Hematopoietic cell transplantation for severe MPS I in the first six months of life: The heart of the matter von Braunlin, Elizabeth, Miettunen, Kelly, Lund, Troy, Luquette, Mark, Orchard, Paul

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Consequences of newborn screening: Neuroimaging in infants with severe MPS I ≤6 months of age von Braunlin, Elizabeth, Miettunen, Kelly, Orchard, Paul, Lund, Troy, Gupta, Ashish, Nascene, David

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Allogeneic hematopoietic stem cell transplant improves outcomes in fucosidosis von Gupta, Ashish, Lund, Troy, Anderson, Nicole, Miettunen, Kelly, Eisengart, Julie, Braunlin, Elizabeth, Orchard, Paul

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Non-invasive biomarkers of disease activity and organ damage in ANCA-associated vasculitis: a systematic review von Renson, Thomas, Kelly, Margaret M, Benediktsson, Hallgrimur, Grundhoefer, Nele, Luca, Nadia, Miettunen, Paivi, Twilt, Marinka, Grisaru, Silviu, Wade, Andrew, Banks, Anke, Fifi-Mah, Aurore, Hamiwka, Lorraine, Benseler, Susanne

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Consensus Treatment Plans for Chronic Nonbacterial Osteomyelitis Refractory to Nonsteroidal Anti-Inflammatory Drugs and/or with Active Spinal Lesions von Zhao, Yongdong, Wu, Eveline Y., Oliver, Melissa S., Cooper, Ashley M., Basiaga, Matthew L., Vora, Sheetal S., Lee, Tzielan C., Fox, Emily, Amarilyo, Gil, Stern, Sara M., Dvergsten, Jeffrey A., Haines, Kathleen A., Rouster-Stevens, Kelly A., Onel, Karen B., Cherian, Julie, Hausmann, Jonathan S., Miettunen, Paivi, Cellucci, Tania, Nuruzzaman, Farzana, Taneja, Angela, Barron, Karyl S., Hollander, Matthew C., Lapidus, Sivia K., Li, Suzanne C., Ozen, Seza, Girschick, Hermann, Laxer, Ronald M., Dedeoglu, Fatma, Hedrich, Christian M., Ferguson, Polly J.

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