Context base editing for splice correction of IVSI-110 β-thalassemia von Naiisseh, Basma, Papasavva, Panayiota L., Papaioannou, Nikoletta Y., Tomazou, Marios, Koniali, Lola, Felekis, Xenia, Constantinou, Constantina G., Sitarou, Maria, Christou, Soteroula, Kleanthous, Marina, Lederer, Carsten W., Patsali, Petros

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Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by HBBAS3 Gene Addition and Mutation-Specific RNA Interference von Koniali, Lola, Flouri, Christina, Kostopoulou, Markela I., Papaioannou, Nikoletta Y., Papasavva, Panayiota L., Naiisseh, Basma, Stephanou, Coralea, Demetriadou, Anthi, Sitarou, Maria, Christou, Soteroula, Antoniou, Michael N., Kleanthous, Marina, Patsali, Petros, Lederer, Carsten W.

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High-efficiency editing in hematopoietic stem cells and the HUDEP-2 cell line based on in vitro mRNA synthesis von Papaioannou, Nikoletta Y, Patsali, Petros, Naiisseh, Basma, Papasavva, Panayiota L, Koniali, Lola, Kurita, Ryo, Nakamura, Yukio, Christou, Soteroula, Sitarou, Maria, Mussolino, Claudio, Cathomen, Toni, Kleanthous, Marina, Lederer, Carsten W

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Distinct miRNA Signatures and Networks Discern Fetal from Adult Erythroid Differentiation and Primary from Immortalized Erythroid Cells von Papasavva, Panayiota L, Papaioannou, Nikoletta Y, Patsali, Petros, Kurita, Ryo, Nakamura, Yukio, Sitarou, Maria, Christou, Soteroulla, Kleanthous, Marina, Lederer, Carsten W

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Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by IHBBAS3/I Gene Addition and Mutation-Specific RNA Interference von Koniali, Lola, Flouri, Christina, Kostopoulou, Markela I, Papaioannou, Nikoletta Y, Papasavva, Panayiota L, Naiisseh, Basma, Stephanou, Coralea, Demetriadou, Anthi, Sitarou, Maria, Christou, Soteroula, Antoniou, Michael N, Kleanthous, Marina, Patsali, Petros, Lederer, Carsten W

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Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by HBB AS3 Gene Addition and Mutation-Specific RNA Interference von Koniali, Lola, Flouri, Christina, Kostopoulou, Markela I, Papaioannou, Nikoletta Y, Papasavva, Panayiota L, Naiisseh, Basma, Stephanou, Coralea, Demetriadou, Anthi, Sitarou, Maria, Christou, Soteroula, Antoniou, Michael N, Kleanthous, Marina, Patsali, Petros, Lederer, Carsten W

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