Comprehensive Lipidomic Workflow for Multicohort Population Phenotyping Using Stable Isotope Dilution Targeted Liquid Chromatography-Mass Spectrometry von Ryan, Monique J., Grant-St James, Alanah, Lawler, Nathan G., Fear, Mark W., Raby, Edward, Wood, Fiona M., Maker, Garth L., Wist, Julien, Holmes, Elaine, Nicholson, Jeremy K., Whiley, Luke, Gray, Nicola

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Nonsevere Burn Induces a Prolonged Systemic Metabolic Phenotype Indicative of a Persistent Inflammatory Response Postinjury von Ryan, Monique J., Raby, Edward, Whiley, Luke, Masuda, Reika, Lodge, Samantha, Nitschke, Philipp, Maker, Garth L., Wist, Julien, Holmes, Elaine, Wood, Fiona M., Nicholson, Jeremy K., Fear, Mark W., Gray, Nicola

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Clinical prediction of wound re-epithelisation outcomes in non-severe burn injury using the plasma lipidome von Ryan, Monique J., Raby, Edward, Masuda, Reika, Lodge, Samantha, Nitschke, Philipp, Maker, Garth L., Wist, Julien, Fear, Mark W., Holmes, Elaine, Nicholson, Jeremy K., Gray, Nicola, Whiley, Luke, Wood, Fiona M.

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Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5‐year update of the NURTURE study von Crawford, Thomas O., Swoboda, Kathryn J., De Vivo, Darryl C., Bertini, Enrico, Hwu, Wuh‐Liang, Finkel, Richard S., Kirschner, Janbernd, Kuntz, Nancy L., Nazario, Aledie Navas, Parsons, Julie A., Pechmann, Astrid, Ryan, Monique M., Butterfield, Russell J., Topaloglu, Haluk, Ben‐Omran, Tawfeg, Sansone, Valeria A., Jong, Yuh‐Jyh, Shu, Francy, Zhu, Cong, Raynaud, Stephanie, Lago, Tiffany R., Paradis, Angela D., Foster, Richard, Chin, Russell, Berger, Zdenek

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Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study von De Vivo, Darryl C., Bertini, Enrico, Swoboda, Kathryn J., Hwu, Wuh-Liang, Crawford, Thomas O., Finkel, Richard S., Kirschner, Janbernd, Kuntz, Nancy L., Parsons, Julie A., Ryan, Monique M., Butterfield, Russell J., Topaloglu, Haluk, Ben-Omran, Tawfeg, Sansone, Valeria A., Jong, Yuh-Jyh, Shu, Francy, Staropoli, John F., Kerr, Douglas, Sandrock, Alfred W., Stebbins, Christopher, Petrillo, Marco, Braley, Gabriel, Johnson, Kristina, Foster, Richard, Gheuens, Sarah, Bhan, Ishir, Reyna, Sandra P., Fradette, Stephanie, Farwell, Wildon

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Snake Cathelicidin NA-CATH and Smaller Helical Antimicrobial Peptides Are Effective against Burkholderia thailandensis von Blower, Ryan J, Barksdale, Stephanie M, van Hoek, Monique L

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A phase 2 open-label study of the safety and efficacy of weekly dosing of ATL1102 in patients with non-ambulatory Duchenne muscular dystrophy and pharmacology in mdx mice von Woodcock, Ian R, Tachas, George, Desem, Nuket, Houweling, Peter J, Kean, Michael, Emmanuel, Jaiman, Kennedy, Rachel, Carroll, Kate, de Valle, Katy, Adams, Justine, Lamandé, Shireen R, Coles, Chantal, Tiong, Chrystal, Burton, Matthew, Villano, Daniella, Button, Peter, Hogrel, Jean-Yves, Catling-Seyffer, Sarah, Ryan, Monique M, Delatycki, Martin B, Yiu, Eppie M

