Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial von Magrin, Elisa, Semeraro, Michaela, Hebert, Nicolas, Joseph, Laure, Magnani, Alessandra, Chalumeau, Anne, Gabrion, Aurélie, Roudaut, Cécile, Marouene, Jouda, Lefrere, Francois, Diana, Jean-Sebastien, Denis, Adeline, Neven, Bénédicte, Funck-Brentano, Isabelle, Negre, Olivier, Renolleau, Sylvain, Brousse, Valentine, Kiger, Laurent, Touzot, Fabien, Poirot, Catherine, Bourget, Philippe, El Nemer, Wassim, Blanche, Stéphane, Tréluyer, Jean-Marc, Asmal, Mohammed, Walls, Courtney, Beuzard, Yves, Schmidt, Manfred, Hacein-Bey-Abina, Salima, Asnafi, Vahid, Guichard, Isabelle, Poirée, Maryline, Monpoux, Fabrice, Touraine, Philippe, Brouzes, Chantal, de Montalembert, Mariane, Payen, Emmanuel, Six, Emmanuelle, Ribeil, Jean-Antoine, Miccio, Annarita, Bartolucci, Pablo, Leboulch, Philippe, Cavazzana, Marina

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Early versus Deferred Antiretroviral Multidrug Therapy in Infants Infected with HIV Type 1 von Faye, Albert, Le Chenadec, Jerôme, Dollfus, Catherine, Thuret, Isabelle, Douard, Danièle, Firtion, Ghislaine, Lachassinne, Eric, Levine, Martine, Nicolas, Joelle, Monpoux, Fabrice, Tricoire, Joelle, Rouzioux, Christine, Tardieu, Marc, Mayaux, Marie Jeanne, Blanche, Stéphane

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Rituximab therapy for childhood Evans syndrome von Bader-Meunier, Brigitte, Aladjidi, Nathalie, Bellmann, Francoise, Monpoux, Fabrice, Nelken, Brigitte, Robert, Alain, Armari-Alla, Corinne, Picard, Capucine, Ledeist, Francoise, Munzer, Martine, Yacouben, Karima, Bertrand, Yves, Pariente, Antoine, Chausse, Arnaud, Perel, Yves, Leverger, Guy

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Long-Term Nonprogression of HIV Infection in Children: Evaluation of the ANRS Prospective French Pediatric Cohort von Warszawski, Josiane, Lechenadec, Jérôme, Faye, Albert, Dollfus, Catherine, Firtion, Ghislaine, Meyer, Laurence, Douard, Danielle, Monpoux, Fabrice, Tricoire, Joëlle, Benmebarek, Yassine, Rouzioux, Christine, Blanche, Stéphane

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Tolerance induction to deferasirox in a child with transfusion-dependent beta thalassemia von Pondrom, Morgane, Monpoux, Fabrice, Rocher, Fanny, Gastaut, Nadia, Bailly-Piccini, Carole, Poirée, Maryline

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Transient elastography (Fibroscan) in HIV-1 vertically infected children. A cross-sectional study von Monpoux, Fabrice, Huguon, Emilie, Truchi, Régine, Rubio, Amandine, Riolo, Valérie, Deville, Anne, Boutte, Patrick, Tran, Albert

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Quality of life of siblings of adolescents with severe haemophilia (FRATHEMO): An ancillary study to the TRANSHEMO project von Nguyen, Ngoc Anh Thu, Auquier, Pascal, Beltran Anzola, Any, Harroche, Annie, Huguenin, Yoann, Hochart, Audrey, Meunier, Sandrine, Frotscher, Birgit, Nguyen, Philippe, Schneider, Pascale, Berger, Claire, Lebreton, Aurélien, Vanderbecken, Stéphane, De Raucourt, Emmanuelle, D'Oiron, Roseline, Oudot‐Challard, Caroline, Baumstarck, Karine, Boucekine, Mohamed, Tabélé, Clémence, Rosso‐Delsemme, Natacha, Sannié, Thomas, Giraud, Nicolas, Chambost, Hervé, Resseguier, Noémie

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Maintenance darunavir/ritonavir monotherapy to prevent perinatal HIV transmission, ANRS-MIE 168 MONOGEST study von Mandelbrot, Laurent, Tubiana, Roland, Frange, Pierre, Peytavin, Gilles, Le Chenadec, Jerome, Canestri, Ana, Morlat, Philippe, Brunet-Cartier, Cécile, Sibiude, Jeanne, Peretti, Delphine, Chambrin, Véronique, Chabrol, Amélie, Bui, Eida, Simon-Toulza, Caroline, Marchand, Lucie, Paul, Christelle, Delmas, Sandrine, Avettand-Fenoel, Véronique, Warszawski, Josiane

