Evaluation of neuroretina following i.v. or intra‐CSF AAV9 gene replacement in mice with MPS IIIA, a childhood dementia von Beard, Helen, Winner, Leanne, Shoubridge, Andrew, Parkinson‐Lawrence, Emma, Lau, Adeline A., Mubarokah, Siti N., Lance, Tabitha‐Rose, King, Barbara, Scott, William, Snel, Marten F., Trim, Paul J., Hemsley, Kim M.

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