Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A von Pasi, K. John, Rangarajan, Savita, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Laffan, Michael, Russell, Chris B, Li, Mingjin, Pierce, Glenn F, Wong, Wing Y

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Targeting of Antithrombin in Hemophilia A or B with RNAi Therapy von Pasi, K. John, Rangarajan, Savita, Georgiev, Pencho, Mant, Tim, Creagh, Michael D, Lissitchkov, Toshko, Bevan, David, Austin, Steve, Hay, Charles R, Hegemann, Inga, Kazmi, Rashid, Chowdary, Pratima, Gercheva-Kyuchukova, Liana, Mamonov, Vasily, Timofeeva, Margarita, Soh, Chang-Heok, Garg, Pushkal, Vaishnaw, Akshay, Akinc, Akin, Sørensen, Benny, Ragni, Margaret V

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AAV5–Factor VIII Gene Transfer in Severe Hemophilia A von Rangarajan, Savita, Walsh, Liron, Lester, Will, Perry, David, Madan, Bella, Laffan, Michael, Yu, Hua, Vettermann, Christian, Pierce, Glenn F, Wong, Wing Y, Pasi, K. John

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Interindividual variability in transgene mRNA and protein production following adeno-associated virus gene therapy for hemophilia A von Fong, Sylvia, Yates, Bridget, Sihn, Choong-Ryoul, Mattis, Aras N., Mitchell, Nina, Liu, Su, Russell, Chris B., Kim, Benjamin, Lawal, Adebayo, Rangarajan, Savita, Lester, Will, Bunting, Stuart, Pierce, Glenn F., Pasi, K. John, Wong, Wing Yen

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Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A von Ozelo, Margareth C, Mahlangu, Johnny, Pasi, K. John, Giermasz, Adam, Leavitt, Andrew D, Laffan, Michael, Symington, Emily, Quon, Doris V, Wang, Jiaan-Der, Peerlinck, Kathelijne, Pipe, Steven W, Madan, Bella, Key, Nigel S, Pierce, Glenn F, O’Mahony, Brian, Kaczmarek, Radoslaw, Henshaw, Joshua, Lawal, Adebayo, Jayaram, Kala, Huang, Mei, Yang, Xinqun, Wong, Wing Y, Kim, Benjamin

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Lupus Anticoagulant and Abnormal Coagulation Tests in Patients with Covid-19 von Bowles, Louise, Platton, Sean, Yartey, Nada, Dave, Minal, Lee, Kurtis, Hart, Daniel P, MacDonald, Vickie, Green, Laura, Sivapalaratnam, Suthesh, Pasi, K. John, MacCallum, Peter

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Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A von Pasi, K John, Rangarajan, Savita, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Laffan, Michael, Russell, Chris B, Li, Mingjin, Pierce, Glenn F, Wong, Wing Y

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Activity of transgene-produced B-domain–deleted factor VIII in human plasma following AAV5 gene therapy von Rosen, Steffen, Tiefenbacher, Stefan, Robinson, Mary, Huang, Mei, Srimani, Jaydeep, Mackenzie, Donnie, Christianson, Terri, Pasi, K. John, Rangarajan, Savita, Symington, Emily, Giermasz, Adam, Pierce, Glenn F., Kim, Benjamin, Zoog, Stephen J., Vettermann, Christian

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The incidence and magnitude of fibrinolytic activation in trauma patients von RAZA, I., DAVENPORT, R., ROURKE, C., PLATTON, S., MANSON, J., SPOORS, C., KHAN, S., De'ATH, H. D., ALLARD, S., HART, D. P., PASI, K. J., HUNT, B. J., STANWORTH, S., MacCALLUM, P. K., BROHI, K.

