Rational Design of Antisense Oligomers to Induce Dystrophin Exon Skipping von Mitrpant, Chalermchai, Adams, Abbie M, Meloni, Penny L, Muntoni, Francesco, Fletcher, Sue, Wilton, Steve D

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Personalized exon skipping strategies to address clustered non-deletion dystrophin mutations von Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D

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Antisense suppression of donor splice site mutations in the dystrophin gene transcript von Fletcher, Sue, Meloni, Penny L., Johnsen, Russell D., Wong, Brenda L., Muntoni, Francesco, Wilton, Stephen D.

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Personalized exon skipping strategies to address clustered non-deletion dystrophin mutations von Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D

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Personalized exon skipping strategies to address clustered non-deletion dystrophin mutations von Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D

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AO sequences, annealing coordinates and cocktail composition. Each cocktail consists of equimolar amounts of the individual oligomers. Oligomer nomenclature is based upon annealing... von Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D

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Personalized exon skipping strategies to address clustered non-deletion dystrophin mutations von Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D

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Sequences of amplification primers used to study the dystrophin transcript von Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D

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Personalized exon skipping strategies to address clustered non-deletion dystrophin mutations von Forrest, Sarah, Meloni, Penny L, Muntoni, Francesco, Kim, Jihee, Fletcher, Sue, Wilton, Steve D

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Splice-switching as a treament for duchenne muscular dystrophy von Fletcher, Sue, Adams, Abbie M., Meloni, Penny L., Johnsen, Russell, Forrest, Sarah, Greer, Kane, Wilton, Steve D.

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Transplantation: clinical studies - A von Yildirim, T., Yilmaz, R., Altindal, M., Turkmen, E., Arici, M., Altun, B., Erdem, Y., Guliyev, O., Erkmen Uyar, M., Tutal, E., Bal, Z., Sezer, S., Bal, U., Say n, B., Erdemir, B., O'Rourke-Potowki, A., Gauge, N., Penny, H., Cronin, A., Frame, S., Goldsmith, D. J., Yagan, J. A., Chandraker, A., Velickovic Radovanovic, R. M., Catic Djordjevic, A., Mitic, B., Stefanovic, N., Cvetkovic, T., Serpieri, N., Grosjean, F., Sileno, G., Torreggiani, M., Esposito, V., Mangione, F., Abelli, M., Castoldi, F., Catucci, D., Esposito, C., Dal Canton, A., Vatazin, A. V., Zulkarnaev, A. B., Borst, C., Liu, Y., Thoning, J., Tepel, M., Libetta, C., Margiotta, E., Borettaz, I., Canevari, M., Martinelli, C., Lainu, E., Meloni, F., Sepe, V., Miguel Costa, R., Vasquez Martul, E., Reboredo, J., Rivera, C., Simonato, F., Tognarelli, G., Daidola, G., Gallo, E., Burdese, M., Cantaluppi, V., Biancone, L., Segoloni, G. P., Priora, M., Messina, M., Tamagnone, M., Linsalata, A., Lavacca, A., Segoloni, G., Zuidema, W., Erdman, R., van de Wetering, J., Dor, F., Roodnat, J., Massey, E., Timmerman, L., IJzermans, J., Weimar, W., Sibley-Allen, C., Hilton, R., Moghul, M., Burnapp, L., Blake, G., Koo, T. Y., Park, J.-S., Park, H. C., Kim, G.-H., Lee, C. H., Oh, I. H., Kang, C. M., Hwang, J. K., Park, S. C., Choi, B. S., Chun, H. J., Kim, J. I., Yang, C. W., Moon, I. S., Van Laecke, S.

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