Steroid treatment response to post SARS-CoV-2 PANS symptoms: Case series von Berloffa, Stefano, Salvati, Andrea, Pantalone, Gloria, Falcioni, Ludovica, Rizzi, Micaela M, Naldini, Francesca, Masi, Gabriele, Gagliano, Antonella

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Corrigendum: Steroid treatment response to post SARS-CoV-2 PANS symptoms: Case series von Berloffa, Stefano, Salvati, Andrea, Pantalone, Gloria, Falcioni, Ludovica, Rizzi, Micaela M, Naldini, Francesca, Masi, Gabriele, Gagliano, Antonella

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A systematic review and meta-analysis of gene therapy with hematopoietic stem and progenitor cells for monogenic disorders von Tucci, Francesca, Galimberti, Stefania, Naldini, Luigi, Valsecchi, Maria Grazia, Aiuti, Alessandro

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Ensuring a future for gene therapy for rare diseases von Aiuti, Alessandro, Pasinelli, Francesca, Naldini, Luigi

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Cellular and transcriptional dynamics of human neutrophils at steady state and upon stress von Montaldo, Elisa, Lusito, Eleonora, Bianchessi, Valentina, Caronni, Nicoletta, Scala, Serena, Basso-Ricci, Luca, Cantaffa, Carla, Masserdotti, Alice, Barilaro, Mattia, Barresi, Simona, Genua, Marco, Vittoria, Francesco Maria, Barbiera, Giulia, Lazarevic, Dejan, Messina, Carlo, Xue, Elisabetta, Marktel, Sarah, Tresoldi, Cristina, Milani, Raffaella, Ronchi, Paola, Gattillo, Salvatore, Santoleri, Luca, Di Micco, Raffaella, Ditadi, Andrea, Belfiori, Giulio, Aleotti, Francesca, Naldini, Matteo Maria, Gentner, Bernhard, Gardiman, Elisa, Tamassia, Nicola, Cassatella, Marco Antonio, Hidalgo, Andrés, Kwok, Immanuel, Ng, Lai Guan, Crippa, Stefano, Falconi, Massimo, Pettinella, Francesca, Scapini, Patrizia, Naldini, Luigi, Ciceri, Fabio, Aiuti, Alessandro, Ostuni, Renato

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In Vivo Tracking of Human Hematopoiesis Reveals Patterns of Clonal Dynamics during Early and Steady-State Reconstitution Phases von Biasco, Luca, Pellin, Danilo, Scala, Serena, Dionisio, Francesca, Basso-Ricci, Luca, Leonardelli, Lorena, Scaramuzza, Samantha, Baricordi, Cristina, Ferrua, Francesca, Cicalese, Maria Pia, Giannelli, Stefania, Neduva, Victor, Dow, David J., Schmidt, Manfred, Von Kalle, Christof, Roncarolo, Maria Grazia, Ciceri, Fabio, Vicard, Paola, Wit, Ernst, Di Serio, Clelia, Naldini, Luigi, Aiuti, Alessandro

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Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome von Aiuti, Alessandro, Biasco, Luca, Scaramuzza, Samantha, Ferrua, Francesca, Cicalese, Maria Pia, Baricordi, Cristina, Dionisio, Francesca, Calabria, Andrea, Giannelli, Stefania, Castiello, Maria Carmina, Bosticardo, Marita, Evangelio, Costanza, Assanelli, Andrea, Casiraghi, Miriam, Di Nunzio, Sara, Callegaro, Luciano, Benati, Claudia, Rizzardi, Paolo, Pellin, Danilo, Di Serio, Clelia, Schmidt, Manfred, Von Kalle, Christof, Gardner, Jason, Mehta, Nalini, Neduva, Victor, Dow, David J., Galy, Anne, Miniero, Roberto, Finocchi, Andrea, Metin, Ayse, Banerjee, Pinaki P., Orange, Jordan S., Galimberti, Stefania, Valsecchi, Maria Grazia, Biffi, Alessandra, Montini, Eugenio, Villa, Anna, Ciceri, Fabio, Roncarolo, Maria Grazia, Naldini, Luigi

