Gene Therapy in Patients with the Crigler–Najjar Syndrome von D’Antiga, Lorenzo, Beuers, Ulrich, Ronzitti, Giuseppe, Brunetti-Pierri, Nicola, Baumann, Ulrich, Di Giorgio, Angelo, Aronson, Sem, Hubert, Aurelie, Romano, Roberta, Junge, Norman, Bosma, Piter, Bortolussi, Giulia, Muro, Andrés F., Soumoudronga, Ravaka F., Veron, Philippe, Collaud, Fanny, Knuchel-Legendre, Nathalie, Labrune, Philippe, Mingozzi, Federico

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Marine litter in coral reef areas along the Jordan Gulf of Aqaba, Red Sea von Hilal, Ahmad Abu, Najjar, T Al

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Reply to Najjar, R.S. Comment on "Dyńka et al. The Ketogenic Diet and Cardiovascular Diseases. Nutrients 2023, 15 , 3368" von Dyńka, Damian, Kowalcze, Katarzyna, Charuta, Anna, Paziewska, Agnieszka

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Therapeutic Options for Crigler-Najjar Syndrome: A Scoping Review von Sambati, Vanessa, Laudisio, Serena, Motta, Matteo, Esposito, Susanna

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Crigler‐Najjar Syndrome Type 1: Pathophysiology, Natural History, and Therapeutic Frontier von Strauss, Kevin A., Ahlfors, Charles E., Soltys, Kyle, Mazareigos, George V., Young, Millie, Bowser, Lauren E., Fox, Michael D., Squires, James E., McKiernan, Patrick, Brigatti, Karlla W., Puffenberger, Erik G., Carson, Vincent J., Vreman, Hendrik J.

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Razan Ashraf al-Najjar von Barghouti, Mustafa

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Disease burden of Crigler–Najjar syndrome: Systematic review and future perspectives von Dhawan, Anil, Lawlor, Michael W, Mazariegos, George V, McKiernan, Patrick, Squires, James E, Strauss, Kevin A, Gupta, Digant, James, Emma, Prasad, Suyash

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Hepatic Parenchymal Injury in Crigler‐Najjar Type I von Mitchell, Ellen, Ranganathan, Sarangarajan, McKiernan, Patrick, Squires, Robert H., Strauss, Kevin, Soltys, Kyle, Mazariegos, George, Squires, James E.

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Disease burden and management of Crigler‐Najjar syndrome: Report of a world registry von Aronson, Sem J., Junge, Norman, Trabelsi, Mediha, Kelmemi, Wided, Hubert, Aurelie, Brigatti, Karlla W., Fox, Michael D., Knegt, Robert J., Escher, Johanna C., Ginocchio, Virginia M., Iorio, Raffaele, Zhu, Yan, Özçay, Figen, Rahim, Fakher, El‐Shabrawi, Mortada H.F., Shteyer, Eyal, Di Giorgio, Angelo, D'Antiga, Lorenzo, Mingozzi, Federico, Brunetti‐Pierri, Nicola, Strauss, Kevin A., Labrune, Philippe, Mrad, Ridha, Baumann, Ulrich, Beuers, Ulrich, Bosma, Piter J.

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Promoterless gene targeting without nucleases rescues lethality of a Crigler‐Najjar syndrome mouse model von Porro, Fabiola, Bortolussi, Giulia, Barzel, Adi, De Caneva, Alessia, Iaconcig, Alessandra, Vodret, Simone, Zentilin, Lorena, Kay, Mark A, Muro, Andrés F

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Hydrogen safety: The road toward green technology von Najjar, Yousef S.H.

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Prevalence and Relevance of Pre-Existing Anti-Adeno-Associated Virus Immunity in the Context of Gene Therapy for Crigler-Najjar Syndrome von Aronson, Sem J, Veron, Philippe, Collaud, Fanny, Hubert, Aurélie, Delahais, Virginie, Honnet, Géraldine, de Knegt, Robert J, Junge, Norman, Baumann, Ulrich, Di Giorgio, Angelo, D'Antiga, Lorenzo, Ginocchio, Virginia M, Brunetti-Pierri, Nicola, Labrune, Philippe, Beuers, Ulrich, Bosma, Piter J, Mingozzi, Federico

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Paternal uniparental disomy of chromosome 2 resulting in a concurrent presentation of Crigler–Najjar syndrome type I and long‐chain 3‐hydroxyacyl‐CoA dehydrogenase deficiency von Knapp, Anna, Jagła, Mateusz, Madetko‐Talowska, Anna, Szewczyk, Katarzyna, Książek, Teofila, Końska, Katarzyna, Kwinta, Przemko

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Behavioral and neurocognitive phenotypes in Crigler-Najjar syndrome in Tunisia von N Bouayed Abdelmoula, Zekri, R, Bouaziz, F, Bensalem, K, Feki, M, Etteyeb, A, Abdelmoula, B

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AAV8 Gene Therapy Rescues the Newborn Phenotype of a Mouse Model of Crigler-Najjar von Greig, Jenny A, Nordin, Jayme M L, Draper, Christine, Bell, Peter, Wilson, James M

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Liver cell transplantation for Crigler-Najjar syndrome type Ⅰ： Update and perspectives von Lysy, Philippe-A, Najimi, Mustapha, Stephenne, Xavier, Bourgois, Annick, Smets, Francoise, Sokal, Etienne-M

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Genotype of UGT1A1 and phenotype correlation between Crigler-Najjar syndrome type II and Gilbert syndrome von Maruo, Yoshihiro, Nakahara, Sayuri, Yanagi, Takahide, Nomura, Akitaka, Mimura, Yu, Matsui, Katsuyuki, Sato, Hiroshi, Takeuchi, Yoshihiro

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A novel heterozygous mutation in desmoplakin gene in a Lebanese patient with Carvajal syndrome and tooth agenesis von Bitar, F., Najjar, T., Hayashi, R., Nemer, G., Shigehara, Y., Hamie, L., Abbas, O., Kibbi, A.G., Shimomura, Y., Kurban, M.

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Kernicterus caused by a rare genetic variant of Crigler-Najjar Syndrome (c.826G>C) von Agarwal, Saurabh, UK, Kandha Kumar, Parameswaran, Arun Sree, Saini, Lokesh, Singh, Kuldeep

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De Novo Donor‐Specific HLA Antibody Formation in Two Patients With Crigler‐Najjar Syndrome Type I Following Human Hepatocyte Transplantation With Partial Hepatectomy Preconditioning von Jorns, C., Nowak, G., Nemeth, A., Zemack, H., Mörk, L.‐M., Johansson, H., Gramignoli, R., Watanabe, M., Karadagi, A., Alheim, M., Hauzenberger, D., Dijk, R., Bosma, P. J., Ebbesen, F., Szakos, A., Fischler, B., Strom, S., Ellis, E., Ericzon, B.‐G.

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