Glucosylceramide synthase inhibition alleviates aberrations in synucleinopathy models von Sardi, S. Pablo, Viel, Catherine, Clarke, Jennifer, Treleaven, Christopher M., Richards, Amy M., Park, Hyejung, Olszewski, Maureen A., Dodge, James C., Marshall, John, Makino, Elina, Wang, Bing, Sidman, Richard L., Cheng, Seng H., Shihabuddin, Lamya S.

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The GTPase Activating Factor for Transducin in Rod Photoreceptors Is the Complex between RGS9 and Type 5 G Protein β Subunit von Makino, Elina R., Handy, Jason W., Li, Tiansen, Arshavsky, Vadim Y.

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Development of a novel encapsulated non-viral cell-based therapy for MPS VI von Pearson, Erika, Donovan, Marissa, Tietz, Drew, Fluharty, Brian, Hsu, Anya, Smith, Devyn, Makino, Elina

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SIG-018: Novel encapsulated non-viral cell-based therapy for MPS II von Tietz, Drew, Donovan, Marissa, Pearson, Erika, Fluharty, Brian, Smith, Devyn, Makino, Elina

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Development of a novel encapsulated non-viral cell-based, BBB-penetrant therapy for MPS I von Pearson, Erika, Hsu, Anya, Tietz, Drew, Donovan, Marissa, Sohn, Lauren, Hussack, Greg, Stanimirovic, Danica, Makino, Elina, Ashton-Rickardt, Philip G.

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Development of a novel encapsulated non-viral cell-based therapy for MPS VI von Pearson, Erika, Yu, Susan, Tietz, Drew, Donovan, Marissa, Sohn, Lauren, Barrett, Kathleen, Makino, Elina, Ashton-Rickardt, Philip G.

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SIG-007: Novel encapsulated non-viral cell-based therapy for Fabry disease von Fluharty, Brian, Tietz, Drew, Jansen, Lauren, Huang, Janet, Li, Jie, Schladenhauffen, Jacob, McAuliffe, Michele, Kelley, Elizabeth, Glyptis, Tina, Zhao, Verna, Barrett, Kathleen, Drapeau, Susan, Smith, Devyn, Makino, Elina

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Preclinical development of SIG-005 for treatment of MPS I von Donovan, Marissa, Makino, Elina, Fluharty, Brian, Tietz, Drew, Pearson, Erika, Jansen, Lauren, Barney, Lauren, Sewell, Jared, Huang, Janet, Corzo, Deya, Moller, David, Peritt, David, Vivaldi, Rogerio

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Preclinical development of SIG-007 for treatment of Fabry disease von Fluharty, Brian, Makino, Elina, Donovan, Marissa, Tietz, Drew, Pearson, Erika, Jansen, Lauren, Barney, Lauren, Sewell, Jared, Huang, Janet, Corzo, Deya, Moller, David, Peritt, David, Vivaldi, Rogerio

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SIG-005: Novel encapsulated non-viral cell-based therapy for MPS I von Donovan, Marissa, Pearson, Erika, Tietz, Drew, Fluharty, Brian, Jansen, Lauren, Schladenhauffen, Jacob, McAuliffe, Michele, Kelley, Elizabeth, Glyptis, Tina, Vo, Tiffany, Li, Jie, Zhao, Verna, Barrett, Kathleen, Drapeau, Susan, Smith, Devyn, Makino, Elina

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Discovery of novel endogenous biomarkers in MPS I von Makino, Elina, Belenky, Alexey, Varban, Mariette Lee, Klodnitsky, Helen, Phaneuf, Clifford, Orchard, Paul, Lund, Troy

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Brain Penetrable Inhibitors of Ceramide Galactosyltransferase for the Treatment of Lysosomal Storage Disorders von Thurairatnam, Sukanthini, Lim, Sungtaek, Choi-Sledeski, Yong Mi, Hirth, Bradford H, Jiang, John, Macor, John E, Makino, Elina, Maniar, Sachin, Musick, Kwon, Pribish, James R, Munson, Mark

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Fast, sensitive method for trisaccharide biomarker detection in mucopolysaccharidosis type 1 von Makino, Elina, Klodnitsky, Helen, Leonard, John, Lillie, James, Lund, Troy C., Marshall, John, Nietupski, Jennifer, Orchard, Paul J., Miller, Weston P., Phaneuf, Clifford, Tietz, Drew, Varban, Mariet L., Donovan, Marissa, Belenki, Alexey

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Publisher Correction: Fast, sensitive method for trisaccharide biomarker detection in mucopolysaccharidosis type 1 von Makino, Elina, Klodnitsky, Helen, Leonard, John, Lillie, James, Lund, Troy C., Marshall, John, Nietupski, Jennifer, Orchard, Paul J., Miller, Weston P., Phaneuf, Clifford, Tietz, Drew, Varban, Mariet L., Donovan, Marissa, Belenki, Alexey

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COMPOSITIONS, DEVICES AND METHODS FOR TREATING MPS VI DISEASE von PEARSON, Erika, MAKINO, Elina

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COMPOSITIONS, DEVICES AND METHODS FOR TREATING MPS VI DISEASE von Makino, Elina, Pearson, Erika

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COMPOSITIONS, DEVICES AND METHODS FOR TREATING MPS VI DISEASE von PEARSON, Erika, MAKINO, Elina

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GENETICALLY MODIFIED HUMAN CELL LINES AND USES THEREOF von Fluharty, Brian Richard, Makino, Elina

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GENETICALLY MODIFIED HUMAN CELL LINES AND USES THEREOF von FLUHARTY, Brian, MAKINO, Elina

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COMPOSITIONS, DEVICES AND METHODS FOR TREATING MPS VI DISEASE von PEARSON, Erika, MAKINO, Elina

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