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Determinants of adherence and consequences of the transition from adolescence to adulthood among young people with severe haemophilia (TRANSHEMO): A multicentric French national ob... von Nguyen, Ngoc Anh Thu, Auquier, Pascal, Beltran Anzola, Any, Harroche, Annie, Castet, Sabine, Huguenin, Yoann, Meunier, Sandrine, Repesse, Yohann, D'Oiron, Roseline, Rauch, Antoine, Desprez, Dominique, Spiegel, Alexandra, Chamouni, Pierre, Schneider, Pascale, Baumstarck, Karine, Boucekine, Mohamed, Tabele, Clémence, Viprey, Marie, Leroy, Tanguy, Roques, Marie‐Anaïs, Sannie, Thomas, Giraud, Nicolas, Chambost, Hervé, Resseguier, Noémie, Apostolidis, Thémis, Ardillon, Laurent, Bayart, Sophie, Berger, Claire, Bertrand, Marie‐Anne, Biron‐Andreani, Christine, Borel‐Derlon, Annie, Calvez, Thierry, Celli, Amandine, Claeyssens Donadel, Ségolène, De Raucourt, Emmanuelle, Falaise, Céline, Fournel, Alexandra, Frotscher, Birgit, Gay, Valérie, Genre‐Volot, Fabienne, Goudemand, Jenny, Gruel, Yves, Guillet, Benoît, Hassoun, Abel, Hochart, Audrey, Lambert, Thierry, Lebreton, Aurélien, Lienhart, Anne, Marlu, Raphaël, Martin, Michèle, Milien, Vanessa, Monpoux, Fabrice, Morange, Pierre‐Emmanuel, Mourey, Guillaume, Negrier, Claude, Nguyen, Philippe, Nyombe, Placide, Oudot‐Challard, Caroline, Pan‐Petesch, Brigitte, Polack, Benoît, Rafowicz, Anne, Rivaud, Delphine, Rohrlich, Pierre‐Simon, Rosso‐Delsemme, Natacha, Rousseau, Florence, Stoven, Cecile, Susen, Sophie, Tardy, Brigitte, Trossaërt, Marc, Valentin, Jean‐Baptiste, Vanderbecken, Stéphane, Voltzenlogel, Romain, Voyer‐Ebrard, Annelise, Wibaut, Bénédicte

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Benefits of rituximab as a second‐line treatment for autoimmune haemolytic anaemia in children: a prospective French cohort study von Ducassou, Stéphane, Leverger, Guy, Fernandes, Helder, Chambost, Hervé, Bertrand, Yves, Armari‐Alla, Corinne, Nelken, Brigitte, Monpoux, Fabrice, Guitton, Corinne, Leblanc, Thierry, Fisher, Alain, Lejars, Odile, Jeziorski, Eric, Fouissac, Fanny, Lutz, Patrick, Pasquet, Marlène, Pellier, Isabelle, Piguet, Christophe, Vic, Philippe, Bayart, Sophie, Marie‐Cardine, Aude, Michel, Marc, Perel, Yves, Aladjidi, Nathalie

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Transfusion requirements and complication rate in β‐thalassemia intermedia due to heterozygous β‐globin gene mutation and triplicated α‐globin genes von Bonello‐Palot, Nathalie, Benoit, Audrey, Agouti, Imane, Hamouda, Ilyes, Brousse, Valentine, Allali, Slimane, Ame, Shanti, Atmani, Sai, Bachir, Dora, Bartolucci, Pablo, Belloy, Marie, Bernit, Emmanuelle, Besancon‐Bergelin, Anne, Blanc, Michel, Brasme, Jean‐François, Brousse, Valentine, Cannas, Giovanna, Comont, Thibault, Conde, Mohamed, Couec, Marie‐Laure, Cougoul, Pierre, De‐Montalembert, Marianne, Donadieu, Jean, Dossier, Antoine, Fasola, Sylvie, Faucher, Benoit, Galacteros, Frederic, Garnier, Nathalie, Gauthier, Alexandra, Gellen‐Dautremer, Justine, Girodon, François, Gonzales, Fanny, Guichard, Isabelle, Guillet, Henri, Guitton, Corinne, Habibi, Anoosha, Holvoet, Laurent, Hot, Arnaud, Huguenin, Yoann, Ithier, Ghislaine, Jean, Estelle, Lachenal, Florence, Lahary, Agnes, Lambilliotte, Anne, Lange, Franciska, Leblanc, Thierry, Lehnert, Agnes, Leverger, Guy, Lioure, Bruno, Lutz, Laurence, Magda, Alexis, Makowski, Caroline, Malvezzi, Paolo, Manoli, Corina, Masseau, Agathe, Masserot‐Lureau, Caroline, Mathey, Catherine, Mathieu, Suzanne, Mattioni, Sarah, Micheau, Marguerite, Michel, Gerard, Missud, Florence, Monpoux, Fabrice, Navarro, Robert, Ngo, Stéphanie, Nimubona, Stanislas, Orvain, Corentin, Oziol, Eric, Paillard, Catherine, Pegourie, Brigitte, Phulpin, Aurélie, Piguet, Christophe, Pluchart, Claire, Pondarre, Corinne, Renard, Cécile, Ribeil, Jean‐Antoine, Rohrlich, Pierre‐Simon, Soto, Bertrand, Spiegel, Alexandra, Stankovic, Katia, Steschenko, Dominique, Swiader, Laure, Thomas, Caroline, Thuret, Isabelle, Valentin, Jean‐Baptiste, Zenchri, Ferielle, Badens, Catherine

