Generation of Isogenic Pluripotent Stem Cells Differing Exclusively at Two Early Onset Parkinson Point Mutations von Soldner, Frank, Laganière, Josée, Cheng, Albert W., Hockemeyer, Dirk, Gao, Qing, Alagappan, Raaji, Khurana, Vikram, Golbe, Lawrence I., Myers, Richard H., Lindquist, Susan, Zhang, Lei, Guschin, Dmitry, Fong, Lauren K., Vu, B. Joseph, Meng, Xiangdong, Urnov, Fyodor D., Rebar, Edward J., Gregory, Philip D., Zhang, H. Steve, Jaenisch, Rudolf

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Targeted Genome Editing Across Species Using ZFNs and TALENs von Wood, Andrew J., Lo, Te-Wen, Zeitler, Bryan, Pickle, Catherine S., Ralston, Edward J., Lee, Andrew H., Amora, Rainier, Miller, Jeffrey C., Leung, Elo, Meng, Xiangdong, Zhang, Lei, Rebar, Edward J., Gregory, Philip D., Urnov, Fyodor D., Meyer, Barbara J.

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Mitochondrially targeted ZFNs for selective degradation of pathogenic mitochondrial genomes bearing large‐scale deletions or point mutations von Gammage, Payam A, Rorbach, Joanna, Vincent, Anna I, Rebar, Edward J, Minczuk, Michal

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In vivo genome editing of the albumin locus as a platform for protein replacement therapy von Sharma, Rajiv, Anguela, Xavier M., Doyon, Yannick, Wechsler, Thomas, DeKelver, Russell C., Sproul, Scott, Paschon, David E., Miller, Jeffrey C., Davidson, Robert J., Shivak, David, Zhou, Shangzhen, Rieders, Julianne, Gregory, Philip D., Holmes, Michael C., Rebar, Edward J., High, Katherine A.

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Efficient targeting of expressed and silent genes in human ESCs and iPSCs using zinc-finger nucleases von Amora, Ranier, Miller, Jeffrey C, Mitalipova, Maisam, Katibah, George E, Rebar, Edward J, Urnov, Fyodor D, Jaenisch, Rudolf, Gregory, Philip D, Boydston, Elizabeth A, Beard, Caroline, Hockemeyer, Dirk, Zeitler, Bryan, Meng, Xiangdong, Soldner, Frank, Gao, Qing, Zhang, Lei, DeKelver, Russell C

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Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells von Hoban, Megan D., Cost, Gregory J., Mendel, Matthew C., Romero, Zulema, Kaufman, Michael L., Joglekar, Alok V., Ho, Michelle, Lumaquin, Dianne, Gray, David, Lill, Georgia R., Cooper, Aaron R., Urbinati, Fabrizia, Senadheera, Shantha, Zhu, Allen, Liu, Pei-Qi, Paschon, David E., Zhang, Lei, Rebar, Edward J., Wilber, Andrew, Wang, Xiaoyan, Gregory, Philip D., Holmes, Michael C., Reik, Andreas, Hollis, Roger P., Kohn, Donald B.

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Diversifying the structure of zinc finger nucleases for high-precision genome editing von Paschon, David E., Lussier, Stephanie, Wangzor, Tenzin, Xia, Danny F., Li, Patrick W., Hinkley, Sarah J., Scarlott, Nicholas A., Lam, Stephen C., Waite, Adam J., Truong, Lynn N., Gandhi, Nimisha, Kadam, Bhakti N., Patil, Deepak P., Shivak, David A., Lee, Gary K., Holmes, Michael C., Zhang, Lei, Miller, Jeffrey C., Rebar, Edward J.

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A Rapid and General Assay for Monitoring Endogenous Gene Modification von Guschin, Dmitry Y., Waite, Adam J., Katibah, George E., Miller, Jeffrey C., Holmes, Michael C., Rebar, Edward J.

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Toward eliminating HLA class I expression to generate universal cells from allogeneic donors von Torikai, Hiroki, Reik, Andreas, Soldner, Frank, Warren, Edus H., Yuen, Carrie, Zhou, Yuanyue, Crossland, Denise L., Huls, Helen, Littman, Nicholas, Zhang, Ziying, Tykodi, Scott S., Kebriaei, Partow, Lee, Dean A., Miller, Jeffrey C., Rebar, Edward J., Holmes, Michael C., Jaenisch, Rudolf, Champlin, Richard E., Gregory, Philip D., Cooper, Laurence J.N.