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Comparative genome analysis indicates high evolutionary potential of pathogenicity genes in Colletotrichum tanaceti von Lelwala, Ruvini V, Korhonen, Pasi K, Young, Neil D, Scott, Jason B, Ades, Peter K, Gasser, Robin B, Taylor, Paul W J

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Functional definition and characterization of acute traumatic coagulopathy von Davenport, Ross, Manson, Joanna, DeʼAth, Henry, Platton, Sean, Coates, Amy, Allard, Shubha, Hart, Daniel, Pearse, Rupert, Pasi, K. John, MacCallum, Peter, Stanworth, Simon, Brohi, Karim

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Lupus Anticoagulant in Patients with Covid-19. Reply von Platton, Sean, Bowles, Louise, Pasi, K John

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Phase 3 study of recombinant factor VIII Fc fusion protein in severe hemophilia A von Mahlangu, Johnny, Powell, Jerry S., Ragni, Margaret V., Chowdary, Pratima, Josephson, Neil C., Pabinger, Ingrid, Hanabusa, Hideji, Gupta, Naresh, Kulkarni, Roshni, Fogarty, Patrick, Perry, David, Shapiro, Amy, Pasi, K. John, Apte, Shashikant, Nestorov, Ivan, Jiang, Haiyan, Li, Shuanglian, Neelakantan, Srividya, Cristiano, Lynda M., Goyal, Jaya, Sommer, Jurg M., Dumont, Jennifer A., Dodd, Nigel, Nugent, Karen, Vigliani, Gloria, Luk, Alvin, Brennan, Aoife, Pierce, Glenn F.

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Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia A von Pasi, K John, Laffan, Michael, Rangarajan, Savita, Robinson, Tara M, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Yang, Xinqun, Kim, Benjamin, Pierce, Glenn F, Wong, Wing Yen

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Whole-genome sequence of the bovine blood fluke Schistosoma bovis supports interspecific hybridization with S. haematobium von Oey, Harald, Zakrzewski, Martha, Gravermann, Kerstin, Young, Neil D, Korhonen, Pasi K, Gobert, Geoffrey N, Nawaratna, Sujeevi, Hasan, Shihab, Martínez, David M, You, Hong, Lavin, Martin, Jones, Malcolm K, Ragan, Mark A, Stoye, Jens, Oleaga, Ana, Emery, Aidan M, Webster, Bonnie L, Rollinson, David, Gasser, Robin B, McManus, Donald P, Krause, Lutz

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Dafachronic acid promotes larval development in Haemonchus contortus by modulating dauer signalling and lipid metabolism von Ma, Guangxu, Wang, Tao, Korhonen, Pasi K, Young, Neil D, Nie, Shuai, Ang, Ching-Seng, Williamson, Nicholas A, Reid, Gavin E, Gasser, Robin B

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First record of a tandem-repeat region within the mitochondrial genome of Clonorchis sinensis using a long-read sequencing approach von Kinkar, Liina, Young, Neil D, Sohn, Woon-Mok, Stroehlein, Andreas J, Korhonen, Pasi K, Gasser, Robin B

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Nuclear genome of Bulinus truncatus, an intermediate host of the carcinogenic human blood fluke Schistosoma haematobium von Young, Neil D., Stroehlein, Andreas J., Wang, Tao, Korhonen, Pasi K., Mentink-Kane, Margaret, Stothard, J. Russell, Rollinson, David, Gasser, Robin B.

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Phylogenomic and biogeographic reconstruction of the Trichinella complex von Korhonen, Pasi K., Pozio, Edoardo, La Rosa, Giuseppe, Chang, Bill C. H., Koehler, Anson V., Hoberg, Eric P., Boag, Peter R., Tan, Patrick, Jex, Aaron R., Hofmann, Andreas, Sternberg, Paul W., Young, Neil D., Gasser, Robin B.

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Targeting of antithrombin in hemophilia A or B with investigational siRNA therapeutic fitusiran—Results of the phase 1 inhibitor cohort von Pasi, K. John, Lissitchkov, Toshko, Mamonov, Vasily, Mant, Tim, Timofeeva, Margarita, Bagot, Catherine, Chowdary, Pratima, Georgiev, Pencho, Gercheva‐Kyuchukova, Liana, Madigan, Kate, Nguyen, Huy, Yu, Qifeng, Mei, Baisong, Benson, Craig C., Ragni, Margaret V.

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