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Results from the Completed Hgb-205 Trial of Lentiglobin for β-Thalassemia and Lentiglobin for Sickle Cell Disease Gene Therapy von Magrin, Elisa, Semeraro, Michaela, Magnani, Alessandra, Puy, Hervé, Miccio, Annarita, Hebert, Nicolas, Diana, Jean-Sebastien, Lefrere, Francois, Suarez, Felipe, Hermine, Olivier, Brousse, Valentine, Poirot, Catherine, Bourget, Philippe, El Nemer, Wassim, Guichard, Isabelle, Moshous, Despina, Neven, Benedicte, Monpoux, Fabrice, Poirée, Marilyne, Bartolucci, Pablo, Meritet, Jean-François, Grévent, David, Lefebvre, Thibaud, Asmal, Mohammed, Whitney, Erin, Gayron, Marisa, Huang, Wenmei, Funck-Brentano, Isabelle, de Montalembert, Mariane, Joseph, Laure, Ribeil, Jean-Antoine, Cavazzana, Marina

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Gene Therapy in Patients with Transfusion-Dependent [beta]-Thalassemia von Thompson, Alexis A, Walters, Mark C, Kwiatkowski, Janet, Rasko, John EJ, Ribeil, Jean-Antoine, Hongeng, Suradej, Magrin, Elisa, Schiller, Gary J, Payen, Emmanuel, Semeraro, Michaela, Moshous, Despina, Lefrere, Francois, Puy, Hervé, Bourget, Philippe, Magnani, Alessandra, Caccavelli, Laure, Diana, Jean-Sébastien, Suarez, Felipe, Monpoux, Fabrice, Brousse, Valentine, Poirot, Catherine, Brouzes, Chantal, Meritet, Jean-François, Pondarré, Corinne, Beuzard, Yves, Chrétien, Stany, Lefebvre, Thibaud, Teachey, David T, Anurathapan, Usanarat, Ho, P Joy, von Kalle, Christof, Kletzel, Morris, Vichinsky, Elliott, Soni, Sandeep, Veres, Gabor, Negre, Olivier, Ross, Robert W, Davidson, David, Petrusich, Alexandria, Sandler, Laura, Asmal, Mohammed, Hermine, Olivier, De Montalembert, Mariane, Hacein-Bey-Abina, Salima, Blanche, Stéphane, Leboulch, Philippe, Cavazzana, Marina

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Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta A... von Cavazzana, Marina, Ribeil, Jean-Antoine, Payen, Emmanuel, Suarez, Felipe, Beuzard, Yves, Touzot, Fabien, Cavallesco, Resy, Lefrere, Francois, Chretien, Stany, Bourget, Philippe, Monpoux, Fabrice, Pondarre, Corinne, Neven, Benedicte, Schmidt, Manfred, von Kalle, Christof, Kuypers, Frans A., Sandler, Laura, Soni, Sandeep, Hermine, Olivier, Blanche, Stephane, De Montalembert, Mariane, Hacien-Bey-Abina, Salima, Leboulch, Philippe

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279. Clinical Outcomes of Gene Therapy with BB305 Lentiviral Vector for Sickle Cell Disease and β-Thalassemia von Cavazzana, Marina, Ribeil, Jean-Antoine, Payen, Emmanuel, Touzot, Fabien, Neven, Bénédicte, Lefrere, Francois, Suarez, Felipe, Magrin, Elisa, Beuzard, Yves, Chretien, Stany, Bourget, Philippe, Monpoux, Fabrice, Pondarré, Corinne, Bartolucci, Pablo, Schmidt, Manfred, von Kalle, Christof, Sandler, Laura, Soni, Sandeep, Semeraro, Michaela, Nemer, Wassim El, Hermine, Olivier, de Montalembert, Mariane, Blanche, Stéphane, Hacein-Bey-Abina, Salima, Leboulch, Philippe

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Fusion of TEL, the ETS-Variant Gene 6 (ETV6), to the Receptor-Associated Kinase JAK2 as a Result of t(9; 12) in a Lymphoid and t(9; 15; 12) in a Myeloid Leukemia von Peeters, Pieter, Raynaud, Sophie D., Cools, Jan, Wlodarska, Iwona, Grosgeorge, Josiane, Philip, Patrick, Monpoux, Fabrice, Van Rompaey, Luc, Baens, Mathijs, Van den Berghe, Herman, Marynen, Peter

