Lentiviral Gene Therapy for Artemis-Deficient SCID von Cowan, Morton J., Yu, Jason, Facchino, Janelle, Fraser-Browne, Carol, Sanford, Ukina, Kawahara, Misako, Dara, Jasmeen, Long-Boyle, Janel, Oh, Jess, Chan, Wendy, Chag, Shivali, Broderick, Lori, Chellapandian, Deepak, Decaluwe, Hélène, Golski, Catherine, Hu, Diana, Kuo, Caroline Y., Miller, Holly K., Petrovic, Aleksandra, Currier, Robert, Hilton, Joan F., Punwani, Divya, Dvorak, Christopher C., Malech, Harry L., McIvor, R. Scott, Puck, Jennifer M.

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Severe eczema in Wiskott–Aldrich syndrome‐related disorder successfully treated with dupilumab von Alzahrani, Fatmah, Miller, Holly K., Sacco, Keith, Dupuy, Elizabeth

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Excellent outcomes following hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report von Burroughs, Lauri M., Petrovic, Aleksandra, Brazauskas, Ruta, Liu, Xuerong, Griffith, Linda M., Ochs, Hans D., Bleesing, Jack J., Edwards, Stephanie, Dvorak, Christopher C., Chaudhury, Sonali, Prockop, Susan E., Quinones, Ralph, Goldman, Frederick D., Quigg, Troy C., Chandrakasan, Shanmuganathan, Smith, Angela R., Parikh, Suhag, Dávila Saldaña, Blachy J., Thakar, Monica S., Phelan, Rachel, Shenoy, Shalini, Forbes, Lisa R., Martinez, Caridad, Chellapandian, Deepak, Shereck, Evan, Miller, Holly K., Kapoor, Neena, Barnum, Jessie L., Chong, Hey, Shyr, David C., Chen, Karin, Abu-Arja, Rolla, Shah, Ami J., Weinacht, Katja G., Moore, Theodore B., Joshi, Avni, DeSantes, Kenneth B., Gillio, Alfred P., Cuvelier, Geoffrey D.E., Keller, Michael D., Rozmus, Jacob, Torgerson, Troy, Pulsipher, Michael A., Haddad, Elie, Sullivan, Kathleen E., Logan, Brent R., Kohn, Donald B., Puck, Jennifer M., Notarangelo, Luigi D., Pai, Sung-Yun, Rawlings, David J., Cowan, Morton J.

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The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions von Dvorak, Christopher C., Haddad, Elie, Heimall, Jennifer, Dunn, Elizabeth, Cowan, Morton J., Pai, Sung-Yun, Kapoor, Neena, Satter, Lisa Forbes, Buckley, Rebecca H., O’Reilly, Richard J., Chandra, Sharat, Bednarski, Jeffrey J., Williams, Olatundun, Rayes, Ahmad, Moore, Theodore B., Ebens, Christen L., Davila Saldana, Blachy J., Petrovic, Aleksandra, Chellapandian, Deepak, Cuvelier, Geoffrey D.E., Vander Lugt, Mark T., Caywood, Emi H., Chandrakasan, Shanmuganathan, Eissa, Hesham, Goldman, Frederick D., Shereck, Evan, Aquino, Victor M., Desantes, Kenneth B., Madden, Lisa M., Miller, Holly K., Yu, Lolie, Broglie, Larisa, Gillio, Alfred, Shah, Ami J., Knutsen, Alan P., Andolina, Jeffrey P., Joshi, Avni Y., Szabolcs, Paul, Kapadia, Malika, Martinez, Caridad A., Parrot, Roberta E., Sullivan, Kathleen E., Prockop, Susan E., Abraham, Roshini S., Thakar, Monica S., Leiding, Jennifer W., Kohn, Donald B., Pulsipher, Michael A., Griffith, Linda M., Notarangelo, Luigi D., Puck, Jennifer M.

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First-Onset Herpesviral Infection and Lung Injury in Allogeneic Hematopoietic Cell Transplantation von Zhou, Xiaofeng, O'Dwyer, David N, Xia, Meng, Miller, Holly K, Chan, Paul R, Trulik, Kelsey, Chadwick, Mathew M, Hoffman, Timothy C, Bulte, Camille, Sekerak, Kevin, Wilke, Carol A, Patel, Swapneel J, Yokoyama, Wayne M, Murray, Susan, Yanik, Gregory A, Moore, Bethany B

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Successful treatment of severe refractory autoimmune hemolytic anemia after hematopoietic stem cell transplant with abatacept von Hess, Jennifer, Su, Leon, Nizzi, Frank, Beebe, Kristen, Magee, Kyrie, Salzberg, Dana, Stahlecker, Jennifer, Miller, Holly K., Adams, Roberta H., Ngwube, Alexander

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Contrasting Clinical Presentations In Brothers With Identical STAT3 Gain-Of-Function Mutations von Sachs, Jonathan W., Miller, Holly K., Wright, Benjamin L., Bauer, Cindy S.

