AAV2.7m8 is a powerful viral vector for inner ear gene therapy von Isgrig, Kevin, McDougald, Devin S., Zhu, Jianliang, Wang, Hong Jun, Bennett, Jean, Chien, Wade W.

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SIRT1 and NRF2 Gene Transfer Mediate Distinct Neuroprotective Effects Upon Retinal Ganglion Cell Survival and Function in Experimental Optic Neuritis von McDougald, Devin S, Dine, Kimberly E, Zezulin, Alexandra U, Bennett, Jean, Shindler, Kenneth S

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Cochlear gene transfer mediated by adeno-associated virus: Comparison of two surgical approaches von Chien, Wade W., McDougald, Devin S., Roy, Soumen, Fitzgerald, Tracy S., Cunningham, Lisa L.

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Rescue of retinal ganglion cells in optic nerve injury using cell-selective AAV mediated delivery of SIRT1 von Ross, Ahmara G., McDougald, Devin S., Khan, Reas S., Duong, Thu T., Dine, Kimberly E., Aravand, Puya, Bennett, Jean, Chavali, Venkata Ramana Murthy, Shindler, Kenneth S.

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AKT3 Gene Transfer Promotes Anabolic Reprogramming and Photoreceptor Neuroprotection in a Pre-clinical Model of Retinitis Pigmentosa von McDougald, Devin S., Papp, Tyler E., Zezulin, Alexandra U., Zhou, Shangzhen, Bennett, Jean

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Dual SMAD inhibition and Wnt inhibition enable efficient and reproducible differentiations of induced pluripotent stem cells into retinal ganglion cells von Chavali, Venkata R. M., Haider, Naqi, Rathi, Sonika, Vrathasha, Vrathasha, Alapati, Teja, He, Jie, Gill, Kamaljot, Nikonov, Roman, Duong, Thu T., McDougald, Devin S., Nikonov, Sergei, O’Brien, Joan, Mills, Jason A.

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Gene Therapy for Sensorineural Hearing Loss von Chien, Wade W, Monzack, Elyssa L, McDougald, Devin S, Cunningham, Lisa L

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Selective Upregulation of SIRT1 Expression in Retinal Ganglion Cells by AAV-Mediated Gene Delivery Increases Neuronal Cell Survival and Alleviates Axon Demyelination Associated wit... von Ross, Ahmara G, Chaqour, Brahim, McDougald, Devin S, Dine, Kimberly E, Duong, Thu T, Shindler, Ryan E, Yue, Jipeng, Liu, Tehui, Shindler, Kenneth S

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Spliceosome-Mediated Pre-mRNA trans-Splicing Can Repair CEP290 mRNA von Dooley, Scott J., McDougald, Devin S., Fisher, Krishna J., Bennicelli, Jeanette L., Mitchell, Lloyd G., Bennett, Jean

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AAV-mediated PEX1 gene augmentation improves visual function in the PEX1-Gly844Asp mouse model for mild Zellweger spectrum disorder von Argyriou, Catherine, Polosa, Anna, Song, Ji Yun, Omri, Samy, Steele, Bradford, Cécyre, Bruno, McDougald, Devin S., Di Pietro, Erminia, Bouchard, Jean-François, Bennett, Jean, Hacia, Joseph G., Lachapelle, Pierre, Braverman, Nancy E.

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CRISPR Activation Enhances In Vitro Potency of AAV Vectors Driven by Tissue-Specific Promoters von McDougald, Devin S., Duong, Thu T., Palozola, Katherine C., Marsh, Anson, Papp, Tyler E., Mills, Jason A., Zhou, Shangzhen, Bennett, Jean

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Personalized models reveal mechanistic and therapeutic insights into CEP290-associated Leber congenital amaurosis von McDougald, Devin S, Kmiec, Eric, Mills, Jason A

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ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES THEREOF von MCDOUGALD, Devin, QIAN, Randolph

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ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES THEREOF von MCDOUGALD, Devin, QIAN, Randolph

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ENGINEERED NUCLEIC ACID REGULATORY ELEMENT AND METHODS OF USES THEREOF von Qiao, Chunping, McDougald, Devin

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ENGINEERED NUCLEIC ACID REGULATORY ELEMENT AND METHODS OF USES THEREOF von MCDOUGALD, Devin, QIAO, Chunping

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TREATMENT OF MUCOPOLYSACCHARIDOSIS IVA von MCDOUGALD, Devin, KARUMUTHIL-MELETHIL, Subha

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ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES THEREOF von MCDOUGALD, Devin, QIAO, Chunping, QIAN, Randolph

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TREATMENT OF MUCOPOLYSACCHARIDOSIS IVA von MCDOUGALD, Devin, KARUMUTHIL-MELETHIL, Subha

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ENGINEERED NUCLEIC ACID REGULATORY ELEMENT AND METHODS OF USES THEREOF von MCDOUGALD, Devin, QIAO, Chunping

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