An orally available, brain penetrant, small molecule lowers huntingtin levels by enhancing pseudoexon inclusion von Keller, Caroline Gubser, Shin, Youngah, Monteys, Alex Mas, Renaud, Nicole, Beibel, Martin, Teider, Natalia, Peters, Thomas, Faller, Thomas, St-Cyr, Sophie, Knehr, Judith, Roma, Guglielmo, Reyes, Alejandro, Hild, Marc, Lukashev, Dmitriy, Theil, Diethilde, Dales, Natalie, Cha, Jang-Ho, Borowsky, Beth, Dolmetsch, Ricardo, Davidson, Beverly L., Sivasankaran, Rajeev

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Plasma phosphorylated tau 217 and phosphorylated tau 181 as biomarkers in Alzheimer's disease and frontotemporal lobar degeneration: a retrospective diagnostic performance study von Thijssen, Elisabeth H, La Joie, Renaud, Strom, Amelia, Fonseca, Corrina, Iaccarino, Leonardo, Wolf, Amy, Spina, Salvatore, Allen, Isabel E, Cobigo, Yann, Heuer, Hilary, VandeVrede, Lawren, Proctor, Nicholas K, Lago, Argentina Lario, Baker, Suzanne, Sivasankaran, Rajeev, Kieloch, Agnieszka, Kinhikar, Arvind, Yu, Lili, Valentin, Marie-Anne, Jeromin, Andreas, Zetterberg, Henrik, Hansson, Oskar, Mattsson-Carlgren, Niklas, Graham, Danielle, Blennow, Kaj, Kramer, Joel H, Grinberg, Lea T, Seeley, William W, Rosen, Howard, Boeve, Bradley F, Miller, Bruce L, Teunissen, Charlotte E, Rabinovici, Gil D, Rojas, Julio C, Dage, Jeffrey L, Boxer, Adam L

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Synthetic transcription elongation factors license transcription across repressive chromatin von Erwin, Graham S., Grieshop, Matthew P., Ali, Asfa, Qi, Jun, Lawlor, Matthew, Kumar, Deepak, Ahmad, Istaq, McNally, Anna, Teider, Natalia, Worringer, Katie, Sivasankaran, Rajeev, Syed, Deeba N., Eguchi, Asuka, Ashraf, Md, Jeffery, Justin, Xu, Mousheng, Park, Paul M. C., Mukhtar, Hasan, Srivastava, Achal K., Faruq, Mohammed, Bradner, James E., Ansari, Aseem Z.

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Plasma Tau and Neurofilament Light in Frontotemporal Lobar Degeneration and Alzheimer Disease von Illán-Gala, Ignacio, Lleo, Alberto, Karydas, Anna, Staffaroni, Adam M., Zetterberg, Henrik, Sivasankaran, Rajeev, Grinberg, Lea T., Spina, Salvatore, Kramer, Joel H., Ramos, Eliana M., Coppola, Giovanni, La Joie, Renaud, Rabinovici, Gil D., Perry, David C., Gorno-Tempini, Maria Luisa, Seeley, William W., Miller, Bruce L., Rosen, Howard J., Blennow, Kaj, Boxer, Adam L., Rojas, Julio C.

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Discovery of Small Molecule Splicing Modulators of Survival Motor Neuron‑2 (SMN2) for the Treatment of Spinal Muscular Atrophy (SMA) von Cheung, Atwood K, Hurley, Brian, Kerrigan, Ryan, Shu, Lei, Chin, Donovan N, Shen, Yiping, O’Brien, Gary, Sung, Moo Je, Hou, Ying, Axford, Jake, Cody, Emma, Sun, Robert, Fazal, Aleem, Tomlinson, Ronald C, Jain, Monish, Deng, Lin, Hoffmaster, Keith, Song, Cheng, Van Hoosear, Mailin, Shin, Youngah, Servais, Rebecca, Towler, Christopher, Hild, Marc, Curtis, Daniel, Dietrich, William F, Hamann, Lawrence G, Briner, Karin, Chen, Karen S, Kobayashi, Dione, Sivasankaran, Rajeev, Dales, Natalie A

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Orally administered branaplam does not impact neurogenesis in juvenile mice, rats, and dogs von Theil, Diethilde, Valdez, Reginald, Darribat, Katy, Doelemeyer, Arno, Sivasankaran, Rajeev, Hartmann, Andreas

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PKC mediates inhibitory effects of myelin and chondroitin sulfate proteoglycans on axonal regeneration von Sivasankaran, Rajeev, Pei, Jiong, Wang, Kevin C, Zhang, Yi Ping, Shields, Christopher B, Xu, Xiao-Ming, He, Zhigang

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Phosphorylated FTY720 promotes astrocyte migration through sphingosine‐1‐phosphate receptors von Mullershausen, Florian, Craveiro, Luis M., Shin, Youngah, Cortes‐Cros, Marta, Bassilana, Frederic, Osinde, Maribel, Wishart, William L., Guerini, Danilo, Thallmair, Michaela, Schwab, Martin E., Sivasankaran, Rajeev, Seuwen, Klaus, Dev, Kumlesh K.

