BIVV001 Fusion Protein as Factor VIII Replacement Therapy for Hemophilia A von Konkle, Barbara A, Shapiro, Amy D, Quon, Doris V, Staber, Janice M, Kulkarni, Roshni, Ragni, Margaret V, Chhabra, Ekta S, Poloskey, Stacey, Rice, Kara, Katragadda, Suresh, Fruebis, Joachim, Benson, Craig C

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Invasive procedures and surgery following etranacogene dezaparvovec gene therapy in people with hemophilia B von O’Connell, Niamh, van der Valk, Paul, Le Quellec, Sandra, Gomez, Esteban, Monahan, Paul E., Crary, Shelley E., Coppens, Michiel, Lemons, Richard, Castaman, Giancarlo, Klamroth, Robert, Symington, Emily, Quon, Doris V., Kampmann, Peter

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Three-year outcomes of valoctocogene roxaparvovec gene therapy for hemophilia A von Madan, Bella, Ozelo, Margareth C., Raheja, Priyanka, Symington, Emily, Quon, Doris V., Leavitt, Andrew D., Pipe, Steven W., Lowe, Gillian, Kenet, Gili, Reding, Mark T., Mason, Jane, Wang, Michael, von Drygalski, Annette, Klamroth, Robert, Shapiro, Susan, Chambost, Hervé, Dunn, Amy L., Oldenburg, Johannes, Chou, Sheng-Chieh, Peyvandi, Flora, Millar, Carolyn M., Osmond, Dane, Yu, Hua, Dashiell-Aje, Ebony, Robinson, Tara M., Mahlangu, Johnny

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Prevalence and Risk Factors for Hypertension in Hemophilia von von Drygalski, Annette, Kolaitis, Nicholas A, Bettencourt, Ricki, Bergstrom, Jaclyn, Kruse-Jarres, R, Quon, Doris V, Wassel, Christina, Li, Ming C, Waalen, Jill, Elias, Darlene J, Mosnier, Laurent O, Allison, Matthew

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Consistency of serial ultrasonographic joint tissue measurements by the Joint tissueActivity and Damage Exam (JADE) protocol in relation to hemophilic joint health parameters von Barnes, Richard F. W., Aguero, Peter, Hanacek, Cris, Flores, Andres, Steiner, Bruno, Bailey, Cindy, Quon, Doris V., Kruse-Jarres, Rebecca, von Drygalski, Annette

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Efficacy, safety, and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr8-1 trial von Leavitt, Andrew D., Mahlangu, Johnny, Raheja, Priyanka, Symington, Emily, Quon, Doris V., Giermasz, Adam, López Fernández, Maria Fernanda, Kenet, Gili, Lowe, Gillian, Key, Nigel S., Millar, Carolyn M., Pipe, Steven W., Madan, Bella, Chou, Sheng-Chieh, Klamroth, Robert, Mason, Jane, Chambost, Hervé, Peyvandi, Flora, Majerus, Elaine, Pepperell, Dominic, Rivat, Christine, Yu, Hua, Robinson, Tara M., Ozelo, Margareth C.

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Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A von Ozelo, Margareth C, Mahlangu, Johnny, Pasi, K. John, Giermasz, Adam, Leavitt, Andrew D, Laffan, Michael, Symington, Emily, Quon, Doris V, Wang, Jiaan-Der, Peerlinck, Kathelijne, Pipe, Steven W, Madan, Bella, Key, Nigel S, Pierce, Glenn F, O’Mahony, Brian, Kaczmarek, Radoslaw, Henshaw, Joshua, Lawal, Adebayo, Jayaram, Kala, Huang, Mei, Yang, Xinqun, Wong, Wing Y, Kim, Benjamin

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Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A von Mahlangu, Johnny, Kaczmarek, Radoslaw, von Drygalski, Annette, Shapiro, Susan, Chou, Sheng-Chieh, Ozelo, Margareth C., Kenet, Gili, Peyvandi, Flora, Wang, Michael, Madan, Bella, Key, Nigel S., Laffan, Michael, Dunn, Amy L., Mason, Jane, Quon, Doris V., Symington, Emily, Leavitt, Andrew D., Oldenburg, Johannes, Chambost, Hervé, Reding, Mark T., Jayaram, Kala, Yu, Hua, Mahajan, Reena, Chavele, Konstantia-Maria, Reddy, Divya B., Henshaw, Joshua, Robinson, Tara M., Wong, Wing Yen, Pipe, Steven W.

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Outcomes and management of invasive procedures in participants with hemophilia A post gene therapy: a post hoc analysis of the GENEr8-1 phase III trial von Quon, Doris V., Wang, Jiaan-Der, Wang, Michael, Pepperell, Dominic, Park, Young-Shil, Kenet, Gili, Mahlangu, Johnny, Khoo, Teh-Liane, Robinson, Tara M., Chavele, Konstantia-Maria, Pipe, Steven W.