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Knockout Rats via Embryo Microinjection of Zinc-Finger Nucleases von Geurts, Aron M, Cost, Gregory J, Freyvert, Yevgeniy, Zeitler, Bryan, Miller, Jeffrey C, Choi, Vivian M, Jenkins, Shirin S, Wood, Adam, Cui, Xiaoxia, Meng, Xiangdong, Vincent, Anna, Lam, Stephen, Michalkiewicz, Mieczyslaw, Schilling, Rebecca, Foeckler, Jamie, Kalloway, Shawn, Weiler, Hartmut, Ménoret, Séverine, Anegon, Ignacio, Davis, Gregory D, Zhang, Lei, Rebar, Edward J, Gregory, Philip D, Urnov, Fyodor D, Jacob, Howard J, Buelow, Roland

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DNA ligase III promotes alternative nonhomologous end-joining during chromosomal translocation formation von Simsek, Deniz, Brunet, Erika, Wong, Sunnie Yan-Wai, Katyal, Sachin, Gao, Yankun, McKinnon, Peter J, Lou, Jacqueline, Zhang, Lei, Li, James, Rebar, Edward J, Gregory, Philip D, Holmes, Michael C, Jasin, Maria

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An improved zinc-finger nuclease architecture for highly specific genome editing von Wang, Jianbin, Rebar, Edward J, Guschin, Dmitry Y, Lee, Ya-Li, Holmes, Michael C, Miller, Jeffrey C, Gregory, Philip D, Kim, Kenneth A, Waite, Adam J, Beausejour, Christian M, Wang, Nathaniel S, Pabo, Carl O, Rupniewski, Igor

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Rapid and efficient clathrin-mediated endocytosis revealed in genome-edited mammalian cells von Drubin, David G, Lee, Andrew H, Cheng, Aaron T, Doyon, Yannick, Vo, Thuy D, Miller, Jeffrey C, Cherone, Jennifer M, Cheng, Jackie, Santiago, Yolanda, Urnov, Fyodor D, Paschon, David E, Doyon, Jeffrey B, Zhang, Lei, Rebar, Edward J, Gregory, Philip D, Zeitler, Bryan

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Site-specific genome editing in Plasmodium falciparum using engineered zinc-finger nucleases von Straimer, Judith, Lee, Marcus C S, Lee, Andrew H, Zeitler, Bryan, Williams, April E, Pearl, Jocelynn R, Zhang, Lei, Rebar, Edward J, Gregory, Philip D, Llinás, Manuel, Urnov, Fyodor D, Fidock, David A

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Long-term multilineage engraftment of autologous genome-edited hematopoietic stem cells in nonhuman primates von Peterson, Christopher W., Wang, Jianbin, Norman, Krystin K., Norgaard, Zachary K., Humbert, Olivier, Tse, Collette K., Yan, Jenny J., Trimble, Richard G., Shivak, David A., Rebar, Edward J., Gregory, Philip D., Holmes, Michael C., Kiem, Hans-Peter

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Targeted gene knockout in mammalian cells by using engineered zinc-finger nucleases von Santiago, Yolanda, Chan, Edmond, Liu, Pei-Qi, Orlando, Salvatore, Zhang, Lin, Urnov, Fyodor D, Holmes, Michael C, Guschin, Dmitry, Waite, Adam, Miller, Jeffrey C, Rebar, Edward J, Gregory, Philip D, Klug, Aaron, Collingwood, Trevor N

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Long-Term Engraftment and Fetal Globin Induction upon BCL11A Gene Editing in Bone-Marrow-Derived CD34 + Hematopoietic Stem and Progenitor Cells von Chang, Kai-Hsin, Smith, Sarah E, Sullivan, Timothy, Chen, Kai, Zhou, Qianhe, West, Jason A, Liu, Mei, Liu, Yingchun, Vieira, Benjamin F, Sun, Chao, Hong, Vu P, Zhang, Mingxuan, Yang, Xiao, Reik, Andreas, Urnov, Fyodor D, Rebar, Edward J, Holmes, Michael C, Danos, Olivier, Jiang, Haiyan, Tan, Siyuan

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Improved specificity of TALE-based genome editing using an expanded RVD repertoire von Miller, Jeffrey C, Zhang, Lei, Xia, Danny F, Campo, John J, Ankoudinova, Irina V, Guschin, Dmitry Y, Babiarz, Joshua E, Meng, Xiangdong, Hinkley, Sarah J, Lam, Stephen C, Paschon, David E, Vincent, Anna I, Dulay, Gladys P, Barlow, Kyle A, Shivak, David A, Leung, Elo, Kim, Jinwon D, Amora, Rainier, Urnov, Fyodor D, Gregory, Philip D, Rebar, Edward J

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Efficient targeted gene disruption in the soma and germ line of the frog Xenopus tropicalis using engineered zinc-finger nucleases von Young, John J, Cherone, Jennifer M, Doyon, Yannick, Ankoudinova, Irina, Faraji, Farhoud M, Lee, Andrew H, Ngo, Catherine, Guschin, Dmitry Y, Paschon, David E, Miller, Jeffrey C, Zhang, Lei, Rebar, Edward J, Gregory, Philip D, Urnov, Fyodor D, Harland, Richard M, Zeitler, Bryan

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Human Intestinal Tissue with Adult Stem Cell Properties Derived from Pluripotent Stem Cells von Forster, Ryan, Chiba, Kunitoshi, Schaeffer, Lorian, Regalado, Samuel G., Lai, Christine S., Gao, Qing, Kiani, Samira, Farin, Henner F., Clevers, Hans, Cost, Gregory J., Chan, Andy, Rebar, Edward J., Urnov, Fyodor D., Gregory, Philip D., Pachter, Lior, Jaenisch, Rudolf, Hockemeyer, Dirk

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