SMA CARNI-VAL trial part I: double-blind, randomized, placebo-controlled trial of L-carnitine and valproic acid in spinal muscular atrophy von Swoboda, Kathryn J, Scott, Charles B, Crawford, Thomas O, Simard, Louise R, Reyna, Sandra P, Krosschell, Kristin J, Acsadi, Gyula, Elsheik, Bakri, Schroth, Mary K, D'Anjou, Guy, LaSalle, Bernard, Prior, Thomas W, Sorenson, Susan L, Maczulski, Jo Anne, Bromberg, Mark B, Chan, Gary M, Kissel, John T

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Consensus Statement on Standard of Care for Congenital Myopathies von Wang, Ching H., Dowling, James J., North, Kathryn, Schroth, Mary K., Sejersen, Thomas, Shapiro, Frederic, Bellini, Jonathan, Weiss, Hali, Guillet, Marc, Amburgey, Kimberly, Apkon, Susan, Bertini, Enrico, Bonnemann, Carsten, Clarke, Nigel, Connolly, Anne M., Estournet-Mathiaud, Brigitte, Fitzgerald, Dominic, Florence, Julaine M., Gee, Richard, Gurgel-Giannetti, Juliana, Glanzman, Allan M., Hofmeister, Brittany, Jungbluth, Heinz, Koumbourlis, Anastassios C., Laing, Nigel G., Main, Marion, Morrison, Leslie A., Munns, Craig, Rose, Kristy, Schuler, Pamela M., Sewry, Caroline, Storhaug, Kari, Vainzof, Mariz, Yuan, Nanci

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Phase II open label study of valproic acid in spinal muscular atrophy von Swoboda, Kathryn J, Scott, Charles B, Reyna, Sandra P, Prior, Thomas W, LaSalle, Bernard, Sorenson, Susan L, Wood, Janine, Acsadi, Gyula, Crawford, Thomas O, Kissel, John T, Krosschell, Kristin J, D'Anjou, Guy, Bromberg, Mark B, Schroth, Mary K, Chan, Gary M, Elsheikh, Bakri, Simard, Louise R

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Special Considerations in the Respiratory Management of Spinal Muscular Atrophy von Schroth, Mary K

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Assessment of Barriers to Referral and Appointment Wait Times for the Evaluation of Spinal Muscular Atrophy (SMA): Findings from a Web-Based Physician Survey von Curry, Mary A., Cruz, Rosángel E., Belter, Lisa T., Schroth, Mary K., Jarecki, Jill

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American College of Chest Physicians Consensus Statement on the Respiratory and Related Management of Patients With Duchenne Muscular Dystrophy Undergoing Anesthesia or Sedation von Birnkrant, David J., Panitch, Howard B., Benditt, Joshua O., Boitano, Louis J., Carter, Edward R., Cwik, Valerie A., Finder, Jonathan D., Iannaccone, Susan T., Jacobson, Lawrence E., Kohn, Gary L., Motoyama, Etsuro K., Moxley, Richard T., Schroth, Mary K., Sharma, Girish D., Sussman, Michael D.

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Diagnosis and management of spinal muscular atrophy: Part 2: Pulmonary and acute care; medications, supplements and immunizations; other organ systems; and ethics von Finkel, Richard S., Mercuri, Eugenio, Meyer, Oscar H., Simonds, Anita K., Schroth, Mary K., Graham, Robert J., Kirschner, Janbernd, Iannaccone, Susan T., Crawford, Thomas O., Woods, Simon, Muntoni, Francesco, Wirth, Brunhilde, Montes, Jacqueline, Main, Marion, Mazzone, Elena S., Vitale, Michael, Snyder, Brian, Quijano-Roy, Susana, Bertini, Enrico, Davis, Rebecca Hurst, Qian, Ying, Sejersen, Thomas

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Hip Pain in Nonambulatory Children with Type-I or II Spinal Muscular Atrophy von Hanna, Rewais B., Nahm, Nick, Bent, Melissa A., Sund, Sarah, Patterson, Karen, Schroth, Mary K., Halanski, Matthew A.

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Sagittal Plane Deformities in Children with SMA2 following Posterior Spinal Instrumentation von Halanski, Matthew A., Hanna, Rewais, Bernatz, James, Twedt, Max, Sund, Sarah, Patterson, Karen, Noonan, Kenneth J., Schultz, Meredith, Schroth, Mary K., Sharafinski, Mark, Hasley, Brian P.

