Cardiovascular manifestations of feline Sandhoff disease after intravenous AAV gene therapy von Ellis, Lauren E, Winter, Randolph, Gray-Edwards, Heather L, Maitland, Stacy, Randle, Ashley E, Edwards, Robert, Sena-Esteves, Miguel, Martin, Douglas R, Wang, Raymond Y

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Adeno-Associated Virus Gene Therapy in a Sheep Model of Tay-Sachs Disease von Gray-Edwards, Heather L, Randle, Ashley N, Maitland, Stacy A, Benatti, Hector R, Hubbard, Spencer M, Canning, Peter F, Vogel, Matthew B, Brunson, Brandon L, Hwang, Misako, Ellis, Lauren E, Bradbury, Allison M, Gentry, Atoska S, Taylor, Amanda R, Wooldridge, Anne A, Wilhite, Dewey R, Winter, Randolph L, Whitlock, Brian K, Johnson, Jacob A, Holland, Merilee, Salibi, Nouha, Beyers, Ronald J, Sartin, James L, Denney, Thomas S, Cox, Nancy R, Sena-Esteves, Miguel, Martin, Douglas R

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The Evolutionary History of Methicillin-Resistant Staphylococcus aureus (MRSA) von Enright, Mark C., Robinson, D. Ashley, Randle, Gaynor, Feil, Edward J., Grundmann, Hajo, Spratt, Brian G.

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Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy von Bradbury, Allison M, Cochran, J Nicholas, McCurdy, Victoria J, Johnson, Aime K, Brunson, Brandon L, Gray-Edwards, Heather, Leroy, Stanley G, Hwang, Misako, Randle, Ashley N, Jackson, Laura S, Morrison, Nancy E, Baek, Rena C, Seyfried, Thomas N, Cheng, Seng H, Cox, Nancy R, Baker, Henry J, Cachón-González, M Begona, Cox, Timothy M, Sena-Esteves, Miguel, Martin, Douglas R

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Life‐Limiting Peripheral Organ Dysfunction in Feline Sandhoff Disease Emerges after Effective CNS Gene Therapy von Johnson, Aime K., McCurdy, Victoria J., Gray‐Edwards, Heather L., Maguire, Anne S., Cochran, J. Nicholas, Gross, Amanda L., Skinner, Haleigh E., Randle, Ashley N., Shirley, Jamie L., Brunson, Brandon L., Bradbury, Allison M., Leroy, Stanley G., Hwang, Misako, Rockwell, Hannah E., Cox, Nancy R., Baker, Henry J., Seyfried, Thomas N., Sena‐Esteves, Miguel, Martin, Douglas R.

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Therapeutic benefit after intracranial gene therapy delivered during the symptomatic stage in a feline model of Sandhoff disease von McCurdy, Victoria J., Johnson, Aime K., Gray-Edwards, Heather L., Randle, Ashley N., Bradbury, Allison M., Morrison, Nancy E., Hwang, Misako, Baker, Henry J., Cox, Nancy R., Sena-Esteves, Miguel, Martin, Douglas R.

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Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model von Gray-Edwards, Heather L., Regier, Debra S., Shirley, Jamie L., Randle, Ashley N., Salibi, Nouha, Thomas, Sarah E., Latour, Yvonne L., Johnston, Jean, Golas, Gretchen, Maguire, Annie S., Taylor, Amanda R., Sorjonen, Donald C., McCurdy, Victoria J., Christopherson, Peter W., Bradbury, Allison M., Beyers, Ronald J., Johnson, Aime K., Brunson, Brandon L., Cox, Nancy R., Baker, Henry J., Denney, Thomas S., Sena-Esteves, Miguel, Tifft, Cynthia J., Martin, Douglas R.

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7T MRI Predicts Amelioration of Neurodegeneration in the Brain after AAV Gene Therapy von Gray-Edwards, Heather L., Maguire, Anne S., Salibi, Nouha, Ellis, Lauren E., Voss, Taylor L., Diffie, Elise B., Koehler, Jey, Randle, Ashley N., Taylor, Amanda R., Brunson, Brandon L., Denney, Thomas S., Beyers, Ronald J., Gentry, Atoska S., Gross, Amanda L., Batista, Ana R., Sena-Esteves, Miguel, Martin, Douglas R.

