Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A von Mahlangu, Johnny, Kaczmarek, Radoslaw, von Drygalski, Annette, Shapiro, Susan, Chou, Sheng-Chieh, Ozelo, Margareth C., Kenet, Gili, Peyvandi, Flora, Wang, Michael, Madan, Bella, Key, Nigel S., Laffan, Michael, Dunn, Amy L., Mason, Jane, Quon, Doris V., Symington, Emily, Leavitt, Andrew D., Oldenburg, Johannes, Chambost, Hervé, Reding, Mark T., Jayaram, Kala, Yu, Hua, Mahajan, Reena, Chavele, Konstantia-Maria, Reddy, Divya B., Henshaw, Joshua, Robinson, Tara M., Wong, Wing Yen, Pipe, Steven W.

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Impact of novel hemophilia therapies around the world von Ozelo, Margareth C., Yamaguti‐Hayakawa, Gabriela G.

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Long‐term safety and efficacy of turoctocog alfa in prophylaxis and treatment of bleeding episodes in severe haemophilia A: Final results from the guardian 2 extension trial von Lentz, Steven R., Janic, Dragana, Kavakli, Kaan, Miljic, Predrag, Oldenburg, Johannes, C. Ozelo, Margareth, Santagostino, Elena, Suzuki, Takashi, Zupancic Šalek, Silva, Korsholm, Lars, Matytsina, Irina, Tiede, Andreas

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Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response von High, Katherine A, Manno, Catherine S, Pierce, Glenn F, Arruda, Valder R, Glader, Bertil, Ragni, Margaret, Rasko, John J E, Ozelo, Margareth C, Hoots, Keith, Blatt, Philip, Konkle, Barbara, Dake, Michael, Kaye, Robin, Razavi, Mahmood, Zajko, Albert, Zehnder, James, Rustagi, Pradip, Nakai, Hiroyuki, Chew, Amy, Leonard, Debra, Wright, J Fraser, Lessard, Ruth R, Sommer, Jürg M, Tigges, Michael, Sabatino, Denise, Luk, Alvin, Jiang, Haiyan, Mingozzi, Federico, Couto, Linda, Ertl, Hildegund C, Kay, Mark A

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Eradication of neutralizing antibodies to factor VIII in canine hemophilia A after liver gene therapy von Finn, Jonathan D., Ozelo, Margareth C., Sabatino, Denise E., Franck, Helen W.G., Merricks, Elizabeth P., Crudele, Julie M., Zhou, Shangzhen, Kazazian, Haig H., Lillicrap, David, Nichols, Timothy C., Arruda, Valder R.

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Immunogenicity of Current and New Therapies for Hemophilia A von Prezotti, Alessandra N. L, Frade-Guanaes, Jéssica O, Yamaguti-Hayakawa, Gabriela G, Ozelo, Margareth C

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The effectiveness and safety of octocog alfa in patients with hemophilia A: up to 7-year follow-up of the real-world AHEAD international study von Ozelo, Margareth C, Hermans, Cedric, Carcao, Manuel, Guillet, Benoît, Gu, Joan, Guerra, Randy, Tang, Leilei, Khair, Kate

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First hemophilia B gene therapy approved: More than two decades in the making von Herzog, Roland W., VandenDriessche, Thierry, Ozelo, Margareth C.

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International consensus recommendations on the management of people with haemophilia B von Hart, Daniel P., Matino, Davide, Astermark, Jan, Dolan, Gerard, d’Oiron, Roseline, Hermans, Cédric, Jiménez-Yuste, Victor, Linares, Adriana, Matsushita, Tadashi, McRae, Simon, Ozelo, Margareth C., Platton, Sean, Stafford, Darrel, Sidonio, Robert F., Tiede, Andreas

