Engineering adeno-associated virus vectors for gene therapy von Li, Chengwen, Samulski, R. Jude

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Adeno-associated virus at 50: a golden anniversary of discovery, research, and gene therapy success--a personal perspective von Hastie, Eric, Samulski, R Jude

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AAV-Mediated Gene Therapy for Research and Therapeutic Purposes von Samulski, R Jude, Muzyczka, Nicholas

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Adeno-associated Virus Serotypes: Vector Toolkit for Human Gene Therapy von Wu, Zhijian, Asokan, Aravind, Samulski, R Jude

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Viral vectors for gene delivery to the central nervous system von Lentz, Thomas B, Gray, Steven J, Samulski, R. Jude

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BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression von Konkle, Barbara A., Walsh, Christopher E., Escobar, Miguel A., Josephson, Neil C., Young, Guy, von Drygalski, Annette, McPhee, Scott W.J., Samulski, R. Jude, Bilic, Ivan, de la Rosa, Maurus, Reipert, Birgit M., Rottensteiner, Hanspeter, Scheiflinger, Friedrich, Chapin, John C., Ewenstein, Bruce, Monahan, Paul E.

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Bound Protein- and Peptide-Based Strategies for Adeno-Associated Virus Vector-Mediated Gene Therapy: Where Do We Stand Now? von Zhang, Xintao, Chai, Zheng, Samulski, R. Jude, Li, Chengwen

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Production and characterization of adeno-associated viral vectors von Samulski, R Jude, Grieger, Joshua C, Choi, Vivian W

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Structure and Dynamics of Adeno-Associated Virus Serotype 1 VP1-Unique N-Terminal Domain and Its Role in Capsid Trafficking von Venkatakrishnan, Balasubramanian, Yarbrough, Joseph, Domsic, John, Bennett, Antonette, Bothner, Brian, Kozyreva, Olga G., Samulski, R. Jude, Muzyczka, Nicholas, McKenna, Robert, Agbandje-McKenna, Mavis

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Enhancement of Adeno-Associated Virus Infection by Mobilizing Capsids into and Out of the Nucleolus von JOHNSON, Jarrod S, SAMULSKI, R. Jude

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Mechanistic Insights into the Enhancement of Adeno-Associated Virus Transduction by Proteasome Inhibitors von Mitchell, Angela M, Samulski, R Jude

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Employing a gain-of-function factor IX variant R338L to advance the efficacy and safety of hemophilia B human gene therapy: preclinical evaluation supporting an ongoing adeno-assoc... von Monahan, Paul E, Sun, Junjiang, Gui, Tong, Hu, Genlin, Hannah, William B, Wichlan, David G, Wu, Zhijian, Grieger, Joshua C, Li, Chengwen, Suwanmanee, Thipparat, Stafford, Darrel W, Booth, Carmen J, Samulski, Jade J, Kafri, Tal, McPhee, Scott W J, Samulski, R Jude

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Structural Characterization of the Dual Glycan Binding Adeno-Associated Virus Serotype 6 von Ng, Robert, Govindasamy, Lakshmanan, Gurda, Brittney L, McKenna, Robert, Kozyreva, Olga G, Samulski, R Jude, Parent, Kristin N, Baker, Timothy S, Agbandje-McKenna, Mavis

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Heparan Sulfate Binding Promotes Accumulation of Intravitreally Delivered Adeno-associated Viral Vectors at the Retina for Enhanced Transduction but Weakly Influences Tropism von Woodard, Kenton T, Liang, Katharine J, Bennett, William C, Samulski, R Jude

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Customized blood-brain barrier shuttle peptide to increase AAV9 vector crossing the BBB and augment transduction in the brain von Zhang, Xintao, Chai, Zheng, Lee Dobbins, Amanda, Itano, Michelle S., Askew, Charles, Miao, Zhe, Niu, Hongqian, Samulski, R. Jude, Li, Chengwen

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Human Galectin 3 Binding Protein Interacts with Recombinant Adeno-Associated Virus Type 6 von DENARD, Jerome, BELEY, Cyriaque, GARCIA, Luis, SVINARTCHOUK, Fedor, KOTIN, Robert, LAI-KUEN, Rene, BLOT, Stephane, LEH, Herve, ASOKAN, Aravind, SAMULSKI, R. Jude, MOULLIER, Philippe, VOIT, Thomas

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Atomic structure of a rationally engineered gene delivery vector, AAV2.5 von Burg, Matthew, Rosebrough, Claire, Drouin, Lauren M., Bennett, Antonette, Mietzsch, Mario, Chipman, Paul, McKenna, Robert, Sousa, Duncan, Potter, Mark, Byrne, Barry, Jude Samulski, R., Agbandje-McKenna, Mavis

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Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle von Asokan, Aravind, Conway, Julia C, Phillips, Jana L, Li, Chengwen, Hegge, Julia, Sinnott, Rebecca, Yadav, Swati, DiPrimio, Nina, Nam, Hyun-Joo, Agbandje-McKenna, Mavis, McPhee, Scott, Wolff, Jon, Samulski, R Jude

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AAV8 virions hijack serum proteins to increase hepatocyte binding for transduction enhancement von Pei, Xiaolei, He, Ting, Hall, Nikita E., Gerber, David, Samulski, R. Jude, Li, Chengwen

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Little Vector, Big Gene Transduction: Fragmented Genome Reassembly of Adeno-associated Virus von Hirsch, Matthew L, Agbandje-McKenna, Mavis, Jude Samulski, R

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