Engineering Protein-Secreting Plasma Cells by Homology-Directed Repair in Primary Human B Cells von Hung, King L., Meitlis, Iana, Hale, Malika, Chen, Chun-Yu, Singh, Swati, Jackson, Shaun W., Miao, Carol H., Khan, Iram F., Rawlings, David J., James, Richard G.

Volltext

Treatment of Hemophilia A Using Factor VIII Messenger RNA Lipid Nanoparticles von Chen, Chun-Yu, Tran, Dominic M., Cavedon, Alex, Cai, Xiaohe, Rajendran, Raj, Lyle, Meghan J., Martini, Paolo G.V., Miao, Carol H.

Volltext

Antigen‐specific in vitro expansion of factor VIII‐specific regulatory T cells induces tolerance in hemophilia A mice von Smith, Bryn M., Lyle, Meghan J., Chen, Alex C., Miao, Carol H.

Volltext

Comparative glycosylation mapping of plasma-derived and recombinant human factor VIII von Qu, Jingyao, Ma, Cheng, Xu, Xiao-Qian, Xiao, Min, Zhang, Junping, Li, Dong, Liu, Ding, Konkle, Barbara A., Miao, Carol H., Li, Lei, Xiao, Weidong

Volltext

Effect of chimeric antigen receptor T cells against protease-activated receptor 1 for treating pancreatic cancer von Hung, Hao-Chien, Fan, Ming-Huei, Wang, Daniel, Miao, Carol H, Su, Pong, Liu, Chao-Lien

Volltext

Rapamycin relieves lentiviral vector transduction resistance in human and mouse hematopoietic stem cells von Wang, Cathy X., Sather, Blythe D., Wang, Xuefeng, Adair, Jennifer, Khan, Iram, Singh, Swati, Lang, Shanshan, Adams, Amie, Curinga, Gabrielle, Kiem, Hans-Peter, Miao, Carol H., Rawlings, David J., Torbett, Bruce E.

Volltext

Microbubbles and ultrasound increase intraventricular polyplex gene transfer to the brain von Tan, James-Kevin Y., Pham, Binhan, Zong, Yujin, Perez, Camilo, Maris, Don O., Hemphill, Ashton, Miao, Carol H., Matula, Thomas J., Mourad, Pierre D., Wei, Hua, Sellers, Drew L., Horner, Philip J., Pun, Suzie H.

Volltext

Development of therapeutic microbubbles for enhancing ultrasound-mediated gene delivery von Sun, Ryan R., Noble, Misty L., Sun, Samuel S., Song, Shuxian, Miao, Carol H.

Volltext

A Treg-Selective IL-2 Mutein Prevents the Formation of Factor VIII Inhibitors in Hemophilia Mice Treated With Factor VIII Gene Therapy von Chen, Alex C., Cai, Xiaohe, Li, Chong, Khoryati, Liliane, Gavin, Marc A., Miao, Carol H.

Volltext

Engineering Chimeric Antigen Receptor T Cells against Immune Checkpoint Inhibitors PD-1/PD-L1 for Treating Pancreatic Cancer von Yang, Ching-Yao, Fan, Ming Huei, Miao, Carol H., Liao, Yi Jen, Yuan, Ray-Hwang, Liu, Chao Lien

Volltext

Ex Vivo Expanded Human Vγ9Vδ2 T-Cells Can Suppress Epithelial Ovarian Cancer Cell Growth von Mao, Tsui Lien, Miao, Carol H, Liao, Yi Jen, Chen, Ying Jen, Yeh, Chia Yu, Liu, Chao Lien

Volltext

Induction of long-term tolerance to a specific antigen using anti-CD3 lipid nanoparticles following gene therapy von Chen, Chun-Yu, Vander Kooi, Amber, Cavedon, Alex, Cai, Xiaohe, Hoggatt, Jonathan, Martini, Paolo G.V., Miao, Carol H.

Volltext

Ultrasound-mediated gene delivery of factor VIII plasmids for hemophilia A gene therapy in mice von Song, Shuxian, Lyle, Meghan J., Noble-Vranish, Misty L., Min-Tran, Dominic M., Harrang, James, Xiao, Weidong, Unger, Evan C., Miao, Carol H.

Volltext

Strategies to target long-lived plasma cells for treating hemophilia A inhibitors von Liu, Chao Lien, Lyle, Meghan J., Shin, Simon C., Miao, Carol H.

Volltext

Site-Specific N- and O-Glycosylation Analysis of Human Plasma Fibronectin von Liu, Ding, Wang, Shuaishuai, Zhang, Junping, Xiao, Weidong, Miao, Carol H., Konkle, Barbara A., Wan, Xiu-Feng, Li, Lei

Volltext

Long-Term and Therapeutic-Level Hepatic Gene Expression of Human Factor IX after Naked Plasmid Transfer in Vivo von Miao, Carol H., Thompson, Arthur R., Loeb, Keith, Ye, Xin

Volltext

Ultrasound-Mediated Gene Therapy in Swine Livers Using Single-Element, Multi-lensed, High-Intensity Ultrasound Transducers von Noble-Vranish, Misty L., Song, Shuxian, Morrison, Kyle P., Tran, Dominic M., Sun, Ryan R., Loeb, Keith R., Keilman, George W., Miao, Carol H.

Volltext

Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors von Snyder, Richard O, Miao, Carol H, Patijn, Gijsbert A, Spratt, S. Kaye, Danos, Olivier, Nagy, Dea, Gown, Allen M, Winther, Brian, Meuse, Leonard, Cohen, Lawrence K, Thompson, Arthur R, Kay, Mark A

Volltext

Ultrasound enhances gene delivery of human factor IX plasmid von MIAO, Carol H, BRAYMAN, Andrew A, LOEB, Keith R, PEIQING YE, LING ZHOU, MOURAD, Pierre, CRUM, Lawrence A

Volltext

Hemophilia A gene therapy via intraosseous delivery of factor VIII-lentiviral vectors von Miao, Carol H

Volltext