Cas-Clover Editing Efficiency and Off-Target Activity in Human Hepatocytes at the KLKB1 Locus von Alvarez, Oscar, Homa, Lucas, Kearney, Stephanie, Hajj, Khal, Ma, Zhibo, Negron, Cindy, Briseno, Kevin, Nitzahn, Matt, Oglesby, Nygel, Barajas-Mora, Mauricio, Barcenas, Arturo, Kubicki, Joseph, Davis, Alicia, Connerney, Mona, Battiprolu, Pavan, Bennett, Michael, Jacques, Bonnie, Rychak, Joshua, Warner, Brent, Madison, Blair

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Conditional disruption of hepatic carbamoyl phosphate synthetase 1 in mice results in hyperammonemia without orotic aciduria and can be corrected by liver-directed gene therapy von Khoja, Suhail, Nitzahn, Matt, Hermann, Kip, Truong, Brian, Borzone, Roberta, Willis, Brandon, Rudd, Mitchell, Palmer, Donna J., Ng, Philip, Brunetti-Pierri, Nicola, Lipshutz, Gerald S.

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