Observational study of spinal muscular atrophy type I and implications for clinical trials von Finkel, Richard S, McDermott, Michael P, Kaufmann, Petra, Darras, Basil T, Chung, Wendy K, Sproule, Douglas M, Kang, Peter B, Foley, A Reghan, Yang, Michelle L, Martens, William B, Oskoui, Maryam, Glanzman, Allan M, Flickinger, Jean, Montes, Jacqueline, Dunaway, Sally, OʼHagen, Jessica, Quigley, Janet, Riley, Susan, Benton, Maryjane, Ryan, Patricia A, Montgomery, Megan, Marra, Jonathan, Gooch, Clifton, De Vivo, Darryl C

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Clinical trial of a farnesyltransferase inhibitor in children with Hutchinson–Gilford progeria syndrome von Gordon, Leslie B, Kleinman, Monica E, Miller, David T, Neuberg, Donna S, Giobbie-Hurder, Anita, Gerhard-Herman, Marie, Smoot, Leslie B, Gordon, Catherine M, Cleveland, Robert, Snyder, Brian D, Fligor, Brian, Bishop, W. Robert, Statkevich, Paul, Regen, Amy, Sonis, Andrew, Riley, Susan, Ploski, Christine, Correia, Annette, Quinn, Nicolle, Ullrich, Nicole J, Nazarian, Ara, Liang, Marilyn G, Huh, Susanna Y, Schwartzman, Armin, Kieran, Mark W

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A three-dimensional osteochondral composite scaffold for articular cartilage repair von Sherwood, Jill K, Riley, Susan L, Palazzolo, Robert, Brown, Scott C, Monkhouse, Donald C, Coates, Matt, Griffith, Linda G, Landeen, Lee K, Ratcliffe, Anthony

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Improving diabetes outcomes by an innovative group visit model: A pilot study von Riley, Susan B.

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Effect of FePd alloy composition on the dynamics of artificial spin ice von Morley, Sophie A., Riley, Susan T., Porro, Jose-Maria, Rosamond, Mark C., Linfield, Edmund H., Cunningham, John E., Langridge, Sean, Marrows, Christopher H.

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An expanded version of the Hammersmith Functional Motor Scale for SMA II and III patients von O’Hagen, Jessica M, Glanzman, Allan M, McDermott, Michael P, Ryan, Patricia A, Flickinger, Jean, Quigley, Janet, Riley, Susan, Sanborn, Erica, Irvine, Carrie, Martens, William B, Annis, Christine, Tawil, Rabi, Oskoui, Maryam, Darras, Basil T, Finkel, Richard S, De Vivo, Darryl C

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Motor and cognitive assessment of infants and young boys with Duchenne Muscular Dystrophy: results from the Muscular Dystrophy Association DMD Clinical Research Network von Connolly, Anne M, Florence, Julaine M, Cradock, Mary M, Malkus, Elizabeth C, Schierbecker, Jeanine R, Siener, Catherine A, Wulf, Charlie O, Anand, Pallavi, Golumbek, Paul T, Zaidman, Craig M, Philip Miller, J, Lowes, Linda P, Alfano, Lindsay N, Viollet-Callendret, Laurence, Flanigan, Kevin M, Mendell, Jerry R, McDonald, Craig M, Goude, Erica, Johnson, Linda, Nicorici, Alina, Karachunski, Peter I, Day, John W, Dalton, Joline C, Farber, Janey M, Buser, Karen K, Darras, Basil T, Kang, Peter B, Riley, Susan O, Shriber, Elizabeth, Parad, Rebecca, Bushby, Kate, Eagle, Michelle

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Spinal muscular atrophy functional composite score: A functional measure in spinal muscular atrophy von Montes, Jacqueline, Glanzman, Allan M., Mazzone, Elena S., Martens, William B., Dunaway, Sally, Pasternak, Amy, Riley, Susan O, Quigley, Janet, Pandya, Shree, De Vivo, Darryl C, Kaufmann, Petra, Chiriboga, Claudia A., Finkel, Richard S., Tennekoon, Gihan I., Darras, Basil T., Pane, Marika, Mercuri, Eugenio, Mcdermott, Michael P.

