Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients von Charrier, S, Dupré, L, Scaramuzza, S, Jeanson-Leh, L, Blundell, M P, Danos, O, Cattaneo, F, Aiuti, A, Eckenberg, R, Thrasher, A J, Roncarolo, M Grazia, Galy, A

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Role of regulatory T cells and FOXP3 in human diseases von Bacchetta, Rosa, MD, Gambineri, Eleonora, MD, Roncarolo, Maria-Grazia, MD

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B-cell reconstitution after lentiviral vector–mediated gene therapy in patients with Wiskott-Aldrich syndrome von Castiello, Maria Carmina, PhD, Scaramuzza, Samantha, PhD, Pala, Francesca, MS, Ferrua, Francesca, MD, Uva, Paolo, PhD, Brigida, Immacolata, PhD, Sereni, Lucia, MS, van der Burg, Mirjam, PhD, Ottaviano, Giorgio, MD, Albert, Michael H., MD, Grazia Roncarolo, Maria, MD, Naldini, Luigi, MD, PhD, Aiuti, Alessandro, MD, PhD, Villa, Anna, MD, Bosticardo, Marita, PhD

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Clinical and molecular profile of a new series of patients with immune dysregulation, polyendocrinopathy, enteropathy, X-linked syndrome: Inconsistent correlation between forkhead... von Gambineri, Eleonora, MD, Perroni, Lucia, PhD, Passerini, Laura, PhD, Bianchi, Lucia, PhD, Doglioni, Claudio, MD, Meschi, Franco, MD, Bonfanti, Riccardo, MD, Sznajer, Yves, MD, Tommasini, Alberto, MD, Lawitschka, Anita, MD, Junker, Anne, MD, Dunstheimer, Desiree, MD, Heidemann, Peter H., MD, Cazzola, Giantonio, MD, Cipolli, Marco, MD, Friedrich, Wilhelm, MD, Janic, Dragana, MD, Azzi, Nadira, MD, Richmond, Erick, MD, Vignola, Silvia, MD, Barabino, Arrigo, MD, Chiumello, Giuseppe, MD, Azzari, Chiara, MD, PhD, Roncarolo, Maria-Grazia, MD, PhD, Bacchetta, Rosa, MD

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Induction of anergic allergen-specific suppressor T cells using tolerogenic dendritic cells derived from children with allergies to house dust mites von Pacciani, Valentina, PhD, Gregori, Silvia, PhD, Chini, Loredana, MD, Corrente, Stefania, MD, Chianca, Marco, MD, Moschese, Viviana, MD, Rossi, Paolo, MD, PhD, Roncarolo, Maria Grazia, MD, Angelini, Federica, MD, PhD

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B-cell development and functions and therapeutic options in adenosine deaminase–deficient patients von Brigida, Immacolata, PhD, Sauer, Aisha V., PhD, Ferrua, Francesca, MD, Giannelli, Stefania, PhD, Scaramuzza, Samantha, PhD, Pistoia, Valentina, MSc, Castiello, Maria Carmina, PhD, Barendregt, Barbara H., BSc, Cicalese, Maria Pia, MD, Casiraghi, Miriam, RCN, Brombin, Chiara, PhD, Puck, Jennifer, MD, Müller, Klaus, MD, PhD, Notarangelo, Lucia Dora, MD, Montin, Davide, MD, van Montfrans, Joris M., MD, PhD, Roncarolo, Maria Grazia, MD, Traggiai, Elisabetta, PhD, van Dongen, Jacques J.M., MD, PhD, van der Burg, Mirjam, PhD, Aiuti, Alessandro, MD, PhD

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Lentiviral-mediated gene therapy leads to improvement of B-cell functionality in a murine model of Wiskott-Aldrich syndrome von Bosticardo, Marita, PhD, Draghici, Elena, MS, Schena, Francesca, PhD, Sauer, Aisha Vanessa, PhD, Fontana, Elena, PhD, Castiello, Maria Carmina, MS, Catucci, Marco, PhD, Locci, Michela, PhD, Naldini, Luigi, MD, PhD, Aiuti, Alessandro, MD, PhD, Roncarolo, Maria Grazia, MD, Poliani, Pietro Luigi, MD, PhD, Traggiai, Elisabetta, PhD, Villa, Anna, MD

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Point mutants of forkhead box P3 that cause immune dysregulation, polyendocrinopathy, enteropathy, X-linked have diverse abilities to reprogram T cells into regulatory T cells von McMurchy, Alicia N., BSc, Gillies, Jana, MSc, Allan, Sarah E., PhD, Passerini, Laura, PhD, Gambineri, Eleonora, MD, Roncarolo, Maria Grazia, MD, Bacchetta, Rosa, MD, Levings, Megan K., PhD