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Genetic circuitry of Survival motor neuron, the gene underlying spinal muscular atrophy von Sen, Anindya, Dimlich, Douglas N, Guruharsha, K G, Kankel, Mark W, Hori, Kazuya, Yokokura, Takakazu, Brachat, Sophie, Richardson, Delwood, Loureiro, Joseph, Sivasankaran, Rajeev, Curtis, Daniel, Davidow, Lance S, Rubin, Lee L, Hart, Anne C, Van Vactor, David, Artavanis-Tsakonas, Spyros

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Identification of novel genes and pathways regulating SREBP transcriptional activity von Chatterjee, Sandipan, Szustakowski, Joseph D, Nanguneri, Nirmala R, Mickanin, Craig, Labow, Mark A, Nohturfft, Axel, Dev, Kumlesh K, Sivasankaran, Rajeev

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Regulated control of gene therapies by drug-induced splicing von Monteys, Alex Mas, Hundley, Amiel A., Ranum, Paul T., Tecedor, Luis, Muehlmatt, Amy, Lim, Euyn, Lukashev, Dmitriy, Sivasankaran, Rajeev, Davidson, Beverly L.

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SMN2 splice modulators enhance U1–pre-mRNA association and rescue SMA mice von Palacino, James, Swalley, Susanne E, Song, Cheng, Cheung, Atwood K, Shu, Lei, Zhang, Xiaolu, Van Hoosear, Mailin, Shin, Youngah, Chin, Donovan N, Keller, Caroline Gubser, Beibel, Martin, Renaud, Nicole A, Smith, Thomas M, Salcius, Michael, Shi, Xiaoying, Hild, Marc, Servais, Rebecca, Jain, Monish, Deng, Lin, Bullock, Caroline, McLellan, Michael, Schuierer, Sven, Murphy, Leo, Blommers, Marcel J J, Blaustein, Cecile, Berenshteyn, Frada, Lacoste, Arnaud, Thomas, Jason R, Roma, Guglielmo, Michaud, Gregory A, Tseng, Brian S, Porter, Jeffery A, Myer, Vic E, Tallarico, John A, Hamann, Lawrence G, Curtis, Daniel, Fishman, Mark C, Dietrich, William F, Dales, Natalie A, Sivasankaran, Rajeev

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Plasma Neurofilament Light for Prediction of Disease Progression in Familial Frontotemporal Lobar Degeneration von Rojas, Julio C., Wang, Ping, Staffaroni, Adam M., Heller, Carolin, Cobigo, Yann, Wolf, Amy, Goh, Sheng-Yang M., Ljubenkov, Peter A., Heuer, Hilary W., Fong, Jamie C., Taylor, Joanne B., Veras, Eliseo, Song, Linan, Jeromin, Andreas, Hanlon, David, Yu, Lili, Khinikar, Arvind, Sivasankaran, Rajeev, Kieloch, Agnieszka, Valentin, Marie-Anne, Karydas, Anna M., Mitic, Laura L., Pearlman, Rodney, Kornak, John, Kramer, Joel H., Miller, Bruce L., Kantarci, Kejal, Knopman, David S., Graff-Radford, Neill, Petrucelli, Leonard, Rademakers, Rosa, Irwin, David J., Grossman, Murray, Ramos, Eliana Marisa, Coppola, Giovanni, Mendez, Mario F., Bordelon, Yvette, Dickerson, Bradford C., Ghoshal, Nupur, Huey, Edward D., Mackenzie, Ian R., Appleby, Brian S., Domoto-Reilly, Kimiko, Hsiung, Ging-Yuek R., Toga, Arthur W., Weintraub, Sandra, Kaufer, Daniel I., Kerwin, Diana, Litvan, Irene, Onyike, Chiadikaobi U., Pantelyat, Alexander, Roberson, Erik D., Tartaglia, Maria C., Foroud, Tatiana, Chen, Weiping, Czerkowicz, Julie, Graham, Danielle L., van Swieten, John C., Borroni, Barbara, Sanchez-Valle, Raquel, Moreno, Fermin, Laforce, Robert, Graff, Caroline, Synofzik, Matthis, Galimberti, Daniela, Rowe, James B., Masellis, Mario, Finger, Elizabeth, Vandenberghe, Rik, de Mendonça, Alexandre, Tagliavini, Fabrizio, Santana, Isabel, Ducharme, Simon, Butler, Chris R., Gerhard, Alexander, Levin, Johannes, Danek, Adrian, Otto, Markus, Sorbi, Sandro, Cash, David M., Convery, Rhian S., Bocchetta, Martina, Foiani, Martha, Greaves, Caroline V., Peakman, Georgia, Russell, Lucy, Swift, Imogen, Todd, Emily, Rohrer, Jonathan D., Boeve, Bradley F., Rosen, Howard J., Boxer, Adam L.

