Engineering adeno-associated virus vectors for gene therapy von Li, Chengwen, Samulski, R. Jude

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Adeno-associated virus at 50: a golden anniversary of discovery, research, and gene therapy success--a personal perspective von Hastie, Eric, Samulski, R Jude

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The AAV Vector Toolkit: Poised at the Clinical Crossroads von Asokan, Aravind, Schaffer, David V, Jude Samulski, R

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Global CNS gene delivery and evasion of anti-AAV-neutralizing antibodies by intrathecal AAV administration in non-human primates von Gray, S J, Nagabhushan Kalburgi, S, McCown, T J, Jude Samulski, R

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AAV-Mediated Gene Therapy for Research and Therapeutic Purposes von Samulski, R Jude, Muzyczka, Nicholas

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Adeno-Associated Virus Vectorology, Manufacturing, and Clinical Applications von Grieger, Joshua C., Samulski, R. Jude

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Adeno-associated Virus Serotypes: Vector Toolkit for Human Gene Therapy von Wu, Zhijian, Asokan, Aravind, Samulski, R Jude

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Preclinical Differences of Intravascular AAV9 Delivery to Neurons and Glia: A Comparative Study of Adult Mice and Nonhuman Primates von Gray, Steven J, Matagne, Valerie, Bachaboina, Lavanya, Yadav, Swati, Ojeda, Sergio R, Samulski, R Jude

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Parkinson's Disease Gene Therapy: Success by Design Meets Failure by Efficacy von Bartus, Raymond T, Weinberg, Marc S, Samulski, R. Jude

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Viral vectors for gene delivery to the central nervous system von Lentz, Thomas B, Gray, Steven J, Samulski, R. Jude

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BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression von Konkle, Barbara A., Walsh, Christopher E., Escobar, Miguel A., Josephson, Neil C., Young, Guy, von Drygalski, Annette, McPhee, Scott W.J., Samulski, R. Jude, Bilic, Ivan, de la Rosa, Maurus, Reipert, Birgit M., Rottensteiner, Hanspeter, Scheiflinger, Friedrich, Chapin, John C., Ewenstein, Bruce, Monahan, Paul E.

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Recombinant adeno-associated virus utilizes host cell nuclear import machinery to enter the nucleus von Nicolson, Sarah C, Samulski, R Jude

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Bound Protein- and Peptide-Based Strategies for Adeno-Associated Virus Vector-Mediated Gene Therapy: Where Do We Stand Now? von Zhang, Xintao, Chai, Zheng, Samulski, R. Jude, Li, Chengwen

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Cytoplasmic Trafficking, Endosomal Escape, and Perinuclear Accumulation of Adeno-Associated Virus Type 2 Particles Are Facilitated by Microtubule Network von XIAOA, Ping-Jie, JUDE SAMULSKIA, R

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Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector von Bowles, Dawn E, McPhee, Scott WJ, Li, Chengwen, Gray, Steven J, Samulski, Jade J, Camp, Angelique S, Li, Juan, Wang, Bing, Monahan, Paul E, Rabinowitz, Joseph E, Grieger, Joshua C, Govindasamy, Lakshmanan, Agbandje-McKenna, Mavis, Xiao, Xiao, Samulski, R Jude

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Production and characterization of adeno-associated viral vectors von Samulski, R Jude, Grieger, Joshua C, Choi, Vivian W

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Sub-2 Å Ewald curvature corrected structure of an AAV2 capsid variant von Tan, Yong Zi, Aiyer, Sriram, Mietzsch, Mario, Hull, Joshua A., McKenna, Robert, Grieger, Joshua, Samulski, R. Jude, Baker, Timothy S., Agbandje-McKenna, Mavis, Lyumkis, Dmitry

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Structure and Dynamics of Adeno-Associated Virus Serotype 1 VP1-Unique N-Terminal Domain and Its Role in Capsid Trafficking von Venkatakrishnan, Balasubramanian, Yarbrough, Joseph, Domsic, John, Bennett, Antonette, Bothner, Brian, Kozyreva, Olga G., Samulski, R. Jude, Muzyczka, Nicholas, McKenna, Robert, Agbandje-McKenna, Mavis

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Enhancement of Adeno-Associated Virus Infection by Mobilizing Capsids into and Out of the Nucleolus von JOHNSON, Jarrod S, SAMULSKI, R. Jude

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Optimizing Promoters for Recombinant Adeno-Associated Virus-Mediated Gene Expression in the Peripheral and Central Nervous System Using Self-Complementary Vectors von GRAY, Steven J, FOTI, Stacey B, SCHWARTZ, Joel W, BACHABOINA, Lavanya, TAYLOR-BLAKE, Bonnie, COLEMAN, Jennifer, EHLERS, Michael D, ZYLKA, Mark J, MCCOWN, Thomas J, SAMULSKI, R. Jude

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