Evaluation of Dose and Safety of AAV7m8 and AAV8BP2 in the Non-Human Primate Retina von Ramachandran, Pavitra S, Lee, Vivian, Wei, Zhangyong, Song, Ji Yun, Casal, Giulia, Cronin, Therese, Willett, Keirnan, Huckfeldt, Rachel, Morgan, Jessica I W, Aleman, Tomas S, Maguire, Albert M, Bennett, Jean

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RNA interference-based therapy for spinocerebellar ataxia type 7 retinal degeneration von Ramachandran, Pavitra S, Bhattarai, Sajag, Singh, Pratibha, Boudreau, Ryan L, Thompson, Stewart, Laspada, Albert R, Drack, Arlene V, Davidson, Beverly L

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Restoration of Vision and Retinal Responses After Adeno-Associated Virus-Mediated Optogenetic Therapy in Blind Dogs von Nikonov, Sergei, Aravand, Puya, Lyubarsky, Arkady, Nikonov, Roman, Luo, Angela J, Wei, Zhangyong, Maguire, Albert M, Phelps, Nicholas T, Shpylchak, Ivan, Willett, Keirnan, Aleman, Tomas S, Huckfeldt, Rachel M, Ramachandran, Pavitra S, Bennett, Jean

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Protocols for Visually Guided Navigation Assessment of Efficacy of Retina-Directed Cell or Gene Therapy in Canines von Aravand, Puya, Ramachandran, Pavitra S, Schpylchak, Ivan, Phelps, Nicholas T, Nikonov, Sergei, Bennett, Jean

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Nonallele Specific Silencing of Ataxin-7 Improves Disease Phenotypes in a Mouse Model of SCA7 von Ramachandran, Pavitra S, Boudreau, Ryan L, Schaefer, Kellie A, La Spada, Albert R, Davidson, Beverly L

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Exploiting metabolic and antioxidant pathways to maintain vision in blinding disease von Ramachandran, Pavitra S, Song, Ji Yun, Bennett, Jean

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Recent Advances in RNA Interference Therapeutics for CNS Diseases von Ramachandran, Pavitra S., Keiser, Megan S., Davidson, Beverly L.

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270. Optogenetic Activation of Remnant Cone Cells Can Restore Ganglion Cell Light Responses in a Canine Model of Retinitis Pigmentosa von Ramachandran, Pavitra S., Nikonov, Sergei, Willett, Keirnan, Huckfeldt, Rachel, Lyubarsky, Arkady, Morgan, Jessica, Aleman, Tomas, Maguire, Albert, Bennett, Jean

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RNA Interference-Based Therapy for Spinocerebellar Ataxia Type 7 Retinal Degeneration: e95362 von Ramachandran, Pavitra S, Bhattarai, Sajag, Singh, Pratibha, Boudreau, Ryan L, Thompson, Stewart, LaSpada, Albert R, Drack, Arlene V, Davidson, Beverly L

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Altered White Matter and Sensory Response to Bodily Sensation in Female-to-Male Transgender Individuals von Case, Laura K., Brang, David, Landazuri, Rosalynn, Viswanathan, Pavitra, Ramachandran, Vilayanur S.

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Use of induced pluripotent stem cell models to probe the pathogenesis of Choroideremia and to develop a potential treatment von Duong, Thu T., Vasireddy, Vidyullatha, Ramachandran, Pavitra, Herrera, Pamela S., Leo, Lanfranco, Merkel, Carrie, Bennett, Jean, Mills, Jason A.

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Association of maternal prenatal copper concentration with gestational duration and preterm birth: a multicountry meta-analysis von Monangi, Nagendra K., Xu, Huan, Fan, Yue-Mei, Khanam, Rasheeda, Khan, Waqasuddin, Deb, Saikat, Pervin, Jesmin, Price, Joan T., Kaur, Lovejeet, Villar, Jose, McGready, Rose, Barros, Fernando C., Victora, Cesar G., Munim, Shama, Papageorgh, Aris T., Ochieng, Roseline, Craik, Rachel, Barososio, Hellen C., Berkley, James A., Carvalho, Maria, Ismail, Leila Cheikh, Lambert, Ann, Norris, Shane A., Tshivuila-Matela, Chrystelle OO, Nosten, Francois, Uauy, Ricardo, Bhutta, Zulfiqar A., Kennedy, Stephen, Al Mahmud, Abdullah, Thanh, Le Quang, Care, Angharad, Landero, Julio A., Combs, Gerald F., Belling, Elizabeth, Chappell, Joanne, Chen, Jing, Kong, Fansheng, Lacher, Craig, Ahmed, Salahuddin, Chowdhury, Nabidul Haque, Rahman, Sayedur, Kabir, Furqan, Nisar, Imran, Hotwani, Aneeta, Mehmood, Usma, Nizar, Ambreen, Khalid, Javairia, Dhingra, Usha, Dutta, Arup, Ali, Said Mohamed, Aftab, Fahad, Juma, Mohammed Hamad, Rahman, Monjur, Ahmed, Tahmeed, Islam, M Munirul, Vwalika, Bellington, Musonda, Patrick, Ashorn, Ulla, Maleta, Kenneth, Hallman, Mikko, Goodfellow, Laura, Gupta, Juhi K., Alfirevic, Ana, Murphy, Susan K., Rand, Larry, Ryckman, Kelli K., Murray, Jeffrey C., Bahl, Rajiv, Litch, James A., Baruch-Gravett, Courtney, Sopory, Shailaja, Chandra Mouli Natchu, Uma, Kumar, Pavitra V., Kumari, Neha, Thiruvengadam, Ramachandran, Singh, Atul Kumar, Kumar, Pankaj, Alfirevic, Zarko, Baqui, Abdullah H., Bhatnagar, Shinjini, Hirst, Jane E., Hoyo, Cathrine, Jehan, Fyezah, Jelliffe-Pawlowski, Laura, Rahman, Anisur, Roth, Daniel E., Sazawal, Sunil, Stringer, Jeffrey S.A., Ashorn, Per, Zhang, Ge, Muglia, Louis J.

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C. elegans HAM-1 functions in the nucleus to regulate asymmetric neuroblast division von Leung, Amy, Hua, Khang, Ramachandran, Pavitra, Hingwing, Kyla, Wu, Maria, Koh, Pei Luan, Hawkins, Nancy

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ANTISENSE OLIGOMERS FOR TREATMENT OF NON-SENSE MEDIATED RNA DECAY BASED CONDITIONS AND DISEASES von AZNAREZ, Isabel, KACH, Jacob, SAIZ, Ana Corrionero, RAMACHANDRAN, Pavitra

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