Uncertainty in an era of transformative therapy for haemophilia: Addressing the unknowns von Pierce, Glenn F.

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AAV5–Factor VIII Gene Transfer in Severe Hemophilia A von Rangarajan, Savita, Walsh, Liron, Lester, Will, Perry, David, Madan, Bella, Laffan, Michael, Yu, Hua, Vettermann, Christian, Pierce, Glenn F, Wong, Wing Y, Pasi, K. John

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Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A von Pasi, K. John, Rangarajan, Savita, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Laffan, Michael, Russell, Chris B, Li, Mingjin, Pierce, Glenn F, Wong, Wing Y

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Ultra-Long factor VIII: a major step forward toward a hemophilia-free mind von Hermans, Cedric, Pierce, Glenn F.

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Second gene therapy for hemophilia B approved: More answers or questions? von Kaczmarek, Radoslaw, Pierce, Glenn F

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Gene Therapy for Hemophilia: Are Expectations Matching Reality? von Pierce, Glenn F.

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Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A von Pasi, K John, Rangarajan, Savita, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Laffan, Michael, Russell, Chris B, Li, Mingjin, Pierce, Glenn F, Wong, Wing Y

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Towards achieving a haemophilia‐free mind von Hermans, Cedric, Pierce, Glenn F.

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The persistent educational digital divide and its impact on societal inequality von Pierce, Glenn L, Cleary, Paul F

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First conditional marketing authorization approval in the European Union for hemophilia “A” gene therapy von VandenDriessche, Thierry, Pipe, Steven W., Pierce, Glenn F., Kaczmarek, Radoslaw

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WFH Guidelines for the Management of Hemophilia, 3rd edition von Srivastava, Alok, Santagostino, Elena, Dougall, Alison, Kitchen, Steve, Sutherland, Megan, Pipe, Steven W., Carcao, Manuel, Mahlangu, Johnny, Ragni, Margaret V., Windyga, Jerzy, Llinás, Adolfo, Goddard, Nicholas J., Mohan, Richa, Poonnoose, Pradeep M., Feldman, Brian M., Lewis, Sandra Zelman, Berg, H. Marijke, Pierce, Glenn F.

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The COVID‐19 pandemic: New global challenges for the haemophilia community von Hermans, Cedric, Weill, Alain, Pierce, Glenn F.

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Two gene therapies for hemophilia available: Now what? von Pierce, Glenn F., Herzog, Roland W.

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The underevaluated impacts of the therapeutic revolution of hemophilia on women and girls von Hermans, Cedric, Krumb, Evelien, Rotellini, Dawn, Pierce, Glenn F.

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Deciphering conundrums of adeno-associated virus liver-directed gene therapy: focus on hemophilia von Pierce, Glenn F., Fong, Sylvia, Long, Brian R., Kaczmarek, Radoslaw

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Interindividual variability in transgene mRNA and protein production following adeno-associated virus gene therapy for hemophilia A von Fong, Sylvia, Yates, Bridget, Sihn, Choong-Ryoul, Mattis, Aras N., Mitchell, Nina, Liu, Su, Russell, Chris B., Kim, Benjamin, Lawal, Adebayo, Rangarajan, Savita, Lester, Will, Bunting, Stuart, Pierce, Glenn F., Pasi, K. John, Wong, Wing Yen

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Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A von Ozelo, Margareth C, Mahlangu, Johnny, Pasi, K. John, Giermasz, Adam, Leavitt, Andrew D, Laffan, Michael, Symington, Emily, Quon, Doris V, Wang, Jiaan-Der, Peerlinck, Kathelijne, Pipe, Steven W, Madan, Bella, Key, Nigel S, Pierce, Glenn F, O’Mahony, Brian, Kaczmarek, Radoslaw, Henshaw, Joshua, Lawal, Adebayo, Jayaram, Kala, Huang, Mei, Yang, Xinqun, Wong, Wing Y, Kim, Benjamin

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Adeno-associated virus and hepatocytes: frenemies? von Pierce, Glenn F.

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Reimbursing the value of gene therapy care in an era of uncertainty von Noone, Declan, Coffin, Donna, Pierce, Glenn F.

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Phase 3 study of recombinant factor VIII Fc fusion protein in severe hemophilia A von Mahlangu, Johnny, Powell, Jerry S., Ragni, Margaret V., Chowdary, Pratima, Josephson, Neil C., Pabinger, Ingrid, Hanabusa, Hideji, Gupta, Naresh, Kulkarni, Roshni, Fogarty, Patrick, Perry, David, Shapiro, Amy, Pasi, K. John, Apte, Shashikant, Nestorov, Ivan, Jiang, Haiyan, Li, Shuanglian, Neelakantan, Srividya, Cristiano, Lynda M., Goyal, Jaya, Sommer, Jurg M., Dumont, Jennifer A., Dodd, Nigel, Nugent, Karen, Vigliani, Gloria, Luk, Alvin, Brennan, Aoife, Pierce, Glenn F.

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