Clinical development of autologous genome-edited hematopoietic stem cells to treat mucopolysaccharidosis type I von Poletto, Edina, Marathe, Manasvi, Margittai, Dana, Liu, Xikun, Jiang, Qiaoshi, Deshpande, Trupti, Fazeli, Fariba, Ikeda, Tsutomu, Van Horn, Timothy, Gomez-Ospina, Natalia

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