High-efficiency transgene integration by homology-directed repair in human primary cells using DNA-PKcs inhibition von Selvaraj, Sridhar, Feist, William N., Viel, Sebastien, Vaidyanathan, Sriram, Dudek, Amanda M., Gastou, Marc, Rockwood, Sarah J., Ekman, Freja K., Oseghale, Aluya R., Xu, Liwen, Pavel-Dinu, Mara, Luna, Sofia E., Cromer, M. Kyle, Sayana, Ruhi, Gomez-Ospina, Natalia, Porteus, Matthew H.

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Mechanisms of NRF2 activation to mediate fetal hemoglobin induction and protection against oxidative stress in sickle cell disease von Zhu, Xingguo, Oseghale, Aluya R, Nicole, Lopez H, Li, Biaoru, Pace, Betty S

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Conjugate prodrug AN-233 induces fetal hemoglobin expression in sickle erythroid progenitors and β-YAC transgenic mice von Oseghale, Aluya R., Zhu, Xingguo, Li, Biaoru, Peterson, Kenneth R., Nudelman, Abraham, Rephaeli, Ada, Xu, Hongyan, Pace, Betty S.

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Novel Conjugates of Butyrate and δ-Aminolevulinate Increase γ-Globin Gene Expression and Fetal Hemoglobin Synthesis in Erythroid Progenitors von Oseghale, Aluya R., Johnson, Marjorie M., Zhu, Xingguo, Nudelman, Abraham, Rephaeli, Ada, Pace, Betty S.

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