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Use of Intramolecular 1,5-Sulfur–Oxygen and 1,5-Sulfur–Halogen Interactions in the Design of N‑Methyl-5-aryl‑N‑(2,2,6,6-tetramethylpiperidin-4-yl)-1,3,4-thiadiazol-2-amine SMN2 Spl... von Axford, Jake, Sung, Moo Je, Manchester, John, Chin, Donovan, Jain, Monish, Shin, Youngah, Dix, Ina, Hamann, Lawrence G, Cheung, Atwood K, Sivasankaran, Rajeev, Briner, Karin, Dales, Natalie A, Hurley, Brian

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Author Correction: Regulated control of gene therapies by drug-induced splicing von Monteys, Alex Mas, Hundley, Amiel A., Ranum, Paul T., Tecedor, Luis, Muehlmatt, Amy, Lim, Euyn, Lukashev, Dmitriy, Sivasankaran, Rajeev, Davidson, Beverly L.

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CSF Proteomics in Patients With Progressive Supranuclear Palsy von Wise, Amy, Li, Jingyao, Yamakawa, Mai, Loureiro, Joseph, Peterson, Brant, Worringer, Kathleen, Sivasankaran, Rajeev, Palma, Jose-Alberto, Mitic, Laura, Heuer, Hilary W, Lario-Lago, Argentina, Staffaroni, Adam M, Clark, Annie, Taylor, Jack, Ljubenkov, Peter A, Vandevrede, Lawren, Grinberg, Lea T, Spina, Salvatore, Seeley, William W, Miller, Bruce L, Boeve, Bradley F, Dickerson, Bradford C, Grossman, Murray, Litvan, Irene, Pantelyat, Alexander, Tartaglia, Maria Carmela, Zhang, Zihan, Wills, Anne-Marie A, Rexach, Jessica, Rojas, Julio C, Boxer, Adam L

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Oligodendrocyte-myelin glycoprotein is a Nogo receptor ligand that inhibits neurite outgrowth von WANG, Kevin C, KOPRIVICA, Vuk, KIM, Jicun A, SIVASANKARAN, Rajeav, YONG GUO, NEVE, Rachel L, ZHIGANG ME

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p75 interacts with the Nogo receptor as a co-receptor for Nogo, MAG and OMgp von Wang, Kevin C., Kim, Jieun A., Sivasankaran, Rajeev, Segal, Rosalind, He, Zhigang

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Leveraging Large‐scale CSF Proteomics to identify Disease Progression Biomarkers in Autosomal Dominant Frontotemporal Lobar Degeneration von Saloner, Rowan, Staffaroni, Adam M., Dammer, Eric B., Johnson, Erik C.B., Paolillo, Emily W., Heuer, Hilary W., Wise, Amy B., Forsberg, Leah K., Kramer, Joel H., Miller, Bruce L, Li, Jingyao, Loureiro, Joseph, Sivasankaran, Rajeev, Worringer, Katie, Boeve, Brad F., Rosen, Howard J., Boxer, Adam L., Rojas, Julio C., Casaletto, Kaitlin B.

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Plasma tau and neurofilament light in frontotemporal lobar degeneration and Alzheimerʼs disease von Illán-Gala, Ignacio, Lleo, Alberto, Karydas, Anna, Staffaroni, Adam M, Zetterberg, Henrik, Sivasankaran, Rajeev, Grinberg, Lea T, Spina, Salvatore, Kramer, Joel, Ramos, Eliana M, Coppola, Giovanni, La Joie, Renaud, Rabinovici, Gil D, Perry, David C, Gorno-Tempini, Maria Luisa, Seeley, William, Miller, Bruce L, Rosen, Howard J, Blennow, Kaj, Boxer, Adam L, Rojas, Julio C

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