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Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded acc... von Fumagalli, Francesca, Calbi, Valeria, Natali Sora, Maria Grazia, Sessa, Maria, Baldoli, Cristina, Rancoita, Paola Maria V, Ciotti, Francesca, Sarzana, Marina, Fraschini, Maddalena, Zambon, Alberto Andrea, Acquati, Serena, Redaelli, Daniela, Attanasio, Vanessa, Miglietta, Simona, De Mattia, Fabiola, Barzaghi, Federica, Ferrua, Francesca, Migliavacca, Maddalena, Tucci, Francesca, Gallo, Vera, Del Carro, Ubaldo, Canale, Sabrina, Spiga, Ivana, Lorioli, Laura, Recupero, Salvatore, Fratini, Elena Sophia, Morena, Francesco, Silvani, Paolo, Calvi, Maria Rosa, Facchini, Marcella, Locatelli, Sara, Corti, Ambra, Zancan, Stefano, Antonioli, Gigliola, Farinelli, Giada, Gabaldo, Michela, Garcia-Segovia, Jesus, Schwab, Laetitia C, Downey, Gerald F, Filippi, Massimo, Cicalese, Maria Pia, Martino, Sabata, Di Serio, Clelia, Ciceri, Fabio, Bernardo, Maria Ester, Naldini, Luigi, Biffi, Alessandra, Aiuti, Alessandro

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The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy von Montini, Eugenio, Cesana, Daniela, Schmidt, Manfred, Sanvito, Francesca, Bartholomae, Cynthia C, Ranzani, Marco, Benedicenti, Fabrizio, Sergi, Lucia Sergi, Ambrosi, Alessandro, Ponzoni, Maurilio, Doglioni, Claudio, Di Serio, Clelia, von Kalle, Christof, Naldini, Luigi

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Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy von Jofra Hernández, Raisa, Calabria, Andrea, Sanvito, Francesca, De Mattia, Fabiola, Farinelli, Giada, Scala, Serena, Visigalli, Ilaria, Carriglio, Nicola, De Simone, Maura, Vezzoli, Michela, Cecere, Francesca, Migliavacca, Maddalena, Basso-Ricci, Luca, Omrani, Maryam, Benedicenti, Fabrizio, Norata, Rossana, Rancoita, Paola Maria Vittoria, Di Serio, Clelia, Albertini, Paola, Cristofori, Patrizia, Naldini, Luigi, Gentner, Bernhard, Montini, Eugenio, Aiuti, Alessandro, Mortellaro, Alessandra

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Longitudinal single-cell profiling of chemotherapy response in acute myeloid leukemia von Naldini, Matteo Maria, Casirati, Gabriele, Barcella, Matteo, Rancoita, Paola Maria Vittoria, Cosentino, Andrea, Caserta, Carolina, Pavesi, Francesca, Zonari, Erika, Desantis, Giacomo, Gilioli, Diego, Carrabba, Matteo Giovanni, Vago, Luca, Bernardi, Massimo, Di Micco, Raffaella, Di Serio, Clelia, Merelli, Ivan, Volpin, Monica, Montini, Eugenio, Ciceri, Fabio, Gentner, Bernhard

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Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model von Visigalli, Ilaria, Delai, Stefania, Politi, Letterio S., Di Domenico, Carmela, Cerri, Federica, Mrak, Emanuela, D'Isa, Raffaele, Ungaro, Daniela, Stok, Merel, Sanvito, Francesca, Mariani, Elisabetta, Staszewsky, Lidia, Godi, Claudia, Russo, Ilaria, Cecere, Francesca, del Carro, Ubaldo, Rubinacci, Alessandro, Brambilla, Riccardo, Quattrini, Angelo, Di Natale, Paola, Ponder, Katherine, Naldini, Luigi, Biffi, Alessandra

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Uncovering and Dissecting the Genotoxicity of Self-inactivating Lentiviral Vectors In Vivo von Cesana, Daniela, Ranzani, Marco, Volpin, Monica, Bartholomae, Cynthia, Duros, Caroline, Artus, Alexandre, Merella, Stefania, Benedicenti, Fabrizio, Sergi Sergi, Lucia, Sanvito, Francesca, Brombin, Chiara, Nonis, Alessandro, Serio, Clelia Di, Doglioni, Claudio, von Kalle, Christof, Schmidt, Manfred, Cohen-Haguenauer, Odile, Naldini, Luigi, Montini, Eugenio

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miR-142-3p Prevents Macrophage Differentiation during Cancer-Induced Myelopoiesis von Sonda, Nada, Simonato, Francesca, Peranzoni, Elisa, Calì, Bianca, Bortoluzzi, Stefania, Bisognin, Andrea, Wang, Ena, Marincola, Francesco M., Naldini, Luigi, Gentner, Bernhard, Trautwein, Christian, Sackett, Sara Dutton, Zanovello, Paola, Molon, Barbara, Bronte, Vincenzo