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Omental implantation of BOECs in hemophilia dogs results in circulating FVIII antigen and a complex immune response von Ozelo, Margareth C., Vidal, Barbara, Brown, Christine, Notley, Colleen, Hegadorn, Carol, Webster, Sandra, Harpell, Lori, Ahlin, James, Winterborn, Andrew, Handforth, Janine, Arruda, Valder R., Hough, Christine, Lillicrap, David

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Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A von Ozelo, Margareth C, Mahlangu, Johnny, Pasi, K. John, Giermasz, Adam, Leavitt, Andrew D, Laffan, Michael, Symington, Emily, Quon, Doris V, Wang, Jiaan-Der, Peerlinck, Kathelijne, Pipe, Steven W, Madan, Bella, Key, Nigel S, Pierce, Glenn F, O’Mahony, Brian, Kaczmarek, Radoslaw, Henshaw, Joshua, Lawal, Adebayo, Jayaram, Kala, Huang, Mei, Yang, Xinqun, Wong, Wing Y, Kim, Benjamin

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Knee radiosynovectomy with 153Sm-hydroxyapatite compared to 90Y-hydroxyapatite: initial results of a prospective trial von Santos, Allan O., Ricciardi, Janaina B. S., Pagnano, Rodrigo, Pereira, Luis Fernando M., Sakuma, Emerson T., Matsuda, Margareth M. N., Bernardes, Emerson S., Araújo, Elaine B., Brunetto, Sérgio Q., Takahashi, Maria Emília S., Brunetto, Edna M., Zulli, Roberto, Ozelo, Margareth C., Etchebehere, Elba C. S. C.

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Breaking ground in haemophilia B gene therapy: insights from the HOPE-B trial and beyond von Ozelo, Margareth C

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Current and emerging gene therapies for haemophilia A and B von Kaczmarek, Radoslaw, Miesbach, Wolfgang, Ozelo, Margareth C., Chowdary, Pratima

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Gene Therapy for Hemophilia A. Reply von Ozelo, Margareth C, Wong, Wing Y

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Gene therapy for hemophilia: looking beyond factor expression von Yamaguti-Hayakawa, Gabriela G, Ozelo, Margareth C

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Angiogenesis-Related Genes in Endothelial Progenitor Cells May Be Involved in Sickle Cell Stroke von Ito, Mirta T., da Silva Costa, Sueli M., Baptista, Leticia C., Carvalho-Siqueira, Gabriela Q., Albuquerque, Dulcineia M., Rios, Vinicius M., Ospina-Prieto, Stephanie, Saez, Roberta C., Vieira, Karla P., Cendes, Fernando, Ozelo, Margareth C., Saad, Sara Teresinha O., Costa, Fernando F., Melo, Monica B.

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Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A von Klamroth, Robert, Hayes, Gregory, Andreeva, Tatiana, Gregg, Keith, Suzuki, Takashi, Mitha, Ismail Haroon, Hardesty, Brandon, Shima, Midori, Pollock, Toni, Slev, Patricia, Oldenburg, Johannes, Ozelo, Margareth C, Stieltjes, Natalie, Castet, Sabine-Marie, Mahlangu, Johnny, Peyvandi, Flora, Kazmi, Rashid, Schved, Jean-François, Leavitt, Andrew D, Callaghan, Michael, Pan-Petesch, Brigitte, Quon, Doris V, Andrews, Jayson, Trinh, Alex, Li, Mingjin, Wong, Wing Yen

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First study of extended half-life rFVIIIFc in previously untreated patients with hemophilia A: PUPs A-LONG final results von Königs, Christoph, Ozelo, Margareth C, Dunn, Amy, Kulkarni, Roshni, Nolan, Beatrice, Brown, Simon A, Schiavulli, Michele, Gunawardena, Sriya, Mukhopadhyay, Sutirtha, Jayawardene, Deepthi, Winding, Bent, Carcao, Manuel

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Haemophilia gene therapy—Update on new country initiatives von Reiss, Ulrike M., Mahlangu, Johnny, Ohmori, Tsukasa, Ozelo, Margareth C., Srivastava, Alok, Zhang, Lei

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