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Fusion of TEL, the ETS-variant gene 6 (ETV6), to the receptor-associated kinase JAK2 as a result of t(9; 12) in a lymphoid and t(9; 15;12) in a myeloid leukemia von PEETERS, P, RAYNAUD, S. D, MARYNEN, P, COOLS, J, WLODARSKA, I, GROSGEORGE, J, PHILIP, P, MONPOUX, F, VAN ROMPAEY, L, BAENS, M, VAN DEN BERGHE, H

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Protective effect of IgM against colonization of the respiratory tract by nontypeable Haemophilus influenzae in patients with hypogammaglobulinemia von Micol, Romain, MD, MPH, PhD, Kayal, Samer, MD, PhD, Mahlaoui, Nizar, MD, MSc, Beauté, Julien, MD, MSc, Brosselin, Pauline, MD, MPH, Dudoit, Yasmine, BS, Obenga, Gaëlle, MD, Barlogis, Vincent, MD, Aladjidi, Nathalie, MD, Kebaili, Kamila, MD, Thomas, Caroline, MD, Dulieu, Fabienne, MD, Monpoux, Fabrice, MD, Nové-Josserand, Raphaële, MD, Pellier, Isabelle, MD, Lambotte, Olivier, MD, PhD, Salmon, Alexandra, MD, Masseau, Agathe, MD, Galanaud, Pierre, MD, Oksenhendler, Eric, MD, Tabone, Marie-Dominique, MD, Teira, Pierre, MD, Coignard-Biehler, Hélène, MD, Lanternier, Fanny, MD, Join-Lambert, Olivier, MD, PhD, Mouillot, Gaël, PhD, Theodorou, Ioannis, MD, PhD, Lecron, Jean-Claude, PhD, Alyanakian, Marie-Alexandra, MD, PhD, Picard, Capucine, MD, PhD, Blanche, Stéphane, MD, Hermine, Olivier, MD, PhD, Suarez, Felipe, MD, PhD, Debré, Marianne, MD, Lecuit, Marc, MD, PhD, Lortholary, Olivier, MD, PhD, Durandy, Anne, MD, PhD, Fischer, Alain, MD, PhD

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Determinants of adherence and consequences of the transition from adolescence to adulthood among young people with severe haemophilia (TRANSHEMO): study protocol for a multicentric... von Resseguier, Noémie, Rosso-Delsemme, Natacha, Beltran Anzola, Any, Baumstarck, Karine, Milien, Vanessa, Ardillon, Laurent, Bayart, Sophie, Berger, Claire, Bertrand, Marie-Anne, Biron-Andreani, Christine, Borel-Derlon, Annie, Castet, Sabine, Chamouni, Pierre, Claeyssens Donadel, Ségolène, De Raucourt, Emmanuelle, Desprez, Dominique, Falaise, Céline, Frotscher, Birgit, Gay, Valérie, Goudemand, Jenny, Gruel, Yves, Guillet, Benoît, Harroche, Annie, Hassoun, Abel, Huguenin, Yoann, Lambert, Thierry, Lebreton, Aurélien, Lienhart, Anne, Martin, Michèle, Meunier, Sandrine, Monpoux, Fabrice, Mourey, Guillaume, Negrier, Claude, Nguyen, Philippe, Nyombe, Placide, Oudot, Caroline, Pan-Petesch, Brigitte, Polack, Benoît, Rafowicz, Anne, Rauch, Antoine, Rivaud, Delphine, Schneider, Pascale, Spiegel, Alexandra, Stoven, Cecile, Tardy, Brigitte, Trossaërt, Marc, Valentin, Jean-Baptiste, Vanderbecken, Stéphane, Volot, Fabienne, Voyer-Ebrard, Annelise, Wibaut, Bénédicte, Leroy, Tanguy, Sannie, Thomas, Chambost, Hervé, Auquier, Pascal

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Study Hgb-205: Outcomes of Gene Therapy for Hemoglobinopathies Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral βΑ-T87Q-Globin Vector... von Cavazzana, Marina, Ribeil, Jean-Antoine, Payen, Emmanuel, Suarez, Felipe, Beuzard, Yves, Touzot, Fabien, Cavallesco, Resy, Lefrère, Francois, Chretien, Stany, Bourget, Phillipe, Monpoux, Fabrice, Pondarre, Corrine, Neven, Benedicte, Schmidt, Manfred, von Kalle, Christof, Sandler, Laura, Soni, Sandeep, Hermine, Olivier, Blanche, Stephanie, De Montalembert, Mariane, Hacein-Bey-Abina, Salima, Leboulch, Philippe

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