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Hematopoietic Cell Transplantation in Patients With Primary Immune Regulatory Disorders (PIRD): A Primary Immune Deficiency Treatment Consortium (PIDTC) Survey von Chan, Alice Y., Leiding, Jennifer W., Liu, Xuerong, Logan, Brent R., Burroughs, Lauri M., Allenspach, Eric J., Skoda-Smith, Suzanne, Uzel, Gulbu, Notarangelo, Luigi D., Slatter, Mary, Gennery, Andrew R., Smith, Angela R., Pai, Sung-Yun, Jordan, Michael B., Marsh, Rebecca A., Cowan, Morton J., Dvorak, Christopher C., Craddock, John A., Prockop, Susan E., Chandrakasan, Shanmuganathan, Kapoor, Neena, Buckley, Rebecca H., Parikh, Suhag, Chellapandian, Deepak, Oshrine, Benjamin R., Bednarski, Jeffrey J., Cooper, Megan A., Shenoy, Shalini, Saldana, Blachy J. Davila, Forbes, Lisa R., Martinez, Caridad, Haddad, Elie, Shyr, David C., Chen, Karin, Sullivan, Kathleen E., Heimall, Jennifer, Wright, Nicola, Bhatia, Monica, Cuvelier, Geoffrey D. E., Goldman, Frederick D., Meyts, Isabelle, Miller, Holly K., Seidel, Markus G., Vander Lugt, Mark T., Bacchetta, Rosa, Weinacht, Katja G., Andolina, Jeffrey R., Caywood, Emi, Chong, Hey, de la Morena, Maria Teresa, Aquino, Victor M., Shereck, Evan, Walter, Jolan E., Dorsey, Morna J., Seroogy, Christine M., Griffith, Linda M., Kohn, Donald B., Puck, Jennifer M., Pulsipher, Michael A., Torgerson, Troy R.

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Cutaneous T-cell lymphoma as a unique presenting malignancy in X-linked magnesium defect with EBV infection and neoplasia (XMEN) disease von Freeman, Catherine M., Wright, Benjamin L., Bauer, Cindy S., Rukasin, Christine R., Chiang, Samuel C., Marsh, Rebecca A., Taylor, Steve, Jacobsen, Jeffrey, Miller, Holly K., Badia, Priscila

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Infectious Risk after Allogeneic Hematopoietic Cell Transplantation Complicated by Acute Graft-versus-Host Disease von Miller, Holly K, Braun, Thomas M, Stillwell, Terri, Harris, Andrew C, Choi, Sung, Connelly, James, Couriel, Daniel, Goldstein, Steven, Kitko, Carrie L, Magenau, John, Pawarode, Attaphol, Reddy, Pavan, Riwes, Mary, Yanik, Gregory A, Levine, John E

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IPEX Syndrome in Siblings with a Novel Variant in FOXP3 von Hines, Brittany, Wright, Benjamin L., Wadera, Sheetal, Cac, Natalie, Miller, Holly K., Abraham, Roshini S., Bauer, Cindy S.

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Adolescent male fertility following reduced‐intensity conditioning regimen for hematopoietic stem cell transplantation in non‐malignant disorders von Zhao, Jun, Beebe, Kristen, Magee, Kyrie, Salzberg, Dana, Stahlecker, Jennifer, Miller, Holly K., Adams, Roberta H., Lipskind, Shane, Walsh, Alexandra, Mirea, Lucia, Ngwube, Alexander

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GATA2 deficiency associated with copy number variation: A reference for considering inborn errors of immunity von Freeman, Catherine M., Barry, Timothy D., Bauer, Cindy S., Miller, Holly K., Rukasin, Christine R., Wright, Benjamin L.