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Long-term lineage commitment in haematopoietic stem cell gene therapy von Calabria, Andrea, Spinozzi, Giulio, Cesana, Daniela, Buscaroli, Elena, Benedicenti, Fabrizio, Pais, Giulia, Gazzo, Francesco, Scala, Serena, Lidonnici, Maria Rosa, Scaramuzza, Samantha, Albertini, Alessandra, Esposito, Simona, Tucci, Francesca, Canarutto, Daniele, Omrani, Maryam, De Mattia, Fabiola, Dionisio, Francesca, Giannelli, Stefania, Marktel, Sarah, Fumagalli, Francesca, Calbi, Valeria, Cenciarelli, Sabina, Ferrua, Francesca, Gentner, Bernhard, Caravagna, Giulio, Ciceri, Fabio, Naldini, Luigi, Ferrari, Giuliana, Aiuti, Alessandro, Montini, Eugenio

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Long-term lineage commitment in hematopoietic stem cell gene therapy von Calabria, Andrea, Spinozzi, Giulio, Cesana, Daniela, Buscaroli, Elena, Benedicenti, Fabrizio, Pais, Giulia, Gazzo, Francesco, Scala, Serena, Lidonnici, Maria Rosa, Scaramuzza, Samantha, Albertini, Alessandra, Esposito, Simona, Tucci, Francesca, Canarutto, Daniele, Omrani, Maryam, De Mattia, Fabiola, Dionisio, Francesca, Giannelli, Stefania, Marktel, Sarah, Fumagalli, Francesca, Calbi, Valeria, Cenciarelli, Sabina, Ferrua, Francesca, Gentner, Bernhard, Caravagna, Giulio, Ciceri, Fabio, Naldini, Luigi, Ferrari, Giuliana, Aiuti, Alessandro, Montini, Eugenio

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Promoter trapping reveals significant differences in integration site selection between MLV and HIV vectors in primary hematopoietic cells von De Palma, Michele, Montini, Eugenio, de Sio, Francesca R.Santoni, Benedicenti, Fabrizio, Gentile, Alessandra, Medico, Enzo, Naldini, Luigi

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Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy von Biffi, Alessandra, Montini, Eugenio, Lorioli, Laura, Cesani, Martina, Fumagalli, Francesca, Plati, Tiziana, Baldoli, Cristina, Martino, Sabata, Calabria, Andrea, Canale, Sabrina, Benedicenti, Fabrizio, Vallanti, Giuliana, Biasco, Luca, Leo, Simone, Kabbara, Nabil, Zanetti, Gianluigi, Rizzo, William B., Mehta, Nalini A. L., Cicalese, Maria Pia, Casiraghi, Miriam, Boelens, Jaap J., Del Carro, Ubaldo, Dow, David J., Schmidt, Manfred, Assanelli, Andrea, Neduva, Victor, Di Serio, Clelia, Stupka, Elia, Gardner, Jason, von Kalle, Christof, Bordignon, Claudio, Ciceri, Fabio, Rovelli, Attilio, Roncarolo, Maria Grazia, Aiuti, Alessandro, Sessa, Maria, Naldini, Luigi

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Retrieval of vector integration sites from cell-free DNA von Cesana, Daniela, Calabria, Andrea, Rudilosso, Laura, Gallina, Pierangela, Benedicenti, Fabrizio, Spinozzi, Giulio, Schiroli, Giulia, Magnani, Alessandra, Acquati, Serena, Fumagalli, Francesca, Calbi, Valeria, Witzel, Maximilian, Bushman, Frederic D., Cantore, Alessio, Genovese, Pietro, Klein, Christoph, Fischer, Alain, Cavazzana, Marina, Six, Emmanuelle, Aiuti, Alessandro, Naldini, Luigi, Montini, Eugenio

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Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome von Vavassori, Valentina, Mercuri, Elisabetta, Marcovecchio, Genni E, Castiello, Maria C, Schiroli, Giulia, Albano, Luisa, Margulies, Carrie, Buquicchio, Frank, Fontana, Elena, Beretta, Stefano, Merelli, Ivan, Cappelleri, Andrea, Rancoita, Paola MV, Lougaris, Vassilios, Plebani, Alessandro, Kanariou, Maria, Lankester, Arjan, Ferrua, Francesca, Scanziani, Eugenio, Cotta‐Ramusino, Cecilia, Villa, Anna, Naldini, Luigi, Genovese, Pietro

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