From IPEX syndrome to FOXP3 mutation: a lesson on immune dysregulation von Bacchetta, Rosa, Barzaghi, Federica, Roncarolo, Maria‐Grazia

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Regulatory T-cell immunotherapy for tolerance to self antigens and alloantigens in humans von Roncarolo, Maria-Grazia, Battaglia, Manuela

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Gene correction for SCID-X1 in long-term hematopoietic stem cells von Pavel-Dinu, Mara, Wiebking, Volker, Dejene, Beruh T., Srifa, Waracharee, Mantri, Sruthi, Nicolas, Carmencita E., Lee, Ciaran, Bao, Gang, Kildebeck, Eric J., Punjya, Niraj, Sindhu, Camille, Inlay, Matthew A., Saxena, Nivedita, DeRavin, Suk See, Malech, Harry, Roncarolo, Maria Grazia, Weinberg, Kenneth I., Porteus, Matthew H.

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In Vivo Tracking of Human Hematopoiesis Reveals Patterns of Clonal Dynamics during Early and Steady-State Reconstitution Phases von Biasco, Luca, Pellin, Danilo, Scala, Serena, Dionisio, Francesca, Basso-Ricci, Luca, Leonardelli, Lorena, Scaramuzza, Samantha, Baricordi, Cristina, Ferrua, Francesca, Cicalese, Maria Pia, Giannelli, Stefania, Neduva, Victor, Dow, David J., Schmidt, Manfred, Von Kalle, Christof, Roncarolo, Maria Grazia, Ciceri, Fabio, Vicard, Paola, Wit, Ernst, Di Serio, Clelia, Naldini, Luigi, Aiuti, Alessandro

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Recent advances in understanding the pathophysiology of Wiskott-Aldrich syndrome von Bosticardo, Marita, Marangoni, Francesco, Aiuti, Alessandro, Villa, Anna, Grazia Roncarolo, Maria

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Identity and Diversity of Human Peripheral Th and T Regulatory Cells Defined by Single-Cell Mass Cytometry von Kunicki, Matthew A, Amaya Hernandez, Laura C, Davis, Kara L, Bacchetta, Rosa, Roncarolo, Maria-Grazia

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Clinical tolerance in allogeneic hematopoietic stem cell transplantation von Roncarolo, Maria-Grazia, Gregori, Silvia, Lucarelli, Barbarella, Ciceri, Fabio, Bacchetta, Rosa

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Role of regulatory T cells and FOXP3 in human diseases von Bacchetta, Rosa, MD, Gambineri, Eleonora, MD, Roncarolo, Maria-Grazia, MD

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Loss of Mismatched HLA in Leukemia after Stem-Cell Transplantation von Vago, Luca, Perna, Serena Kimi, Zanussi, Monica, Mazzi, Benedetta, Barlassina, Cristina, Stanghellini, Maria Teresa Lupo, Perrelli, Nicola Flavio, Cosentino, Cristian, Torri, Federica, Angius, Andrea, Forno, Barbara, Casucci, Monica, Bernardi, Massimo, Peccatori, Jacopo, Corti, Consuelo, Bondanza, Attilio, Ferrari, Maurizio, Rossini, Silvano, Roncarolo, Maria Grazia, Bordignon, Claudio, Bonini, Chiara, Ciceri, Fabio, Fleischhauer, Katharina

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Human‐engineered Treg‐like cells suppress FOXP3‐deficient T cells but preserve adaptive immune responses in vivo von Sato, Yohei, Passerini, Laura, Piening, Brian D, Uyeda, Molly Javier, Goodwin, Marianne, Gregori, Silvia, Snyder, Michael P, Bertaina, Alice, Roncarolo, Maria‐Grazia, Bacchetta, Rosa

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HLA-G expression levels influence the tolerogenic activity of human DC-10 von Amodio, Giada, Comi, Michela, Tomasoni, Daniela, Gianolini, Monica Emma, Rizzo, Roberta, LeMaoult, Joël, Roncarolo, Maria-Grazia, Gregori, Silvia

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Gene therapy for ADA‐SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products von Aiuti, Alessandro, Roncarolo, Maria Grazia, Naldini, Luigi

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Concise Review: Cell‐Based Therapies and Other Non‐Traditional Approaches for Type 1 Diabetes von Creusot, Remi J., Battaglia, Manuela, Roncarolo, Maria‐Grazia, Fathman, C. Garrison

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A novel FOXP3 knockout-humanized mouse model for pre-clinical safety and efficacy evaluation of Treg-like cell products von Sato, Yohei, Nathan, Abinaya, Shipp, Suzette, Wright, John Fraser, Tate, Keri Marie, Wani, Prachi, Roncarolo, Maria-Grazia, Bacchetta, Rosa

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Stability of human rapamycin-expanded CD4+CD25+ T regulatory cells von TRESOLDI, Eleonora, DELL'ALBANI, Ilaria, STABILINI, Angela, JOFRA, Tatiana, VALLE, Andrea, GAGLIANI, Nicola, BONDANZA, Attilio, GRAZIA RONCAROLO, Maria, BATTAGLIA, Manuela

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Engineered T Regulatory Type 1 Cells for Clinical Application von Gregori, Silvia, Roncarolo, Maria Grazia

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B-cell reconstitution after lentiviral vector–mediated gene therapy in patients with Wiskott-Aldrich syndrome von Castiello, Maria Carmina, PhD, Scaramuzza, Samantha, PhD, Pala, Francesca, MS, Ferrua, Francesca, MD, Uva, Paolo, PhD, Brigida, Immacolata, PhD, Sereni, Lucia, MS, van der Burg, Mirjam, PhD, Ottaviano, Giorgio, MD, Albert, Michael H., MD, Grazia Roncarolo, Maria, MD, Naldini, Luigi, MD, PhD, Aiuti, Alessandro, MD, PhD, Villa, Anna, MD, Bosticardo, Marita, PhD

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Rapamycin and Interleukin-10 Treatment Induces T Regulatory Type 1 Cells That Mediate Antigen-Specific Transplantation Tolerance von BATTAGLIA, Manuela, STABILINI, Angela, DRAGHICI, Elena, GREGORI, Silvia, MOCCHETTI, Cristina, BONIFACIO, Ezio, RONCAROLO, Maria-Grazia

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Antigen-Specific Dependence of Tr1-Cell Therapy in Preclinical Models of Islet Transplant von GAGLIANI, Nicola, JOFRA, Tatiana, STABILINI, Angela, VALLE, Andrea, ATKINSON, Mark, RONCAROLO, Maria-Grazia, BATTAGLIA, Manuela

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Clinical and molecular profile of a new series of patients with immune dysregulation, polyendocrinopathy, enteropathy, X-linked syndrome: Inconsistent correlation between forkhead... von Gambineri, Eleonora, MD, Perroni, Lucia, PhD, Passerini, Laura, PhD, Bianchi, Lucia, PhD, Doglioni, Claudio, MD, Meschi, Franco, MD, Bonfanti, Riccardo, MD, Sznajer, Yves, MD, Tommasini, Alberto, MD, Lawitschka, Anita, MD, Junker, Anne, MD, Dunstheimer, Desiree, MD, Heidemann, Peter H., MD, Cazzola, Giantonio, MD, Cipolli, Marco, MD, Friedrich, Wilhelm, MD, Janic, Dragana, MD, Azzi, Nadira, MD, Richmond, Erick, MD, Vignola, Silvia, MD, Barabino, Arrigo, MD, Chiumello, Giuseppe, MD, Azzari, Chiara, MD, PhD, Roncarolo, Maria-Grazia, MD, PhD, Bacchetta, Rosa, MD

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