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Three-dimensional culture of rat calvarial osteoblasts in porous biodegradable polymers von Ishaug-Riley, Susan L., Crane-Kruger, Genevieve M., Yaszemski, Michael J., Mikos, Antonios G.

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Human articular chondrocyte adhesion and proliferation on synthetic biodegradable polymer films von Ishaug-Riley, Susan L, Okun, Laura E, Prado, Gustavo, Applegate, Mark A, Ratcliffe, Anthony

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An investigation of the photo-clastogenic potential of ultrafine titanium dioxide particles von Theogaraj, Elizabeth, Riley, Susan, Hughes, Laurie, Maier, Monika, Kirkland, David

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Validation of the Children's Hospital of Philadelphia Infant Test of Neuromuscular Disorders (CHOP INTEND) von Glanzman, Allan M, McDermott, Michael P, Montes, Jacqueline, Martens, William B, Flickinger, Jean, Riley, Susan, Quigley, Janet, Dunaway, Sally, O'Hagen, Jessica, Deng, Liyong, Chung, Wendy K, Tawil, Rabi, Darras, Basil T, Yang, Michele, Sproule, Douglas, De Vivo, Darryl C, Kaufmann, Petra, Finkel, Richard S

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Impact of Farnesylation Inhibitors on Survival in Hutchinson-Gilford Progeria Syndrome von GORDON, Leslie B, MASSARO, Joe, D'AGOSTINO, Ralph B, CAMPBELL, Susan E, BRAZIER, Joan, BROWN, W. Ted, KLEINMAN, Monica E, KIERAN, Mark W

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Issues in the development of open access to research data von Wessels, Bridgette, Finn, Rachel L., Linde, Peter, Mazzetti, Paolo, Nativi, Stefano, Riley, Susan, Smallwood, Rod, Taylor, Mark J., Tsoukala, Victoria, Wadhwa, Kush, Wyatt, Sally

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Group Visits in Diabetes Care: A Systematic Review von Riley, Susan Braun, Marshall, Elaine Sorensen

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Strength retention of 70:30 poly(L-lactide-co-D,L-lactide) following real-time aging von Moser, Rodney C., McManus, Anastasia J., Riley, Susan L., Thomas, Kevin A.

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Prospective cohort study of spinal muscular atrophy types 2 and 3 von KAUFMANN, Petra, MCDERMOTT, Michael P, YANG, Michele L, TAWIL, Rabi, CHUNG, Wendy K, MARTENS, William B, MONTES, Jacqueline, BATTISTA, Vanessa, O'HAGEN, Jessica, DUNAWAY, Sally, FLICKINGER, Jean, QUIGLEY, Janet, DARRAS, Basil T, RILEY, Susan, GLANZMAN, Allan M, BENTON, Maryjane, RYAN, Patricia A, PUNYANITYA, Mark, MONTGOMERY, Megan J, MARRA, Jonathan, KOO, Benjamin, DE VIVO, Darryl C, FINKEL, Richard S, SPROULE, Douglas M, KANG, Peter B, OSKOUI, Maryam, CONSTANTINESCU, Andrei, GOOCH, Clifton L, REGHAN FOLEY, A

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Formulation of PEG-based hydrogels affects tissue-engineered cartilage construct characteristics von Riley, S L, Dutt, S, De La Torre, R, Chen, A C, Sah, R L, Ratcliffe, A

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Autoimmune disease and COVID-19: a multicentre observational study in the United Kingdom von Arachchillage, Deepa J, Rajakaruna, Indika, Pericleous, Charis, Nicolson, Philip L R, Makris, Mike, Laffan, Mike

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Validation of NucleoCounter, an Automated Cell Counter von Saini, Jaspreet, Kim, Jacquelynne J., Preston, Lori A., Riley, Susan L., Ashley, Louise J., Landeen, Lee K.

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