Efficient and sustained FOXP3 locus editing in hematopoietic stem cells as a therapeutic approach for IPEX syndrome von Singh, Swati, Pugliano, Cole M., Honaker, Yuchi, Laird, Aidan, DeGottardi, M. Quinn, Lopez, Ezra, Lachkar, Stefan, Stoffers, Claire, Sommer, Karen, Khan, Iram F., Rawlings, David J.

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DNA-PK inhibition enhances gene editing efficiency in HSPCs for CRISPR-based treatment of X-linked hyper IgM syndrome von Pugliano, Cole M., Berger, Mason, Ray, Roslyn M., Sapkos, Kai, Wu, Betty, Laird, Aidan, Ye, Yidian, Thomson, Daniel, DeGottardi, M. Quinn, Khan, Iram F., Tatiossian, Kristina, Miles, Brodie A., Aeschimann, Florian, Pasquier, Jerome, Kim, Mihee M., Rawlings, David J.

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