Profound phenotypic and epigenetic heterogeneity of the HIV-1-infected CD4+ T cell reservoir von Wu, Vincent H., Nordin, Jayme M. L., Nguyen, Son, Joy, Jaimy, Mampe, Felicity, del Rio Estrada, Perla M., Torres-Ruiz, Fernanda, González-Navarro, Mauricio, Luna-Villalobos, Yara Andrea, Ávila-Ríos, Santiago, Reyes-Terán, Gustavo, Tebas, Pablo, Montaner, Luis J., Bar, Katharine J., Vella, Laura A., Betts, Michael R.

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AAV8 Gene Therapy Rescues the Newborn Phenotype of a Mouse Model of Crigler-Najjar von Greig, Jenny A, Nordin, Jayme M L, Draper, Christine, Bell, Peter, Wilson, James M

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A Gene Therapy Approach to Improve Copper Metabolism and Prevent Liver Damage in a Mouse Model of Wilson Disease von Greig, Jenny A, Nordin, Jayme M L, Smith, Melanie K, Ashley, Scott N, Draper, Christine, Zhu, Yanqing, Bell, Peter, Buza, Elizabeth L, Wilson, James M

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AAV8 Gene Therapy for Crigler-Najjar Syndrome in Macaques Elicited Transgene T Cell Responses That Are Resident to the Liver von Greig, Jenny A, Calcedo, Roberto, Kuri-Cervantes, Leticia, Nordin, Jayme M L, Albrecht, Jessica, Bote, Erin, Goode, Tamara, Chroscinski, Edward A, Bell, Peter, Richman, Laura K, Betts, Michael R, Wilson, James M

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Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Crigler-Najjar Syndrome von Greig, Jenny A., Nordin, Jayme M.L., Draper, Christine, McMenamin, Deirdre, Chroscinski, Edward A., Bell, Peter, Gray, John T., Richman, Laura K., Wilson, James M.

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Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates von Costa-Verdera, Helena, Collaud, Fanny, Riling, Christopher R., Sellier, Pauline, Nordin, Jayme M. L., Preston, G. Michael, Cagin, Umut, Fabregue, Julien, Barral, Simon, Moya-Nilges, Maryse, Krijnse-Locker, Jacomina, van Wittenberghe, Laetitia, Daniele, Natalie, Gjata, Bernard, Cosette, Jeremie, Abad, Catalina, Simon-Sola, Marcelo, Charles, Severine, Li, Mathew, Crosariol, Marco, Antrilli, Tom, Quinn, William J., Gross, David A., Boyer, Olivier, Anguela, Xavier M., Armour, Sean M., Colella, Pasqualina, Ronzitti, Giuseppe, Mingozzi, Federico

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Optimized Adeno-Associated Viral-Mediated Human Factor VIII Gene Therapy in Cynomolgus Macaques von Greig, Jenny A, Nordin, Jayme M L, White, John W, Wang, Qiang, Bote, Erin, Goode, Tamara, Calcedo, Roberto, Wadsworth, Samuel, Wang, Lili, Wilson, James M

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Determining the Minimally Effective Dose of a Clinical Candidate Adeno-Associated Virus Vector in a Mouse Model of Hemophilia A von Greig, Jenny A, Smith, Melanie K, Nordin, Jayme M L, Goode, Tamara, Chroscinski, Edward A, Buza, Elizabeth L, Schmidt, Nicole, Kattenhorn, Lisa M, Wadsworth, Samuel, Wilson, James M

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Adeno-associated viral gene therapy corrects a mouse model of argininosuccinic aciduria von Ashley, Scott N., Nordin, Jayme M.L., Buza, Elizabeth L., Greig, Jenny A., Wilson, James M.

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Impact of intravenous infusion time on AAV8 vector pharmacokinetics, safety, and liver transduction in cynomolgus macaques von Greig, Jenny A, Nordin, Jayme Ml, Bote, Erin, Makaron, Leah, Garnett, Mason E, Kattenhorn, Lisa M, Bell, Peter, Goode, Tamara, Wilson, James M

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