Design and Analysis of Effects of Triplet Repeat Oligonucleotides in Cell Models for Myotonic Dystrophy von González-Barriga, Anchel, Mulders, Susan AM, van de Giessen, Jeroen, Hooijer, Jeroen D, Bijl, Suzanne, van Kessel, Ingeborg DG, van Beers, Josee, van Deutekom, Judith CT, Fransen, Jack AM, Wieringa, Bé, Wansink, Derick G

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Triplet-repeat oligonucleotide-mediated reversal of RNA toxicity in myotonic dystrophy von Mulders, Susan A.M, van den Broek, Walther J.A.A, Wheeler, Thurman M, Croes, Huib J.E, van Kuik-Romeijn, Petra, de Kimpe, Sjef J, Furling, Denis, Platenburg, Gerard J, Gourdon, Geneviève, Thornton, Charles A, Wieringa, Bé, Wansink, Derick G

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Targeting several CAG expansion diseases by a single antisense oligonucleotide von Evers, Melvin M, Pepers, Barry A, van Deutekom, Judith C T, Mulders, Susan A M, den Dunnen, Johan T, Aartsma-Rus, Annemieke, van Ommen, Gert-Jan B, van Roon-Mom, Willeke M C

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Intracellular Distribution and Nuclear Activity of Antisense Oligonucleotides After Unassisted Uptake in Myoblasts and Differentiated Myotubes In Vitro von González-Barriga, Anchel, Nillessen, Bram, Kranzen, Julia, van Kessel, Ingeborg D.G., Croes, Huib J.E., Aguilera, Begoña, de Visser, Peter C., Datson, Nicole A., Mulders, Susan A.M., van Deutekom, Judith C.T., Wieringa, Bé, Wansink, Derick G.

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