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Revertant T lymphocytes in a patient with Wiskott-Aldrich syndrome: Analysis of function and distribution in lymphoid organs von Trifari, Sara, PhD, Scaramuzza, Samantha, PhD, Catucci, Marco, MS, Ponzoni, Maurilio, MD, Mollica, Luca, PhD, Chiesa, Robert, MD, Cattaneo, Federica, MD, Lafouresse, Fanny, MS, Calvez, Ronan, PhD, Vermi, William, MD, Medicina, Daniela, MS, Castiello, Maria Carmina, MS, Marangoni, Francesco, PhD, Bosticardo, Marita, PhD, Doglioni, Claudio, MD, Caniglia, Maurizio, MD, Aiuti, Alessandro, MD, Villa, Anna, MD, Roncarolo, Maria-Grazia, MD, Dupré, Loïc, PhD

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FLK-2/FLT-3 Ligand Regulates the Growth of Early Myeloid Progenitors Isolated From Human Fetal Liver von Muench, Marcus O., Roncarolo, Maria Grazia, Menon, Satish, Xu, Yuming, Kastelein, Robert, Zurawski, Sandra, Hannum, Charles H., Culpepper, Janice, Lee, Frank, Namikawa, Reiko

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In vivo T-cell dynamics during immune reconstitution after hematopoietic stem cell gene therapy in adenosine deaminase severe combined immune deficiency von Selleri, Silvia, PhD, Brigida, Immacolata, MSc, Casiraghi, Miriam, RCN, Scaramuzza, Samantha, PhD, Cappelli, Barbara, MD, Cassani, Barbara, PhD, Ferrua, Francesca, MD, Aker, Memet, MD, Slavin, Shimon, MD, Scarselli, Alessia, MD, Cancrini, Caterina, MD, Marktel, Sarah, MD, Grazia Roncarolo, Maria, MD, Aiuti, Alessandro, MD, PhD

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Host-reactive CD4+ and CD8+ T cell clones isolated from a human chimera produce IL-5, IL-2, IFN-gamma and granulocyte/macrophage-colony- stimulating factor but not IL-4 von Bacchetta, R, de Waal Malefijt, R, Yssel, H, Abrams, J, de Vries, JE, Spits, H, Roncarolo, MG

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Clonal analysis of the peripheral T cell compartment of the SCID-hu mouse von Vandekerckhove, BA, Krowka, JF, McCune, JM, de Vries, JE, Spits, H, Roncarolo, MG

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IgE content of commercial intravenous IgG preparations von Tovo, P A, Gabiano, C, Grazia Roncarolo, M, Altare, F

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Therapeutic binding molecules von KOLBINGER FRANK,HERRERA JOSE M. CARBALLIDO,ASZODIANDRAS,SALDANHA JOSE W.,HALL BRUCE M.,GREGORI SILVIA,RONCAROLO MARIA GRAZIA,LOUX VERONIQUE,AVERSA GREGORIO,JESCHKE MARGIT

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Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial von Sessa, Maria, MD, Lorioli, Laura, MD, Fumagalli, Francesca, MD, Acquati, Serena, PhD, Redaelli, Daniela, MSc, Baldoli, Cristina, MD, Canale, Sabrina, MSc, Lopez, Ignazio D, MD, Morena, Francesco, PhD, Calabria, Andrea, PhD, Fiori, Rossana, MD, Silvani, Paolo, MD, Rancoita, Paola M V, PhD, Gabaldo, Michela, MSc, Benedicenti, Fabrizio, MSc, Antonioli, Gigliola, RN, Assanelli, Andrea, MD, Cicalese, Maria Pia, MD, del Carro, Ubaldo, MD, Sora, Maria Grazia Natali, MD, Martino, Sabata, PhD, Quattrini, Angelo, MD, Montini, Eugenio, PhD, Di Serio, Clelia, Prof, Ciceri, Fabio, MD, Roncarolo, Maria Grazia, Prof, Aiuti, Alessandro, MD, Naldini, Luigi, Prof, Biffi, Alessandra, Dr

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The Biology of T Regulatory Type 1 Cells and Their Therapeutic Application in Immune-Mediated Diseases von Roncarolo, Maria Grazia, Gregori, Silvia, Bacchetta, Rosa, Battaglia, Manuela, Gagliani, Nicola

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HLA-G expression levels influence the tolerogenic activity of human DC-10 von Amodio, Giada, Comi, Michela, Tomasoni, Daniela, Gianolini, Monica Emma, Rizzo, Roberta, LeMaoult, Joël, Roncarolo, Maria-Grazia, Gregori, Silvia

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Rapamycin selectively expands CD4+CD25+FoxP3+ regulatory T cells von Battaglia, Manuela, Stabilini, Angela, Roncarolo, Maria-Grazia

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Tr1 cells: From discovery to their clinical application von Battaglia, Manuela, Gregori, Silvia, Bacchetta, Rosa, Roncarolo, Maria-Grazia

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