Non-immunogenic utrophin gene therapy for the treatment of muscular dystrophy animal models von Song, Yafeng, Morales, Leon, Malik, Alock S., Mead, Andrew F., Greer, Christopher D., Mitchell, Marilyn A., Petrov, Mihail T., Su, Leonard T., Choi, Margaret E., Rosenblum, Shira T., Lu, Xiangping, VanBelzen, Daniel J., Krishnankutty, Ranjith K., Balzer, Frederick J., Loro, Emanuele, French, Robert, Propert, Kathleen J., Zhou, Shangzhen, Kozyak, Benjamin W., Nghiem, Peter P., Khurana, Tejvir S., Kornegay, Joe N., Stedman, Hansell H.

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Suite of clinically relevant functional assays to address therapeutic efficacy and disease mechanism in the dystrophic mdx mouse von Song, Yafeng, Rosenblum, Shira T, Morales, Leon, Petrov, Mihail, Greer, Christopher, Globerman, Samantha, Stedman, Hansell H

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552. AAV9-Utrophin Restores Muscle Function in Dystrophic Mice von Rosenblum, Shira T., Stedman, Hansell H.

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Specific quinone reductase 2 inhibitors reduce metabolic burden and reverse Alzheimer's disease phenotype in mice von Gould, Nathaniel L, Scherer, Gila R, Carvalho, Silvia, Shurrush, Khriesto, Kayyal, Haneen, Edry, Efrat, Elkobi, Alina, David, Orit, Foqara, Maria, Thakar, Darshit, Pavesi, Tommaso, Sharma, Vijendra, Walker, Matthew, Maitland, Matthew, Dym, Orly, Albeck, Shira, Peleg, Yoav, Germain, Nicolas, Babaev, Ilana, Sharir, Haleli, Lalzar, Maya, Shklyar, Boris, Hazut, Neta, Khamaisy, Mohammad, Lévesque, Maxime, Lajoie, Gilles, Avoli, Massimo, Amitai, Gabriel, Lefker, Bruce, Subramanyam, Chakrapani, Shilton, Brian, Barr, Haim, Rosenblum, Kobi

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633. A Reproducible and Reliable Non-Invasive Approach to Assess the Efficacy of Gene Therapy in mdx Mice with Relevance to Clinical Trials von Song, Yafeng, Petrov, Mihail, Rosenblum, Shira, Morales, Leon, Stedman, Hansell H.

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388. Hypersensitivity of MYH16 Fibers (M Fibers) to Myodegeneration in Canine Muscular Dystrophy von Song, Yafeng, Mead, Andy, Petrov, Mihail, Ingraham, Phoebe, Morales, Leon, Rosenblum, Shira, Kornegay, Joe, Stedman, Hansell H.

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726. Prevention of Muscular Dystrophy by an AAV Vector Encoding a Nonimmunogenic Protein Based on the Evolution of Utrophin and Dystrophin von Song, Yafeng, Malik, Alock, Mead, Andy F., Mitchell, Marilyn, Petrov, Mihail, Su, Leonard, Morales, Leon, Rosenblum, Shira, Khurana, Tejvir, Kornegay, Joe N., Stedman, Hansell H.

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