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AAV-Mediated Gene Delivery in a Feline Model of Sandhoff Disease Corrects Lysosomal Storage in the Central Nervous System von Rockwell, Hannah E., McCurdy, Victoria J., Eaton, Samuel C., Wilson, Diane U., Johnson, Aime K., Randle, Ashley N., Bradbury, Allison M., Gray-Edwards, Heather L., Baker, Henry J., Hudson, Judith A., Cox, Nancy R., Sena-Esteves, Miguel, Seyfried, Thomas N., Martin, Douglas R.

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AAV-mediated gene delivery attenuates neuroinflammation in feline Sandhoff disease von Bradbury, Allison M, Peterson, Tiffany A, Gross, Amanda L, Wells, Stephen Z, McCurdy, Victoria J, Wolfe, Karen G, Dennis, John C, Brunson, Brandon L, Gray-Edwards, Heather, Randle, Ashley N, Johnson, Aime K, Morrison, Edward E, Cox, Nancy R, Baker, Henry J, Sena-Esteves, Miguel, Martin, Douglas R

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Drug-Resistant Epilepsy in Tuberous Sclerosis Complex Is Associated With TSC2 Genotype: More Findings From the Preventing Epilepsy Using Vigatrin (PREVeNT) Trial von Farach, Laura S., Richard, Melissa A., Wulsin, Aynara C., Bebin, Elizabeth M., Krueger, Darcy A., Sahin, Mustafa, Porter, Brenda E., McPherson, Tarrant O., Peters, Jurriaan M., O'Kelley, Sarah, Taub, Katherine S., Rajaraman, Rajsekar, Randle, Stephanie C., McClintock, William M., Koenig, Mary Kay, Frost, Michael D., Werner, Klaus, Nolan, Danielle A., Wong, Michael, Cutter, Gary, Northrup, Hope, Au, Kit Sing, Bebin, E. Martina, Krueger, Darcy, Sahin, Mustafa, Flamini, Robert, Sergott, Robert C., Cutter, Gary, McPherson, Tarrant, Peri, Kalyani, Krefting, Jessica, Porter, Brenda, Peters, Jurriaan M., Taub, Katherine, Litt, Brian, Wu, Joyce, Lagory, Denise, Korf, Bruce, Messiaen, Ludwig, O'Kelley, Sarah, Biasini, Fred, Byars, Anna, Roberds, Steven L., Rushing, Gabrielle, Griffith, Molly, Davis, Peter, Hansen, Ellen, Arcasoy, Emine, Phillips, Jennifer, Solidum, Rayann, Rajaraman, Rajsekar, Gulsrud, Amanda, Solis, Natalie, Randle, Stephanie, Patrick, Kristina, Lee-Eng, Jacqueline, Frost, Mike D., Branson, Janet, Ellis, Sarah, Wong, Michael, White, Desiree, Novak, Olga, Fasciola, Ashley, Werner, Klaus, Lorenzi, Jill, Layer, Marcus, Thomas, Allison, Chanbers, Emily, McClintock, William M., Berl, Madison, Elling, Nancy, Kassoff, Bergen, Hardie, Kinaya, Nolan, Danielle, DeBastos, Angela, Batchelder, Christine, Koening, Mary Kay, Northrup, Hope, Au, Kit Su, Pearson, Deborah, Mansour, Rosleen, Farach, Laura, Salazar, Elida

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Abstract TP167: Prevalence of Growth Hormone Deficiency in the Chronic Phase of Recovery From Stroke von Kreber, Lisa A, Ashley, Mark J, Singh, Charan K, Randle, Kevin D, Masel, Brent E, Johnson, Christine, Helvie, Richard E, Ashley, Matthew J, Griesbach, Grace S

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Spatiotemporal regulation of endothelin receptor-B by SOX10 in neural crest-derived enteric neuron precursors von Shin, Myung K, Zhu, Lei, Lee, Hyung-Ok, Jordan, ChaRandle S, Cantrell, V Ashley, Southard-Smith, E Michelle

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