Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial von Mercuri, Eugenio, Muntoni, Francesco, Baranello, Giovanni, Masson, Riccardo, Boespflug-Tanguy, Odile, Bruno, Claudio, Corti, Stefania, Daron, Aurore, Deconinck, Nicolas, Servais, Laurent, Straub, Volker, Ouyang, Haojun, Chand, Deepa, Tauscher-Wisniewski, Sitra, Mendonca, Nuno, Lavrov, Arseniy, Seferian, A., De Lucia, S., Tachibana, S., Jollet, A., Mouffak, S., Pedemonte, M., Brolatti, N., Morando, S., Vanlander, A., De Vos, E., Tahon, V., Govoni, A., Magri, F., Comi, G., Foa, M., Parente, V., Buscemi, L., Dal Farra, F., Schneider, O., Jonas, A., Defeldre, A.C., Pagliano, E., Zanin, R., Arnoldi, M.T., Schembri, V., Del Sole, M., Mandelli, A., Pera, M.C., Antonaci, L., Coratti, G., de Sanctis, R., Pane, M., Scoto, M., Groves, K., Edel, L., Abel, F., Van Ruiten, H., Lofra, R.M., Thompson, E.

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2018 consensus statement by the Spanish Society of Pathology and the Spanish Society of Medical Oncology on the diagnosis and treatment of cancer of unknown primary von Losa, F., Iglesias, L., Pané, M., Sanz, J., Nieto, B., Fusté, V., de la Cruz-Merino, L., Concha, Á., Balañá, C., Matías-Guiu, X.

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Labor cost and organizational performance of a restaurant company in Indonesia during the pandemic von Pane, M. A. F., Setiadi, N. J.

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Longitudinal effect of eteplirsen versus historical control on ambulation in Duchenne muscular dystrophy von Mendell, Jerry R., Goemans, Nathalie, Lowes, Linda P., Alfano, Lindsay N., Berry, Katherine, Shao, James, Kaye, Edward M., Mercuri, Eugenio

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The Children’s Hospital of Philadelphia Infant Test of Neuromuscular Disorders (CHOP INTEND): Test development and reliability von Glanzman, A.M, Mazzone, E, Main, M, Pelliccioni, M, Wood, J, Swoboda, K.J, Scott, C, Pane, M, Messina, S, Bertini, E, Mercuri, E, Finkel, R.S

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MYH7-related myopathies: clinical, histopathological and imaging findings in a cohort of Italian patients von Fiorillo, C, Astrea, G, Savarese, M, Cassandrini, D, Brisca, G, Trucco, F, Pedemonte, M, Trovato, R, Ruggiero, L, Vercelli, L, D'Amico, A, Tasca, G, Pane, M, Fanin, M, Bello, L, Broda, P, Musumeci, O, Rodolico, C, Messina, S, Vita, G L, Sframeli, M, Gibertini, S, Morandi, L, Mora, M, Maggi, L, Petrucci, A, Massa, R, Grandis, M, Toscano, A, Pegoraro, E, Mercuri, E, Bertini, E, Mongini, T, Santoro, L, Nigro, V, Minetti, C, Santorelli, F M, Bruno, C

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Functional changes in Duchenne muscular dystrophy: A 12-month longitudinal cohort study von MAZZONE, E, VASCO, G, FROSINI, S, BELLO, L, BONFIGLIO, S, ZUCCHINI, E, DE SANCTIS, R, SCUTIFERO, M, BIANCO, F, ROSSI, F, MOTTA, M. C, SACCO, A, SORMANI, M. P, DONATI, M. A, MONGINI, T, PINI, A, BATTINI, R, PEGORARO, E, PANE, M, GASPERINI, S, PREVITALI, S, NAPOLITANO, S, MARTINELLI, D, TORRENTE, Y, BRUNO, C, VITA, G, COMI, G, BERTINI, E, MERCURI, E, BERARDINELLI, A, MESSINA, S, D'AMICO, A, DOGLIO, L, POLITANO, L, CAVALLARO, F

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Cognitive profile in Duchenne muscular dystrophy boys without intellectual disability: The role of executive functions von Battini, R., Chieffo, D., Bulgheroni, S., Piccini, G., Pecini, C., Lucibello, S., Lenzi, S., Moriconi, F., Pane, M., Astrea, G., Baranello, G., Alfieri, P., Vicari, S., Riva, D., Cioni, G., Mercuri, E.

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Extensive intragenomic variation in the internal transcribed spacer region of fungi von Bradshaw, Michael J., Aime, M. Catherine, Rokas, Antonis, Maust, Autumn, Moparthi, Swarnalatha, Jellings, Keila, Pane, Alexander M., Hendricks, Dylan, Pandey, Binod, Li, Yuanning, Pfister, Donald H.