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Eradication of large established tumors in mice by combination immunotherapy that engages innate and adaptive immune responses von Moynihan, Kelly D, Opel, Cary F, Szeto, Gregory L, Tzeng, Alice, Zhu, Eric F, Engreitz, Jesse M, Williams, Robert T, Rakhra, Kavya, Zhang, Michael H, Rothschilds, Adrienne M, Kumari, Sudha, Kelly, Ryan L, Kwan, Byron H, Abraham, Wuhbet, Hu, Kevin, Mehta, Naveen K, Kauke, Monique J, Suh, Heikyung, Cochran, Jennifer R, Lauffenburger, Douglas A, Wittrup, K Dane, Irvine, Darrell J

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A prospective evaluation of whole-exome sequencing as a first-tier molecular test in infants with suspected monogenic disorders von Stark, Zornitza, Tan, Tiong Y., Chong, Belinda, Brett, Gemma R., Yap, Patrick, Walsh, Maie, Yeung, Alison, Peters, Heidi, Mordaunt, Dylan, Cowie, Shannon, Amor, David J., Savarirayan, Ravi, McGillivray, George, Downie, Lilian, Ekert, Paul G., Theda, Christiane, James, Paul A., Yaplito-Lee, Joy, Ryan, Monique M., Leventer, Richard J., Creed, Emma, Macciocca, Ivan, Bell, Katrina M., Oshlack, Alicia, Sadedin, Simon, Georgeson, Peter, Anderson, Charlotte, Thorne, Natalie, Gaff, Clara, White, Susan M.

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Neurofilament as a potential biomarker for spinal muscular atrophy von Darras, Basil T., Crawford, Thomas O., Finkel, Richard S., Mercuri, Eugenio, De Vivo, Darryl C., Oskoui, Maryam, Tizzano, Eduardo F., Ryan, Monique M., Muntoni, Francesco, Zhao, Guolin, Staropoli, John, McCampbell, Alexander, Petrillo, Marco, Stebbins, Christopher, Fradette, Stephanie, Farwell, Wildon, Sumner, Charlotte J.

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Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial von Guglieri, Michela, Clemens, Paula R, Perlman, Seth J, Smith, Edward C, Horrocks, Iain, Finkel, Richard S, Mah, Jean K, Deconinck, Nicolas, Goemans, Nathalie, Haberlova, Jana, Straub, Volker, Mengle-Gaw, Laurel J, Schwartz, Benjamin D, Harper, Amy D, Shieh, Perry B, De Waele, Liesbeth, Castro, Diana, Yang, Michelle L, Ryan, Monique M, McDonald, Craig M, Tulinius, Mar, Webster, Richard, McMillan, Hugh J, Kuntz, Nancy L, Rao, Vashmi K, Baranello, Giovanni, Spinty, Stefan, Childs, Anne-Marie, Sbrocchi, Annie M, Selby, Kathryn A, Monduy, Migvis, Nevo, Yoram, Vilchez-Padilla, Juan J, Nascimento-Osorio, Andres, Niks, Erik H, de Groot, Imelda J.M, Katsalouli, Marina, James, Meredith K, van den Anker, Johannes, Damsker, Jesse M, Ahmet, Alexandra, Ward, Leanne M, Jaros, Mark, Shale, Phil, Dang, Utkarsh J, Hoffman, Eric P

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Three mutations switch H7N9 influenza to human-type receptor specificity von de Vries, Robert P, Peng, Wenjie, Grant, Oliver C, Thompson, Andrew J, Zhu, Xueyong, Bouwman, Kim M, de la Pena, Alba T Torrents, van Breemen, Marielle J, Ambepitiya Wickramasinghe, Iresha N, de Haan, Cornelis A M, Yu, Wenli, McBride, Ryan, Sanders, Rogier W, Woods, Robert J, Verheije, Monique H, Wilson, Ian A, Paulson, James C

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An engineered protein antagonist of K-Ras/B-Raf interaction von Kauke, Monique J., Traxlmayr, Michael W., Parker, Jillian A., Kiefer, Jonathan D., Knihtila, Ryan, McGee, John, Verdine, Greg, Mattos, Carla, Wittrup, K. Dane

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Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug von Conklin, Laurie S., Damsker, Jesse M., Hoffman, Eric P., Jusko, William J., Mavroudis, Panteleimon D., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., Smith, Edward C., Mah, Jean K., Guglieri, Michela, Nevo, Yoram, Kuntz, Nancy, McDonald, Craig M., Tulinius, Mar, Ryan, Monique M., Webster, Richard, Castro, Diana, Finkel, Richard S., Smith, Andrea L., Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Jaros, Mark, Shale, Phil, McCall, John M., Hathout, Yetrib, Nagaraju, Kanneboyina, van den Anker, John, Ward, Leanne M., Ahmet, Alexandra, Cornish, Michaelyn R., Clemens, Paula R.

