Intravenous delivery of a chemically modified sulfamidase efficiently reduces heparan sulfate storage and brain pathology in mucopolysaccharidosis IIIA mice von Gustavsson, Susanne, Ohlin Sjöström, Elisabet, Tjernberg, Agneta, Janson, Juliette, Westermark, Ulrica, Andersson, Tommy, Makower, Åsa, Arnelöf, Erik, Andersson, Gudrun, Svartengren, Jan, Ekholm, Carina, Svensson Gelius, Stefan

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Ancestral lysosomal enzymes with increased activity harbor therapeutic potential for treatment of Hunter syndrome von Hendrikse, Natalie M., Sandegren, Anna, Andersson, Tommy, Blomqvist, Jenny, Makower, Åsa, Possner, Dominik, Su, Chao, Thalén, Niklas, Tjernberg, Agneta, Westermark, Ulrica, Rockberg, Johan, Svensson Gelius, Stefan, Syrén, Per-Olof, Nordling, Erik

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Improved identification of host cell proteins in a protein biopharmaceutical by LC–MS/MS using the ProteoMiner™ Enrichment Kit von Mörtstedt, Harriet, Makower, Åsa, Edlund, Per-Olof, Sjöberg, Katarina, Tjernberg, Agneta

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Robust LC–MS/MS methods for analysis of heparan sulfate levels in CSF and brain for application in studies of MPS IIIA von Makower, Åsa, Arnelöf, Erik, Andersson, Tommy, Edlund, Per-Olof, Gustavsson, Susanne, Janson, Juliette, Gelius, Stefan Svensson, Tjernberg, Agneta

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