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Rhinovirus Replication Causes RANTES Production in Primary Bronchial Epithelial Cells von Schroth, Mary K, Grimm, Elizabeth, Frindt, Paula, Galagan, Dawn M, Konno, Shin-Ichi, Love, Robert, Gern, James E

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Perspectives on Clinical Trials in Spinal Muscular Atrophy von Swoboda, Kathryn J., Kissel, John T., Crawford, Thomas O., Bromberg, Mark B., Acsadi, Gyula, D'Anjou, Guy, Krosschell, Kristin J., Reyna, Sandra P., Schroth, Mary K., Scott, Charles B., Simard, Louise R.

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Radiographic and Respiratory Effects of Growing Rods in Children With Spinal Muscular Atrophy von Lenhart, Rachel L, Youlo, Sylvester, Schroth, Mary K, Noonan, Kenneth J, McCarthy, James, Mann, David, Hetzel, Scott, Sund, Sarah A, Halanski, Matthew A

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SMA CARNI-VAL TRIAL PART II: A Prospective, Single-Armed Trial of L-Carnitine and Valproic Acid in Ambulatory Children with Spinal Muscular Atrophy von Kissel, John T, Scott, Charles B, Reyna, Sandra P, Crawford, Thomas O, Simard, Louise R, Krosschell, Kristin J, Acsadi, Gyula, Elsheik, Bakri, Schroth, Mary K, D'Anjou, Guy, LaSalle, Bernard, Prior, Thomas W, Sorenson, Susan, Maczulski, Jo Anne, Bromberg, Mark B, Chan, Gary M, Swoboda, Kathryn J

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SMA valiant trial: A prospective, double-blind, placebo-controlled trial of valproic acid in ambulatory adults with spinal muscular atrophy von Kissel, John T., Elsheikh, Bakri, King, Wendy M., Freimer, Miriam, Scott, Charles B., Kolb, Stephen J., Reyna, Sandra P., Crawford, Thomas O., Simard, Louise R., Krosschell, Kristin J., Acsadi, Gyula, Schroth, Mary K., D'Anjou, Guy, LaSalle, Bernard, Prior, Thomas W., Sorenson, Susan, Maczulski, Jo Anne, Swoboda, Kathryn J.

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Spinal Muscular Atrophy Update in Best Practices: Recommendations for Treatment Considerations von Schroth, Mary K, Deans, Jennifer, Bharucha Goebel, Diana X, Burnette, W Bryan, Darras, Basil T, Elsheikh, Bakri H, Felker, Marcia V, Klein, Andrea, Krueger, Jena, Proud, Crystal M, Veerapandiyan, Aravindhan, Graham, Robert J

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Nutritional Practices at a Glance: Spinal Muscular Atrophy Type I Nutrition Survey Findings von Davis, Rebecca Hurst, Godshall, Barbara J., Seffrood, Erin, Marcus, Mary, LaSalle, Bernard A, Wong, Brenda, Schroth, Mary K., Swoboda, Kathryn J.

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Compound muscle action potential and motor function in children with spinal muscular atrophy von Lewelt, Aga, Krosschell, Kristin J., Scott, Charles, Sakonju, Ai, Kissel, John T., Crawford, Thomas O., Acsadi, Gyula, D'anjou, Guy, Elsheikh, Bakri, Reyna, Sandra P., Schroth, Mary K., Maczulski, Jo Anne, Stoddard, Gregory J., Elovic, Elie, Swoboda, Kathryn J.

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Clinical trial of L‐Carnitine and valproic acid in spinal muscular atrophy type I von Krosschell, Kristin J., Kissel, John T., Townsend, Elise L., Simeone, Sarah D., Zhang, Ren Zhe, Reyna, Sandra P., Crawford, Thomas O., Schroth, Mary K., Acsadi, Gyula, Kishnani, Priya S., Von Kleist‐Retzow, Jürgen‐Christoph, Hero, Barbara, D'Anjou, Guy, Smith, Edward C., Elsheikh, Bakri, Simard, Louise R., Prior, Thomas W., Scott, Charles B., Lasalle, Bernard, Sakonju, Ai, Wirth, Brunhilde, Swoboda, Kathryn J.

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Is prophylactic formal fusion with implant revision necessary in non-ambulatory children with spinal muscular atrophy and growing rods who are no longer lengthened? von Hanna, Rewais, Sharafinski, Mark, Patterson, Karen, Noonan, Kenneth J., Sund, Sarah, Schultz, Meredith, Schroth, Mary K., Hetzel, Scott, Halanski, Matthew A.

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Early laparoscopic fundoplication and gastrostomy in infants with spinal muscular atrophy type I von Durkin, Emily T, Schroth, Mary K, Helin, Margaret, Shaaban, Aimen F

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