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Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A von Klamroth, Robert, Hayes, Gregory, Andreeva, Tatiana, Gregg, Keith, Suzuki, Takashi, Mitha, Ismail Haroon, Hardesty, Brandon, Shima, Midori, Pollock, Toni, Slev, Patricia, Oldenburg, Johannes, Ozelo, Margareth C, Stieltjes, Natalie, Castet, Sabine-Marie, Mahlangu, Johnny, Peyvandi, Flora, Kazmi, Rashid, Schved, Jean-François, Leavitt, Andrew D, Callaghan, Michael, Pan-Petesch, Brigitte, Quon, Doris V, Andrews, Jayson, Trinh, Alex, Li, Mingjin, Wong, Wing Yen

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Risk of diabetes in haemophilia patients compared to clinic and non‐clinic control cohorts von Pandey, Braj, Barnes, Richard F.W., Sun, Haowei (Linda), Jackson, Shannon, Kruse‐Jarres, Rebecca, Quon, Doris V., von Drygalski, Annette

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The Hypertension of Hemophilia Is Not Explained by the Usual Cardiovascular Risk Factors: Results of a Cohort Study von Quon, Doris V. K., Kruse-Jarres, Rebecca, Sait, Afrah S., Cramer, Thomas J., Barnes, Richard F. W., von Drygalski, A.

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Real‐world data demonstrate improved bleed control and extended dosing intervals for patients with haemophilia B after switching to recombinant factor IX Fc fusion protein (rFIXFc)... von Shapiro, Amy, Chaudhury, Ateefa, Wang, Michael, Escobar, Miguel, Tsao, Elisa, Barnowski, Christopher, Feng, Jing, Jain, Nisha, Quon, Doris V.

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Development and Reliability of the Joint Tissue Activity and Damage Examination for Quantitation of Structural Abnormalities by Musculoskeletal Ultrasound in Hemophilic Joints von Volland, Lena M., Zhou, Jenny Y., Barnes, Richard F. W., Kruse‐Jarres, Rebecca, Steiner, Bruno, Quon, Doris V., Bailey, Cindy, Hughes, Tudor H., Moore, Randy E., Chang, Eric Y., von Drygalski, Annette

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Diabetes, hepatitis C and human immunodeficiency virus influence hypertension risk differently in cohorts of haemophilia patients, veterans and the general population von Barnes, Richard F.W., Pandey, Braj, Sun, Haowei (Linda), Jackson, Shannon, Kruse‐Jarres, Rebecca, Quon, Doris V., Drygalski, Annette

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Blood pressure in persons with haemophilia with a focus on haemophilia‐specific risk factors von Ter‐Zakarian, Anna, Barnes, Richard F. W., Kruse‐Jarres, Rebecca, Quon, Doris V., Jackson, Shannon, Sun, Haowei (Linda), Drygalski, Annette

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Physical activity in individuals with haemophilia and experience with recombinant factor VIII Fc fusion protein and recombinant factor IX Fc fusion protein for the treatment of act... von Wang, Michael, Álvarez-Román, María Teresa, Chowdary, Pratima, Quon, Doris V, Schafer, Kim

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A Dynamin Is Required for the Biogenesis of Secretory Organelles in Toxoplasma gondii von Breinich, Manuela S., Ferguson, David J.P., Foth, Bernardo J., van Dooren, Giel G., Lebrun, Maryse, Quon, Doris V., Striepen, Boris, Bradley, Peter J., Frischknecht, Friedrich, Carruthers, Vern B., Meissner, Markus

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Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial von Coppens, Michiel, Pipe, Steven W, Miesbach, Wolfgang, Astermark, Jan, Recht, Michael, van der Valk, Paul, Ewenstein, Bruce, Pinachyan, Karen, Galante, Nicholas, Le Quellec, Sandra, Monahan, Paul E, Leebeek, Frank W G, Castaman, Giancarlo, Crary, Shelley E, Escobar, Miguel, Gomez, Esteban, Haley, Kristina M, Hermans, Cedric R J R, Kampmann, Peter, Kazmi, Rashid, Key, Nigel S, Klamroth, Robert, Konkle, Barbara A, Kruse-Jarres, Rebecca, Lattimore, Susan, Lemons, Richard, Meijer, Karina, O'Connell, Niamh, Quon, Doris V, Raheja, Priyanka, Symington, Emily, Verhamme, Peter, Visweshwar, Nathan, von Drygalski, Annette, Wang, Michael, Wheeler, Allison P, White, Shanna, Young, Guy

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A phase 1B/2 study of aldoxorubicin in patients with soft tissue sarcoma von Chawla, Sant P., Chua, Victoria S., Hendifar, Andrew F., Quon, Doris V., Soman, Neelesh, Sankhala, Kamalesh K., Wieland, D. Scott, Levitt, Daniel J.

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