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Pulmonary Biodistribution of Platelet-Derived Regenerative Exosomes in a Porcine Model von Rizzo, Skylar A, Bagwell, Monique S, Schiebel, Paige, Rolland, Tyler J, Mahlberg, Ryan C, Witt, Tyra A, Nagel, Mary E, Stalboerger, Paul G, Behfar, Atta

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Peripheral nerve ultrasound in pediatric Charcot-Marie-Tooth disease type 1A von Yiu, Eppie M, Brockley, Cain R, Lee, Katherine J, Carroll, Kate, de Valle, Katy, Kennedy, Rachel, Rao, Padma, Delatycki, Martin B, Ryan, Monique M

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The severe epilepsy syndromes of infancy: A population‐based study von Howell, Katherine B., Freeman, Jeremy L., Mackay, Mark T., Fahey, Michael C., Archer, John, Berkovic, Samuel F., Chan, Eunice, Dabscheck, Gabriel, Eggers, Stefanie, Hayman, Michael, Holberton, James, Hunt, Rodney W., Jacobs, Susan E., Kornberg, Andrew J., Leventer, Richard J., Mandelstam, Simone, McMahon, Jacinta M., Mefford, Heather C., Panetta, Julie, Riseley, Jessica, Rodriguez‐Casero, Victoria, Ryan, Monique M., Schneider, Amy L., Smith, Lindsay J., Stark, Zornitza, Wong, Flora, Yiu, Eppie M., Scheffer, Ingrid E., Harvey, A. Simon

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Two-year follow-up of KTE-X19 in patients with relapsed or refractory adult B-cell acute lymphoblastic leukemia in ZUMA-3 and its contextualization with SCHOLAR-3, an external hist... von Shah, Bijal D, Ghobadi, Armin, Oluwole, Olalekan O, Logan, Aaron C, Boissel, Nicolas, Cassaday, Ryan D, Leguay, Thibaut, Bishop, Michael R, Topp, Max S, Tzachanis, Dimitrios, O'Dwyer, Kristen M, Arellano, Martha L, Lin, Yi, Baer, Maria R, Schiller, Gary J, Park, Jae H, Subklewe, Marion, Abedi, Mehrdad, Minnema, Monique C, Wierda, William G, DeAngelo, Daniel J, Stiff, Patrick, Jeyakumar, Deepa, Dong, Jinghui, Adhikary, Sabina, Zhou, Lang, Schuberth, Petra C, Faghmous, Imi, Masouleh, Behzad Kharabi, Houot, Roch

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Hepatitis A Person-to-Person Outbreaks: Epidemiology, Morbidity Burden, and Factors Associated With Hospitalization—Multiple States, 2016–2019 von Hofmeister, Megan G, Xing, Jian, Foster, Monique A, Augustine, Ryan J, Burkholder, Cole, Collins, Jim, McBee, Shannon, Thomasson, Erica D, Thoroughman, Douglas, Weng, Mark K, Spradling, Philip R

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Hemagglutinin Traits Determine Transmission of Avian A/H10N7 Influenza Virus between Mammals von Herfst, Sander, Zhang, Jie, Richard, Mathilde, McBride, Ryan, Lexmond, Pascal, Bestebroer, Theo M., Spronken, Monique I.J., de Meulder, Dennis, van den Brand, Judith M., Rosu, Miruna E., Martin, Stephen R., Gamblin, Steve J., Xiong, Xiaoli, Peng, Wenjie, Bodewes, Rogier, van der Vries, Erhard, Osterhaus, Albert D.M.E., Paulson, James C., Skehel, John J., Fouchier, Ron A.M.

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