Lentiviral-mediated Gene Therapy for Adults and Children with Severe Pyruvate Kinase Deficiency: Results from an Ongoing Global Phase 1 Study von Shah, Ami J., López Lorenzo, José Luis, Sevilla, Julián, Navarro, Susana, Llanos, Lucía, Pérez de Camino Gaisse, Begoña, Sanchez, Sol, Zubicaray, Josune, Glader, Bert, Chien, May, Quintana Bustamante, Oscar, Zeini, Miriam, Choi, Grace, Nicoletti, Eileen, Rao, Gayatri R., Roncarolo, Maria Grazia, Bueren, Juan A., Schwartz, Jonathan D., Segovia, José C.

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Lentiviral Mediated Gene Therapy for Pyruvate Kinase Deficiency: Interim Results of a Global Phase 1 Study for Adult and Pediatric Patients von Shah, Ami J, López Lorenzo, José Luis, Navarro, Susana, Sevilla, Julián, Llanos, Lucía, Pérez de Camino Gaisse, Begoña, Sanchez, Sol, Glader, Bert, Chien, May, Quintana Bustamante, Oscar, Beard, Brian C, Law, Kenneth M, Zeini, Miriam, Choi, Grace, Nicoletti, Eileen, Rao, Gayatri R, Roncarolo, Maria Grazia, Bueren, Juan A, Schwartz, Jonathan D, Segovia, José C

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Lentiviral Mediated Gene Therapy for Pyruvate Kinase Deficiency: A Global Phase 1 Study for Adult and Pediatric Patients von López Lorenzo, José Luis, Navarro, Susana, Shah, Ami J, Roncarolo, Maria Grazia, Sevilla, Julián, Llanos, Lucía, Pérez Camino de Gaisse, Begoña, Sanchez, Sol, Glader, Bertil, Chien, May, Quintana Bustamante, Oscar, Beard, Brian C, Law, Kenneth M, Zeini, Miriam, Choi, Grace, Nicoletti, Eileen, Bueren, Juan A, Rao, Gayatri R, Schwartz, Jonathan D, Segovia, José C

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293 - Lentiviral-Mediated Gene Therapy for Severe Pyruvate Kinase Deficiency: Results from an Ongoing Global Phase 1 Study von Shah, Ami J, Lorenzo, José Luis López, Sevilla, Julian, Navarro, Susana, Llanos, Lucía, Gaisse, Begoña Perez de Camino, Sánchez, Sol, Zubicaray, Josune, Glader, Bert, Chien, May, Quintana-Bustamante, Oscar, Zeini, Miriam, Choi, Grace, Nicoletti, Eileen, Rao, Gayatri, Roncarolo, Maria Grazia, Bueren, Juan, Schwartz, Jonathan, Segovia, José Carlos

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Lentiviral-Mediated Gene Therapy for Severe Pyruvate Kinase Deficiency: Results from an Ongoing Global Phase 1 Study von Shah, Ami J, Lorenzo, José Luis López, Sevilla, Julian, Navarro, Susana, Llanos, Lucía, Gaisse, Begoña Perez de Camino, Sánchez, Sol, Zubicaray, Josune, Glader, Bert, Chien, May, Quintana-Bustamante, Oscar, Zeini, Miriam, Choi, Grace, Nicoletti, Eileen, Rao, Gayatri, Roncarolo, Maria Grazia, Bueren, Juan, Schwartz, Jonathan, Segovia, José Carlos

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