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The effectiveness of a Lactobacillus probiotic on measures of psychosocial health in adults diagnosed with subthreshold depression: a double-blind, randomised, placebo-controlled t... von Moschonis, G., Sarapis, K., Resciniti, S., Hall, R., Yim, K., Tonkovic, M., Fitzgerald, C., Anixiadis, F., Nhu Dinh, Q., Hale, M., Wright, B., Pane, M., Tuck, C.J., Biesiekierski, J.R.

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A randomized placebo-controlled phase 3 trial of an antisense oligonucleotide, drisapersen, in Duchenne muscular dystrophy von Goemans, Nathalie, Mercuri, Eugenio, Belousova, Elena, Komaki, Hirofumi, Dubrovsky, Alberto, McDonald, Craig M., Kraus, John E., Lourbakos, Afrodite, Lin, Zhengning, Campion, Giles, Wang, Susanne X., Campbell, Craig, Araujo, A., Bertini, E., Born, P., Cances, C., Chabrol, B., Chae, J.-H., Colomer Oferil, J., Comi, G.P., Cuisset, J.-M., D'Anjou, G., Desguerre, I., Erazo Torricelli, R., Escobar, R., Feder, D., Ferlini, A., Giugliani, R., Henricson, E., Herczegfalvi, A., Jong, Y.-J., Kimura, S., Kirschner, J.-B., Kleinsteuber, K., Kostera-Pruszczyk, A., Kudr, M., Mueller-Felber, W., Niks, E.H., Ogata, K., Palermo, C., Pane, M., Pascual, I., Pereon, Y., Raskin, S., Rasmussen, M., Reed, U., Schara, U., Selby, K., Sobreira, C., Takeshima, Y., Vilchez Padilla, J.J., Vita, G., Vondracek, P., Wiegand, G., Wilichowski, E.

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Reliability of the North Star Ambulatory Assessment in a multicentric setting von Mazzone, E.S, Messina, S, Vasco, G, Main, M, Eagle, M, D’Amico, A, Doglio, L, Politano, L, Cavallaro, F, Frosini, S, Bello, L, Magri, F, Corlatti, A, Zucchini, E, Brancalion, B, Rossi, F, Ferretti, M, Motta, M.G, Cecio, M.R, Berardinelli, A, Alfieri, P, Mongini, T, Pini, A, Astrea, G, Battini, R, Comi, G, Pegoraro, E, Morandi, L, Pane, M, Angelini, C, Bruno, C, Villanova, M, Vita, G, Donati, M.A, Bertini, E, Mercuri, E

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The association between short-term temperature variability and mortality in Virginia von Pane, Melanie M, Davis, Robert E

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Factors associated with regular counselling attendance of HIV outpatients of a national referral hospital in Jakarta, Indonesia: a cross sectional study von Pane, M, Sianturi, E I, Kong, Yin Mei Fiona, Bautista, Philip, Herlina, Taxis, K

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Longitudinal data of neuropsychological profile in a cohort of Duchenne muscular dystrophy boys without cognitive impairment von Battini, R, Lenzi, S, Lucibello, S, Chieffo, D, Moriconi, F., Cristofani, P., Bulgheroni, S., Cumbo, F., Pane, M., Baranello, G., Alfieri, P., Astrea, G., Cioni, G., Vicari, S., Mercuri, E.

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Multiple schedules with response interruption and redirection to reduce stereotypy in children with autism spectrum disorder: Generalization and social validity von Callahan, Ashley E., Sidener, Tina M., DeBar, Ruth M., Deshais, Meghan A., Pane, Heather M., Patil, Priya

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Randomized, double-blind, placebo-controlled trial of phenylbutyrate in spinal muscular atrophy von MERCURI, E, BERTINI, E, CINI, C, COLITTO, F, KINALI, M, MINETTI, C, MONGINI, T, MORANDI, L, NERI, G, ORCESI, S, PANE, M, PELLICCIONI, M, MESSINA, S, PINI, A, TIZIANO, F. D, VILLANOVA, M, VITA, G, BRAHE, C, SOLARI, A, D'AMICO, A, ANGELOZZI, C, BATTINI, R, BERARDINELLI, A, BOFFI, P, BRUNO, C

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Development of a patient‐reported outcome measure for upper limb function in Duchenne muscular dystrophy: DMD Upper Limb PROM von Klingels, K, Mayhew, A G, Mazzone, E S, Duong, T, Decostre, V, Werlauff, U, Vroom, E, Mercuri, E, Goemans, N M, Eagle, M, De Groot, I, Main, M, Messina, S, Campion, G, Servais, L, Van den Hauwe, M, Es, E, Pane, M, Buccella, F, Kuijer, J, Ceradini, F, Henricson, E, McDonald, C, Florence, J

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Modification of geometry of airfoil NACA 0018 towards work testing vertical axis wind type Darrieus Eggbeater von Tarihoran, B, Sebayang, M D, Pane, M

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061 - Lymphomatoid papulosis type E with subcutaneous tissue infiltration and prominent rimming von Climent, F., Bosch, J., Penin, R., Kempf, W., Varela, M., Pané, M., Salaverria, I., Muniesa, C., Servitje, O.

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