von Smith, Theodore, Idamakanti, Neeraja, Kylefjord, Helen, Rollence, Michele, King, Laura, Kaloss, Michele, Kaleko, Michael, Stevenson, Susan C.

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Targeting Adenoviral Vectors by Using the Extracellular Domain of the Coxsackie-Adenovirus Receptor: Improved Potency via Trimerization von Kim, Jin, Smith, Theodore, Idamakanti, Neeraja, Mulgrew, Kathy, Kaloss, Michele, Kylefjord, Helen, Ryan, Patricia C, Kaleko, Michael, Stevenson, Susan C

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Identification of novel modulators of mitochondrial function by a genome-wide RNAi screen in Drosophila melanogaster von Chen, Jian, Shi, Xiaoying, Padmanabhan, Ranjani, Wang, Qiong, Wu, Zhidan, Stevenson, Susan C, Hild, Marc, Garza, Dan, Li, Hao

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Adenovirus serotype 5 fiber shaft influences in vivo gene transfer in mice von SMITH, Theodore A. G, IDAMAKANTI, Neeraja, ROLLENCE, Michele L, MARSHALL-NEFF, Jennifer, JIN KIM, MULGREW, Kathy, NEMEROW, Glen R, KALEKO, Michael, STEVENSON, Susan C

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Interaction of Systemically Delivered Adenovirus Vectors with Kupffer Cells in Mouse Liver von SMITH, Jeffrey S, ZHILI XU, JIE TIAN, STEVENSON, Susan C, BYRNES, Andrew P

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Estrogen-related receptor α is essential for the expression of antioxidant protection genes and mitochondrial function von Rangwala, Shamina M., Li, Xiaoyan, Lindsley, Loren, Wang, Xiaomei, Shaughnessy, Stacey, Daniels, Thomas G., Szustakowski, Joseph, Nirmala, N.R., Wu, Zhidan, Stevenson, Susan C.

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Effect of adenovirus serotype 5 fiber and penton modifications on in vivo tropism in rats von Nicol, Campbell G, Graham, Delyth, Miller, William H, White, Stephen J, Smith, Theodore A G, Nicklin, Stuart A, Stevenson, Susan C, Baker, Andrew H

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Gene Therapy With Inducible Nitric Oxide Synthase Protects Against Myocardial Infarction via a Cyclooxygenase-2-Dependent Mechanism von Li, Qianhong, Guo, Yiru, Xuan, Yu-Ting, Lowenstein, Charles J, Stevenson, Susan C, Prabhu, Sumanth D, Wu, Wen-Jian, Zhu, Yanqing, Bolli, Roberto

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Adenovirus Vector Pseudotyping in Fiber-Expressing Cell Lines: Improved Transduction of Epstein-Barr Virus-Transformed B Cells von Von Seggern, D J, Huang, S, Fleck, S K, Stevenson, S C, Nemerow, G R

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Adenovirus Type 5 Viral Particles Pseudotyped with Mutagenized Fiber Proteins Show Diminished Infectivity of Coxsackie B-Adenovirus Receptor-Bearing Cells von Jakubczak, J L, Rollence, M L, Stewart, D A, Jafari, J D, Von Seggern, D J, Nemerow, G R, Stevenson, S C, Hallenbeck, P L

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Treatment of Individuals with Severe Sickle Cell Disease with OTQ923, an Autologous, Ex Vivo, CRISPR/Cas9-Edited, CD34+ Hematopoietic Stem and Progenitor Cell Product, Leads to Dur... von Sharma, Akshay, Boelens, Jaap Jan, Cancio, Maria I., Hankins, Jane, Bhad, Prafulla A, Lewandowski, Andrew, Zhao, Xiaojun, Chitnis, Shripad, Peddinti, Radhika, Zheng, Yan, Kapoor, Neena, Ciceri, Fabio, Yuan, Jianping, Yu, Vionnie W., Stevenson, Susan C., De Vita, Serena, LaBelle, James

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CRISPR/Cas9 Genome-Edited Autologous Hematopoietic Stem Cell Transplantation Therapies for Sickle Cell Disease von Liu, Yi, Yu, Vionnie W., Zhang, Qi, Panditrao, Madhura, Yang, Yi, Rio-Espinola, Alberto Del, Aibo, Daher Ibrahim, Elhajouji, Azeddine, Mueller, Konrad, Abitorabi, Karin, O'Connell, Daniel, Han, Bo, Patel, Nishit, Russ, Carsten, Mickanin, Craig, MacLachlan, Timothy K., Stevenson, Susan C.

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381. The Adenoviral Fiber Shaft Is a Major Determinant of Kupffer Cell Necrosis von Smith, Jeffrey S., Tian, Jie, Stevenson, Susan C., Byrnes, Andrew P.

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