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High risk of relapsed disease in patients with NK/T-cell chronic active Epstein-Barr virus disease outside of Asia von Dávila Saldaña, Blachy J., John, Tami, Bonifant, Challice, Buchbinder, David, Chandra, Sharat, Chandrakasan, Shanmuganathan, Chang, Weni, Chen, Leon, Elfassy, Hannah L., Geerlinks, Ashley V., Giller, Roger H., Goyal, Rakesh, Hagin, David, Islam, Shahidul, Mallhi, Kanwaldeep, Miller, Holly K., Owen, William, Pacheco, Martha, Patel, Niraj C., Querfeld, Christiane, Quigg, Troy, Richard, Nameeta, Schiff, Deborah, Shereck, Evan, Stenger, Elizabeth, Jordan, Michael B., Heslop, Helen E., Bollard, Catherine M., Cohen, Jeffrey I.

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TWO INFANTS PRESENTING WITH POLYMICROBIAL PNEUMONIA AND HYPOXEMIC RESPIRATORY FAILURE ASSOCIATED WITH HETEROZYGOUS VARIANTS IN CARMIL2 AND ITK von FORMOSO, AGATHA M, SIDEBOTTOM, NICOLE, LAND, MEGAN, K MILLER, HOLLY, S BAUER, CINDY, SACCO, KEITH

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Pediatric Graft-Versus-Host Disease von McInnis-Smith, Kerri, Miller, Holly K., Ramasubramanian, Aparna

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Antiviral T Cells for Adenovirus in the Pretransplant Period: A Bridge Therapy for Severe Combined Immunodeficiency von Miller, Holly K., Hanley, Patrick J., Lang, Haili, Lazarski, Christopher A., Chorvinsky, Elizabeth A., McCormack, Sarah, Roesch, Lauren, Albihani, Shuroug, Dean, Marcus, Hoq, Fahmida, Adams, Roberta H., Bollard, Catherine M., Keller, Michael D.

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Genotype, oxidase status, and preceding infection or autoinflammation do not affect allogeneic HCT outcomes for CGD von Leiding, Jennifer W, Arnold, Danielle E, Parikh, Suhag, Logan, Brent, Marsh, Rebecca A, Griffith, Linda M, Wu, Ruizhe, Kidd, Sharon, Mallhi, Kanwaldeep, Chellapandian, Deepak, Si Lim, Stephanie J, Grunebaum, Eyal, Falcone, E Liana, Murguia-Favela, Luis, Grossman, Debbi, Prasad, Vinod K, Heimall, Jennifer R, Touzot, Fabien, Burroughs, Lauri M, Bleesing, Jack, Kapoor, Neena, Dara, Jasmeen, Williams, Olatundun, Kapadia, Malika, Oshrine, Benjamin R, Bednarski, Jeffrey J, Rayes, Ahmad, Chong, Hey, Cuvelier, Geoffrey D E, Forbes Satter, Lisa R, Martinez, Caridad, Vander Lugt, Mark T, Yu, Lolie C, Chandrakasan, Shanmuganathan, Joshi, Avni, Prockop, Susan E, Dávila Saldaña, Blachy J, Aquino, Victor, Broglie, Larisa A, Ebens, Christen L, Madden, Lisa M, DeSantes, Kenneth, Milner, Jordan, Rangarajan, Hemalatha G, Shah, Ami J, Gillio, Alfred P, Knutsen, Alan P, Miller, Holly K, Moore, Theodore B, Graham, Pamela, Bauchat, Andrea, Bunin, Nancy J, Teira, Pierre, Petrovic, Aleksandra, Chandra, Sharat, Abdel-Azim, Hisham, Dorsey, Morna J, Birbrayer, Olga, Cowan, Morton J, Dvorak, Christopher C, Haddad, Elie, Kohn, Donald B, Notarangelo, Luigi D, Pai, Sung-Yun, Puck, Jennifer M, Pulsipher, Michael A, Torgerson, Troy R, Malech, Harry L, Kang, Elizabeth M

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Early Post-Transplant Viral Infections and the Incidence of Acute and Chronic Noninfectious Pulmonary Complications Following Hematopoietic Stem Cell Transplantation (HSCT) von Zhou, Xiaofeng, Trulik, Kelsey, Chadwick, Matthew M, Hoffman, Timothy, Bulte, Camille, Bloye, Kiernan, Miller, Holly K, Sekerak, Kevin, O'Dywer, David N, Moore, Bethany, Yanik, Gregory A

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Retrospective Analysis of Fresh Vs Cryopreserved Allogenic Bone Marrow Transplant within Pediatric Population: A Change in Practice Due to COVID-19 Pandemic von Hans, Rhea, Schwalbach, Charlotte, Salzberg, Dana, Adams, Roberta, Miller, Holly K., Sinno, Mohamad, Beebe, Kristen L., Giralt, Daniela, Stahlecker, Jennifer, Ngwube, Alexander

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