Olipudase alfa for treatment of acid sphingomyelinase deficiency (ASMD): safety and efficacy in adults treated for 30 months von Wasserstein, Melissa P., Diaz, George A., Lachmann, Robin H., Jouvin, Marie-Hélène, Nandy, Indrani, Ji, Allena J., Puga, Ana Cristina

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Safety and Efficacy of Mitapivat in Pyruvate Kinase Deficiency von Grace, Rachael F, Rose, Christian, Layton, D. Mark, Galactéros, Frédéric, Barcellini, Wilma, Morton, D. Holmes, van Beers, Eduard J, Yaish, Hassan, Ravindranath, Yaddanapudi, Kuo, Kevin H.M, Sheth, Sujit, Kwiatkowski, Janet L, Barbier, Ann J, Bodie, Susan, Silver, Bruce, Hua, Lei, Kung, Charles, Hawkins, Peter, Jouvin, Marie-Hélène, Bowden, Chris, Glader, Bertil

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Safety and Efficacy of Nipocalimab in Patients With Generalized Myasthenia Gravis: Results From the Randomized Phase 2 Vivacity-MG Study von Antozzi, Carlo, Guptill, Jeffrey, Bril, Vera, Gamez, Josep, Meuth, Sven G, Nowak, Richard J, Quan, Dianna, Sevilla, Teresa, Jouvin, Marie-Helene, Jin, Jim, Karcher, Keith, Ramchandren, Sindhu, Sun, Hong, Ling, Leona, Zhu, Yaowei, Arroyo, Santiago

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Defective mast cell effector functions in mice lacking the CRACM1 pore subunit of store-operated calcium release-activated calcium channels von Bird, Gary S, Rao, Patricia E, DeHaven, Wayne I, Vig, Monika, Billingsley, James M, Jouvin, Marie-Hélène, Kinet, Jean-Pierre, Hutchings, Amy B, Wang, Huiyun, Putney, James W

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Trichuris suis ova: Testing a helminth-based therapy as an extension of the hygiene hypothesis von Jouvin, Marie-Hélène, MD, Kinet, Jean-Pierre, MD

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Once- versus twice-daily dosing of eliglustat in adults with Gaucher disease type 1: The Phase 3, randomized, double-blind EDGE trial von Charrow, Joel, Fraga, Cristina, Gu, Xuefan, Ida, Hiroyuki, Longo, Nicola, Lukina, Elena, Nonino, Alexandre, Gaemers, Sebastiaan J.M., Jouvin, Marie-Helene, Li, Jing, Wu, Yaoshi, Xue, Yong, Peterschmitt, M. Judith

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The tetraspanin CD63 is required for efficient IgE-mediated mast cell degranulation and anaphylaxis von Kraft, Stefan, Jouvin, Marie-Hélène, Kulkarni, Nitin, Kissing, Sandra, Morgan, Ellen S, Dvorak, Ann M, Schröder, Bernd, Saftig, Paul, Kinet, Jean-Pierre

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The TRPM4 channel controls monocyte and macrophage, but not neutrophil, function for survival in sepsis von Serafini, Nicolas, Dahdah, Albert, Barbet, Gaëtan, Demion, Marie, Attout, Tarik, Gautier, Grégory, Arcos-Fajardo, Michelle, Souchet, Hervé, Jouvin, Marie-Hélène, Vrtovsnik, François, Kinet, Jean-Pierre, Benhamou, Marc, Monteiro, Renato C, Launay, Pierre

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Safety and Tolerability of Losmapimod for the Treatment of FSHD (P3-11.010) von Jouvin, Marie-Helene, Ramana, Vivekananda, Jiang, John

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Anti-CD63 antibodies suppress IgE-dependent allergic reactions in vitro and in vivo von Kraft, Stefan, Fleming, Tony, Billingsley, James M, Lin, Shih-Yao, Jouvin, Marie-Hélène, Storz, Peter, Kinet, Jean-Pierre

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Direct Effects of Interleukin-13 on Signaling Pathways for Physiological Responses in Cultured Human Airway Smooth Muscle Cells von LAPORTE, JOHANNE C, MOORE, PAUL E, BARALDO, SIMONETTA, JOUVIN, MARIE-HELENE, CHURCH, TRUDI L, SCHWARTZMAN, IGOR N, PANETTIERI, REYNOLD A., Jr, KINET, JEAN-PIERRE, SHORE, STEPHANIE A

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Cotranslational endoplasmic reticulum assembly of FcεRI controls the formation of functional IgE-binding receptors von Fiebiger, Edda, Tortorella, Domenico, Jouvin, Marie-Helene, Kinet, Jean-Pierre, Ploegh, Hidde L.

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Low-Voltage-Activated CaV3.1 Calcium Channels Shape T Helper Cell Cytokine Profiles von Wang, Huiyun, Zhang, Xuexin, Xue, Li, Xing, Juan, Jouvin, Marie-Hélène, Putney, James W., Anderson, Matthew P., Trebak, Mohamed, Kinet, Jean-Pierre

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Role of the extracellular domain of Fc epsilon RI alpha in intracellular processing and surface expression of the high affinity receptor for IgE Fc epsilon RI von Hartman, Mor-Li, Lin, Shih-Yao, Jouvin, Marie-Hélène, Kinet, Jean-Pierre

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Phosphorylation and dephosphorylation of the high-affinity receptor for immunoglobulin E immediately after receptor engagement and disengagement von Paolini, Rossella, Jouvin, Marie-Hélène, Kinet, Jean-Pierre

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Molecular dissection of the FcRbeta signaling amplifier von On, Marina, Billingsley, James M, Jouvin, Marie-Hélène, Kinet, Jean-Pierre

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Nipocalimab Dose Selection for A Phase 3 Study in Adult Patients with Generalized Myasthenia Gravis (P1-5.018) von Pérez-Ruixo, Juan-José, Zhu, Yaowei, Neyens, Martine, Jouvin, Marie-Helene, Ramchandren, Sindhu, Xu, Yan, Leu, Jocelyn, Dosne, Anne-Gaëlle, Xiong, Yuan, Valenzuela, Belén, Ling, Leona, Nandy, Partha, Sun, Hong

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Human anti‐FcϵRIα autoantibodies isolated from healthy donors cross‐react with tetanus toxoid von Horn, Michael P., Gerster, Tamara, Ochensberger, Brigitte, Derer, Tanja, Kricek, Franz, Jouvin, Marie‐Hélène, Kinet, Jean‐Pierre, Tschernig, Thomas, Vogel, Monique, Stadler, Beda M., Miescher, Sylvia M.

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Vivacity-MG: A Phase 2, Multicenter, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Safety, Tolerability, Efficacy, Pharmacokinetics, Pharmacodynamics, and Immu... von Guptill, Jeffrey, Antozzi, Carlo, Bril, Vera, Gamez, Josep, Meuth, Sven G., Blanco, Jose Luis Muñoz, Nowak, Richard J., Quan, Dianna, Sevilla, Teresa, Szczudlik, Andrzej, Hegarty, Brooke, Jouvin, Marie-Helene, Jin, Jim, Arroyo, Santiago

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A Second Amplifier Function for the Allergy-Associated FcεRI-β Subunit von Donnadieu, Emmanuel, Jouvin, Marie-Hélène, Kinet, Jean-Pierre

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